- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Epidermolysis Bullosa Dystrophica
Total 1341 results
-
Rigshospitalet, DenmarkUltragenyx Pharmaceutical IncCompletedTarui Disease | Debrancher Deficiency | GYG1 DEFICIENCYDenmark
-
Janssen Research & Development, LLCCompletedInterstitial Cystitis | Pigmentary Retinopathy | Pigmentary MaculopathyUnited States
-
Batman Training and Research HospitalCompletedCorneal Dystrophy | Macular Dystrophy | Hyperemesis Gravidarum - SevereTurkey
-
McGill UniversityCanadian Institutes of Health Research (CIHR); McGill University Health Centre... and other collaboratorsCompletedCerebral Palsy | Muscular Dystrophies | Spina Bifida | Musculoskeletal DisorderCanada
-
Icare Finland OyUnknownCorneal Dystrophy | Corneal Degeneration | Corneal Sensation Reduced | Corneal Transplant Failure | Herpetic Keratitis
-
Hôpital CochinAssociation Monégasque contre les MyopathiesUnknownDuchenne Muscular Dystrophy | Duchenne Muscular Dystrophy-Associated Dilated CardiomyopathyFrance
-
Seoul National University HospitalMinistry of Health & Welfare, KoreaAvailableLimbal Stem Cell Deficiency | Ocular Cicatricial Pemphigoid | Stevens-johnson Syndrome | Chemical BurnKorea, Republic of
-
National Institute of Neurological Disorders and...RecruitingMotor Neuron Disease | Muscular Dystrophy | Peripheral Nervous System Disease | Muscular DiseaseUnited States, Mali
-
Harmony Biosciences, LLCActive, not recruitingMyotonic Dystrophy 1 | Excessive Daytime SleepinessUnited States, Canada
-
Johns Hopkins UniversityNational Heart, Lung, and Blood Institute (NHLBI)Enrolling by invitationHypertrophic Cardiomyopathy (HCM) | Long QT Syndrome (LQTS) | Catecholaminergic Polymorphic Ventricular Tachycardia (CPVT) | Inherited Cardiac Arrythmias | Brugada Syndrome (BrS) | Early Repolarization Syndrome (ERS) | Arrhythmogenic Cardiomyopathy (AC, ARVD/C) | Dilated Cardiomyopathy (DCM) | Muscular... and other conditionsUnited States
-
Avidity Biosciences, Inc.Not yet recruitingMyotonic Dystrophy | Myotonic Disorders | Myotonia | Myotonic Dystrophy Type 1 (DM1) | Myotonic Dystrophy 1 | Myotonic Muscular Dystrophy | DM1 | Dystrophy Myotonic | Steinert Disease | Steinert
-
Centre Hospitalier National d'Ophtalmologie des...RecruitingStroke | Glaucoma | Hypertension | Diabetes | Retinal Degeneration | Macular Edema | Retinitis Pigmentosa | Retinal Detachment | Vascular Inflammation | Macular Dystrophy | Maculopathy, Age RelatedFrance
-
Myogem Health Company, S.L.CompletedMyotonic Dystrophy 1Spain
-
Gillette Children's Specialty HealthcareUniversity of MinnesotaCompletedSpinal Muscular Dystrophy | Neuromuscular DisabilityUnited States
-
Gilles BoireProcter and GambleCompletedMuscular Dystrophy | Osteoporosis | Cystic FibrosisCanada
-
Assistance Publique - Hôpitaux de ParisAssociation Française contre les Myopathies (AFM), ParisUnknownRespiratory Insufficiency | Myopathy | Muscular WeaknessFrance
-
Virginia Commonwealth UniversityMuscular Dystrophy AssociationRecruitingLGMD2E | LGMD2I | LGMD2A | LGMD2B | LGMD2C | LGMD1B | LGMD1C | LGMD1D | LGMD1E | LGMD1F | LGMD1G | LGMD1H | LGMD2D | LGMD2F | LGMD2G | LGMD2J | LGMD2K | LGMD2L | LGMD2M | LGMD2N | LGMD2O | LGMD2P | LGMD2Q | LGMD2S | LGMD2T | LGMD2U | LGMD2W | LGMD2X | LGMD2YUnited States
-
University of California, DavisActive, not recruitingDiabetic Retinopathy | Retinitis Pigmentosa | Non-exudative Age-related Macular Degeneration | Retina Vein Occlusion | Hereditary Macular DegenerationUnited States
-
Sensor Technology for DeafblindCentral Clinical Hospital under President Affairs; Deaf-Blind Support Foundation... and other collaboratorsCompletedRetinitis Pigmentosa | Usher SyndromesRussian Federation
-
ProQR TherapeuticsActive, not recruitingEye Diseases | Retinitis | Eye Diseases, Hereditary | Retinal Dystrophies | Vision Disorders | Retinal Disease | Autosomal Dominant Retinitis Pigmentosa | Vision TunnelUnited States
-
National Taiwan University HospitalUnknownAlkaline Chemical Burn Of Cornea And Conjunctival Sac | Acid Chemical Burn Of Cornea And Conjunctival Sac | Benign Mucous Membrane Pemphigoid With Ocular InvolvementTaiwan
-
