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Clinical Trials on Epidermolysis Bullosa Dystrophica
Total 1341 results
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Lokman Hekim ÜniversitesiCompletedParents | Duchenne Muscular Dystrophy | Psychoeducation | Psychological WellnessTurkey
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PTC TherapeuticsCompletedNonsene Mutation Duchenne Muscular DystrophyUnited States
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Avidity Biosciences, Inc.Enrolling by invitationDuchenne Muscular Dystrophy | DMD | Exon 44 | DuchenneUnited States
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Children's Hospital Medical Center, CincinnatiActive, not recruitingMusculoskeletal Abnormalities | Duchenne Muscular DystrophyUnited States
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Ondokuz Mayıs UniversityCompletedDuchenne Muscular Dystrophy (DMD)Turkey
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Université de SherbrookeRare Disease FoundationCompletedMyotonic Dystrophy 1Canada
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Hacettepe UniversityCompletedDuchenne Muscular Dystrophy | Gait Disorders in ChildrenTurkey
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LMU KlinikumCompleted
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Sarepta Therapeutics, Inc.CompletedDuchenne Muscular Dystrophy (DMD)United States
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University Hospital, GrenobleCompletedMyotonic DystrophyFrance
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Bioblast Pharma Ltd.WithdrawnOculopharyngeal Muscular DystrophyCanada
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National Human Genome Research Institute (NHGRI)TerminatedCommunication | Genetic DiseaseUnited States
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Cynthia GagnonFondation du Grand défi Pierre LavoieCompletedEffects of a Multiple Component Training Program on Muscles in Adults With Myotonic Dystrophy Type 1Myotonic Dystrophy 1Canada
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Parent Project, ItalyCompletedDuchenne Muscular Dystrophy (DMD)Italy
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GenethonInstitute of MyologyCompletedDuchenne Muscular Dystrophy (DMD)France
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University Hospital, Basel, SwitzerlandCompletedBecker's Muscular Dystrophy (BMD)Switzerland
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Ann & Robert H Lurie Children's Hospital of ChicagoChildren's National Research InstituteWithdrawnDuchenne Muscular Dystrophy (DMD)United States
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Vertex Pharmaceuticals IncorporatedRecruitingMyotonic Dystrophy Type 1 (DM1)United Kingdom, Canada, Australia
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Centre Hospitalier Universitaire de NiceRecruitingFacioscapulohumeral Muscular Dystrophy Type 2France, Italy, Spain
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Assistance Publique - Hôpitaux de ParisNot yet recruitingMyotonic Dystrophy 1 | Steinert's Disease | MetforminFrance
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Dyne TherapeuticsRecruitingMyotonic Dystrophy Type 1 (DM1)United Kingdom, France, Netherlands, Italy, Germany, New Zealand
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University of PennsylvaniaNational Eye Institute (NEI)RecruitingAge-related Macular Degeneration | Stargardts | Retinitis Pigmentosa | Choroideremia | Geographic AtrophyUnited States
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Swiss Federal Institute of TechnologyCompletedMuscle Weakness | Muscular Dystrophies | Muscular Dystrophy | Muscular Dystrophy, Facioscapulohumeral | Scapular Dyskinesis | Muscular WeaknessGermany, Switzerland
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PTC TherapeuticsTerminatedNervous System Diseases | Genetic Diseases, Inborn | Genetic Diseases, X-Linked | Musculoskeletal Diseases | Muscular Diseases | Neuromuscular Diseases | Muscular Dystrophies | Muscular Disorders, Atrophic | Muscular Dystrophy, DuchenneUnited States, Spain, Korea, Republic of, Belgium, France, Canada, Australia, United Kingdom, Israel, Italy, Germany, Brazil, Bulgaria, Chile, Czechia, Poland, Sweden, Switzerland, Turkey
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Hacettepe UniversityCompletedDuchenne Muscular Dystrophy | Upper Limb Function | Respiratory Function Test
