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Clinical Trials on Epidermolysis Bullosa Dystrophica in United States
Total 670 results
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PfizerRecruitingDuchenne Muscular DystrophyUnited States
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Akashi TherapeuticsTerminatedDuchenne Muscular DystrophyUnited States
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PfizerActive, not recruitingDuchenne Muscular DystrophyUnited States
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Processa PharmaceuticalsTerminated
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Capricor Inc.CompletedDuchenne Muscular DystrophyUnited States
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Indiana UniversityRecruitingPigmentary Retinopathy | Pentosan Polysulfate Sodium Maculopathy | Pigmentary Maculopathy | Toxic Maculopathy | Interstitial Cystitis, ChronicUnited States
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Capricor Inc.Active, not recruiting
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Susan J. HayflickOregon Health and Science University; Oregon Clinical and Translational Research...CompletedPantothenate Kinase-associated Neurodegeneration (PKAN)United States
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Sarepta Therapeutics, Inc.RecruitingDuchenne Muscular DystrophyUnited States
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University of California, Santa BarbaraJohns Hopkins University; National Eye Institute (NEI); University of Michigan; University of MinnesotaCompleted
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Catabasis PharmaceuticalsCompletedMuscular Dystrophy, DuchenneUnited States
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Processa PharmaceuticalsTerminatedDuchenne Muscular DystrophyUnited States
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University of SouthamptonUnknownKeratoconus | Fuchs Dystrophy | Corneal DiseaseUnited Kingdom
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Sarepta Therapeutics, Inc.Hoffmann-La RocheEnrolling by invitation
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University of PittsburghRespirtech, Inc.CompletedDuchenne Muscular DystrophyUnited States
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Ultragenyx Pharmaceutical IncCompletedGNE Myopathy | Hereditary Inclusion Body Myopathy (HIBM)United States, Israel
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Nanoscope Therapeutics Inc.Enrolling by invitationEye Diseases | Retinal Degeneration | Retinal Diseases | Retinitis Pigmentosa | Retinitis | Eye Diseases, Hereditary | Retinal DystrophiesUnited States, Puerto Rico
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NS Pharma, Inc.Active, not recruitingDuchenne Muscular DystrophyUnited States, Canada
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PTC TherapeuticsCompletedDuchenne Muscular DystrophyUnited States
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Janssen Research & Development, LLCJanssen Research & Development, LLCActive, not recruitingX-Linked Retinitis PigmentosaUnited States, Canada, Israel, United Kingdom, Spain, Denmark, France, Belgium, Italy, Netherlands, Switzerland
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aTyr Pharma, Inc.CompletedFacioscapulohumeral Muscular Dystrophy (FSHD)United States, Netherlands, France, Italy
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Nanoscope Therapeutics Inc.CompletedEye Diseases | Retinal Degeneration | Retinal Diseases | Retinitis Pigmentosa | Retinitis | Eye Diseases, Hereditary | Retinal DystrophiesUnited States, Puerto Rico
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Janssen Research & Development, LLCJanssen Research & Development, LLCActive, not recruitingX-Linked Retinitis PigmentosaBelgium, Canada, United States, Israel, United Kingdom, Spain, Denmark, France, Italy, Netherlands, Switzerland
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University College, LondonNot yet recruiting
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Cooperative International Neuromuscular Research...Completed
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Sarepta Therapeutics, Inc.RecruitingLimb-girdle Muscular DystrophyUnited States, Brazil, Belgium, Canada, Germany, Italy, Spain, Sweden, Turkey, United Kingdom
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PTC TherapeuticsCompletedDuchenne Muscular DystrophyUnited States
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PTC TherapeuticsGenzyme, a Sanofi CompanyTerminatedDuchenne Muscular DystrophyUnited States
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Susan J. HayflickOregon Health and Science UniversityRecruitingNeurodegeneration With Brain Iron Accumulation (NBIA)United States
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Boston Children's HospitalMuscular Dystrophy AssociationRecruitingCentronuclear Myopathy | Myotubular Myopathy | Nemaline Myopathy | Central Core Disease | Congenital Fiber Type Disproportion | Multiminicore Disease | Rigid Spine Muscular Dystrophy | Undefined Congenital MyopathyUnited States
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National Heart, Lung, and Blood Institute (NHLBI)CompletedCardiomyopathy, Hypertrophic | Muscular Dystrophy, OculopharyngealUnited States
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Dart Therapeutics. LLCCompletedDuchenne Muscular DystrophyUnited States
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ApoPharmaFood and Drug Administration (FDA)CompletedPantothenate Kinase-Associated NeurodegenerationUnited States, Germany, Italy, United Kingdom
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Subha RamanBallou SkiesCompletedDuchenne Muscular DystrophyUnited States
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Wave Life Sciences Ltd.CompletedDuchenne Muscular DystrophyBelgium, United Kingdom, France, United States, Italy, Canada, Netherlands
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PTC TherapeuticsMuscular Dystrophy AssociationCompletedDuchenne Muscular DystrophyUnited States
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PepGen IncRecruitingMyotonic Dystrophy 1United States, Canada
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Washington University School of MedicineUniversity of California, Davis; Nationwide Children's Hospital; University of... and other collaboratorsCompletedDuchenne Muscular DystrophyUnited States
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PYC TherapeuticsRecruitingRetinitis Pigmentosa | Eye Diseases, Hereditary | Retinal Dystrophies | Retinal Dystrophy Rod | Retinal Dystrophy Rod ProgressiveUnited States, Australia
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ApoPharmaCompletedPantothenate Kinase-Associated NeurodegenerationUnited States, Germany, Italy, United Kingdom
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University of Kansas Medical CenterHoffmann-La Roche; Seattle Children's Hospital; University of Rochester; University... and other collaboratorsRecruitingFSHDUnited States, Canada, United Kingdom
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NS Pharma, Inc.Cooperative International Neuromuscular Research Group; Nippon Shinyaku Co.... and other collaboratorsCompletedDuchenne Muscular DystrophyUnited States, Canada
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PTC TherapeuticsCompletedDuchenne Muscular DystrophyUnited States
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QLT Inc.CompletedLCA (Leber Congenital Amaurosis) | RP (Retinitis Pigmentosa)Canada, United States, Germany, Netherlands, United Kingdom
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Hoffmann-La RocheActive, not recruitingFacioscapulohumeral Muscular Dystrophy (FSHD)United States, United Kingdom, Italy, Denmark
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University of Kansas Medical CenterNational Institute of Neurological Disorders and Stroke (NINDS)Active, not recruitingFacioscapulohumeral Muscular DystrophyUnited States
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Astellas Pharma IncTerminatedDuchenne Muscular Dystrophy (DMD)United States
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Capricor Inc.CompletedDuchenne Muscular Dystrophy | CardiomyopathyUnited States
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Hoffmann-La RocheTerminatedMuscular Dystrophy (DMD)United States, Canada
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NS Pharma, Inc.Nippon Shinyaku Co., Ltd.CompletedDuchenne Muscular DystrophySpain, United States, Russian Federation, Italy, China, Turkey