Chulalongkorn UniversityMahidol University; Chiang Mai University; Phramongkutklao College of Medicine... and other collaboratorsUnknownDrug Reaction With Eosinophilia and Systemic Symptoms | Toxic Epidermal Necrolysis | Acute Generalized Exanthematous Pustulosis | Steven-Johnson Syndrome | Generalized Bullous Fixed Drug EruptionThailand
-
University of Colorado, DenverRecruitingHearing Loss | Smith-Lemli-Opitz Syndrome | Cone-Rod DystrophyUnited States
-
Ohio State UniversityNational Institute on Deafness and Other Communication Disorders (NIDCD)RecruitingUsher Syndrome | Cochlear ImplantationUnited States
-
University of Campania "Luigi Vanvitelli"RecruitingSudden Cardiac Death | Myotonic Dystrophy 1Italy
-
University of RochesterNational Institute of Neurological Disorders and Stroke (NINDS)RecruitingMuscular Dystrophy | Myotonic Dystrophy Type 2 | Myotonic Dystrophy Type 1 | Myotonic Dystrophy | Facioscapulohumeral Muscular Dystrophy | Steinert's Disease | Congenital Myotonic Dystrophy | PROMM (Proximal Myotonic Myopathy) | Myotonic Muscular DystrophyUnited States
-
Nacuity Pharmaceuticals, Inc.Foundation Fighting BlindnessActive, not recruitingUsher SyndromesAustralia
-
University Hospital, LilleMinistry of Health, FranceCompletedMitochondrial Cytopathies DisordersFrance
-
National Center for Research Resources (NCRR)Oregon Health and Science UniversityTerminatedRetinitis Pigmentosa | Usher SyndromeUnited States
-
Centre Hospitalier National d'Ophtalmologie des...StreetlabCompletedRetinitis Pigmentosa | Leber's Hereditary Optic Neuropathy | Stargardt DiseaseFrance
-
University College, LondonNational Institute for Health Research, United Kingdom; Myotonic Dystrophy... and other collaboratorsRecruitingMyotonic Dystrophy 1 | Dysphagia, OropharyngealUnited Kingdom
-
Centre Hospitalier National d'Ophtalmologie des...Assistance Publique - Hôpitaux de ParisRecruiting
-
MejoraVisionMDMaisonneuve-Rosemont Hospital; Retina and Genomics InstituteRecruitingRetinitis Pigmentosa | Usher Syndromes | Cone Dystrophy | Retina; DystrophyMexico
-
Assistance Publique - Hôpitaux de ParisRecherche Clinique Paris Descartes Necker Cochin Sainte Anne; AFM-Téléthon...Recruiting
-
Nemours Children's ClinicCompletedMuscular Dystrophy | Spinal Muscular Atrophy | Arthrogryposis
-
Ente Ospedaliero Ospedali GallieraActive, not recruitingIron Overload | Neurodegenerative DiseaseItaly
-
Rigshospitalet, DenmarkCompletedSpinal Muscular Atrophy | Merosin Deficient Congenital Muscular DystrophyDenmark
-
Indiana University School of MedicineMuscular Dystrophy AssociationCompletedMuscular Dystrophy | Arrhythmia | Sudden Cardiac DeathUnited States
-
Centre Hospitalier National d'Ophtalmologie des...Institut National de la Santé Et de la Recherche Médicale, FranceUnknownUsher SyndromeFrance, Germany, Netherlands, Portugal
-
National Eye Institute (NEI)Completed
-
SanofiTerminatedRetinitis Pigmentosa | Usher SyndromeUnited States, France
-
University Hospital Inselspital, BerneCompletedMitochondrial Diseases | Mitochondrial Myopathies | Mitochondrial CytopathiesSwitzerland
-
National Center for Research Resources (NCRR)CompletedRetinitis Pigmentosa | Usher Syndrome | Congenital Hearing ImpairmentUnited States
-
IRCCS Ospedale San RaffaeleNot yet recruitingRare Diseases | Corneal Neovascularization | Limbal Stem Cell Deficiency | Aniridia | Neurotrophic Keratopathy | Ocular Cicatricial Pemphigoid | Ocular Graft-versus-host Disease | EEC Syndrome
-
National Institutes of Health Clinical Center (CC)RecruitingCerebral Palsy | Muscular Dystrophy | Spina Bifida | Incomplete Spinal Cord InjuryUnited States
-
Bahçeşehir UniversityNot yet recruitingDuchenne Muscular Dystrophy | Spinal Muscular Atrophy | Healthy Individuals
-
National Institutes of Health Clinical Center (CC)RecruitingCerebral Palsy | Muscular Dystrophy | Spina Bifida | Incomplete Spinal Cord InjuryUnited States
-
Jaeb Center for Health ResearchFoundation Fighting BlindnessActive, not recruitingUsher Syndrome, Type 2A | Retinitis Pigmentosa 39United States, Canada, France, Germany, Netherlands, United Kingdom
-
Radboud University Medical CenterStichting UshersyndroomActive, not recruitingRetinitis Pigmentosa | Usher Syndrome, Type 2A | USH2ANetherlands
-
Sensor Technology for DeafblindDeaf-Blind Support Foundation Con-nection; Federal State Budgetary Institution... and other collaboratorsCompletedRetinitis Pigmentosa | Usher Syndrome | Congenital DeafnessRussian Federation