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Radboud University Medical CenterAssistance Publique - Hôpitaux de Paris; Ludwig-Maximilians - University of... and other collaboratorsCompletedMyotonic Dystrophy Type 1Netherlands, France, Germany, United Kingdom
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Grete Andersen, MDCompletedFSHD - Facioscapulohumeral Muscular DystrophyDenmark
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Laurent ServaisSYSNAVRecruitingDuchenne Muscular Dystrophy | Fascioscapulohumeral Muscular DystrophyBelgium
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Virginia Commonwealth UniversityEdgewise Therapeutics, Inc.RecruitingMuscular Dystrophies | Becker Muscular Dystrophy | Muscular Dystrophy in Children | Muscular Dystrophy, BeckerUnited States, New Zealand, United Kingdom
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Université du Québec à ChicoutimiRecruitingMyotonic Dystrophy Type 1 (DM1)Canada
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Spark Therapeutics, Inc.Children's Hospital of Philadelphia; University of IowaActive, not recruitingLeber Congenital Amaurosis | Inherited Retinal Dystrophy Due to RPE65 MutationsUnited States
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Sahra ŞirvanEnrolling by invitationDuchenne Muscular DystrophyTurkey
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ItalfarmacoCompletedDuchenne and Becker Muscular Dystrophy | Polycytemia VeraCanada
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Universidad de AlmeriaCompletedNeurologic Disorder | Pediatric Disorder | Duchenne | Sensorimotor Disorder NosSpain
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PTC TherapeuticsGenzyme, a Sanofi CompanyTerminatedDuchenne Muscular DystrophyUnited States
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PTC TherapeuticsCompletedNervous System Diseases | Genetic Diseases, Inborn | Genetic Diseases, X-Linked | Musculoskeletal Diseases | Muscular Diseases | Neuromuscular Diseases | Muscular Dystrophies | Muscular Disorders, Atrophic | Muscular Dystrophy, DuchenneUnited States, Spain, Korea, Republic of, Belgium, France, Canada, Australia, United Kingdom, Israel, Italy, Brazil, Chile, Czechia, Sweden, Switzerland, Turkey, Germany, Poland
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University Hospital, ToulouseUnknownDuchenne Muscular DystrophyFrance
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Eyecure Therapeutics Inc.Beijing Tongren HospitalUnknownLeber Congenital Amaurosis, Retinitis PigmentosaChina
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Hacettepe UniversityCompletedDuchenne Muscular DystrophyTurkey
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Oslo University HospitalUniversity Hospital of North Norway; The Research Council of NorwayCompletedDuchenne Muscular DystrophyNorway
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Massachusetts General HospitalCompletedDuchenne Muscular Dystrophy | Dystrophinopathy | Becker's Muscular DystrophyUnited States
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Wake Forest University Health SciencesNational Institute of Neurological Disorders and Stroke (NINDS)RecruitingMyotonic Dystrophy Type 2United States
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Virginia Commonwealth UniversityRecruitingCongenital Myotonic Dystrophy | Childhood Myotonic Dystrophy | CDM | CHDMUnited States, Italy
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Medical University of GdanskRecruitingMuscular Dystrophy, DuchennePoland
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University of OsloOslo University Hospital; Vikersund Rehabilitation CenterCompletedMyotonic Dystrophy Type 1 (DM1)Norway
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Stanford UniversityBiogenActive, not recruitingMyotonic Dystrophy 1United States
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Moorfields Eye Hospital NHS Foundation TrustCompletedRetinal Degeneration | Diabetic Retinopathy | Retinal Dystrophies | AMDUnited Kingdom
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McMaster UniversityCompletedMuscular Dystrophies | Myotonic Dystrophy 1Canada
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Expansion Therapeutics, Inc.CompletedMyotonic Dystrophy | Myotonic Dystrophy, Type 1 (DM1)United States
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Hugo W. Moser Research Institute at Kennedy Krieger...Johns Hopkins UniversityTerminatedDuchenne Muscular Dystrophy | Becker Muscular DystrophyUnited States