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Clinical Trials on Factor VIII Deficiency, Congenital
Total 543 results
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IpsenCompletedGrowth Disorders | Insulin-Like Growth Factor-1 DeficiencyUnited States
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Hospital Universitari Vall d'Hebron Research InstituteUniversidad de MurciaUnknownCongenital Heart Diseases | Antithrombin III Deficiency | Congenital Disorder of Glycosylation | Conotruncal DefectsSpain
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Northwestern UniversityCompletedCongenital Leptin Deficiency (Disorder)United States
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University of MinnesotaRecruiting
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QOL Medical, LLCJohns Hopkins University; Massachusetts General Hospital; Baylor College of Medicine and other collaboratorsCompletedCongenital Sucrase-isomaltase Deficiency (CSID)United States
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Cairo UniversityCompletedLeiden Factor V Deficiency,Preeclampsia | Doppler Examination | Palental Pathology
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Origin BiosciencesCompletedMolybdenum Cofactor Deficiency, Type AUnited States, Spain, Israel, Norway, Turkey, United Kingdom
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PATHMahidol Oxford Tropical Medicine Research UnitTerminated
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Maggie's Pearl, LLCActive, not recruitingPmm2-CDG | Phosphomannomutase 2 Deficiency | Phosphomannomutase 2 Congenital Disorder of Glycosylation | Phosphomannomutase II Congenital Disorder of Glycosylation | Phosphomannomutase II DeficiencyUnited States
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Orphatech Pharmaceuticals, GmbHWithdrawnMolybdenum Cofactor Deficiency Type AAustralia
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Malaria ConsortiumCenters for Disease Control and Prevention; World Health Organization; National... and other collaboratorsCompleted
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Marmara UniversityNational Institute of Allergy and Infectious Diseases (NIAID)UnknownProtein-Losing Enteropathies | CD55 - Cluster of Differentiation Antigen 55 Deficiency | Primary Intestinal Lymphangiectasis | Complement Regulatory Factor DefectTurkey
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Origin BiosciencesCompletedMolybdenum Cofactor Deficiency, Type AUnited States, Australia, Netherlands, United Kingdom, Tunisia
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Izmir Katip Celebi UniversityRecruitingClass III Malocclusion | Anterior Crossbite | Maxillary DeficiencyTurkey
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IpsenTerminatedPrimary Insulin-like Growth Factor-1 DeficiencyUnited States
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IpsenTerminatedrhGH and rhIGF-1 Combination Therapy in Children With Short Stature Associated With IGF-1 DeficiencyInsulin-like Growth Factor-1 DeficiencyUnited States
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Skane University HospitalIndiana Hemophilia &Thrombosis Center, Inc.; Bioverativ Therapeutics Inc.; Swedish...Active, not recruitingFactor IX DeficiencyUnited States
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Universitas Sumatera UtaraRecruitingAtrial Septal Defect | Congenital Heart Disease | Patent Ductus Arteriosus | Ventricular Septal Defect | Thiamine DeficiencyIndonesia
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Menzies School of Health ResearchPATH; Indonesia University; Institute of Tropical Medicine, Belgium; UNITAID; Burnet... and other collaboratorsRecruitingVivax Malaria | G6PD DeficiencyIndonesia
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Macfarlane Burnet Institute for Medical Research...PATH; UNITAID; University of Melbourne; Menzies School of Health Research; Medicines... and other collaboratorsRecruitingVivax Malaria | G6PD DeficiencyPapua New Guinea
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QOL Medical, LLCRecruitingCongenital Sucrase-Isomaltase Deficiency | CSID | Sucrase Isomaltase DeficiencyUnited States
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Dr. Prayuth SudathipMedicines for Malaria VentureCompletedMalaria, Vivax | G6PD DeficiencyThailand
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Fundação de Medicina Tropical Dr. Heitor Vieira...Ministry of Health, Brazil; Medicines for Malaria Venture; Centro de Pesquisa... and other collaboratorsActive, not recruitingMalaria, Vivax | G6PD DeficiencyBrazil
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Fundação de Medicina Tropical Dr. Heitor Vieira...Oswaldo Cruz Foundation; Conselho Nacional de Desenvolvimento Científico e...Active, not recruitingVivax Malaria | G6PD DeficiencyBrazil
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Liverpool School of Tropical MedicineKenya Medical Research Institute; Medicines for Malaria Venture; Worldwide Antimalarial...Recruiting
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University of Alabama at BirminghamCompletedFolic Acid Deficiency | Neural Tube Defects | FortificationUnited States
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Jiangsu Gensciences lnc.CompletedFactor VII Deficiency | Hemophilia A With Inhibitor | Hemophilia B With InhibitorChina
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University of Sao Paulo General HospitalMerit Medical Systems, Inc.RecruitingHemophilia | Arthropathy | Synovitis | Hemarthrosis | Embolization | Clotting Factor DeficiencyBrazil
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University of Texas Southwestern Medical CenterRecruitingHemophilia A | Factor VIIIUnited States
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Hospital Universitario La FeUnknownHemophilia A | Factor VIIISpain
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University of MinnesotaEnrolling by invitationIron-deficiency | Anemia | Malaria | Iron Deficiency Anemia | Anemia, Iron Deficiency | Anemia in ChildrenUganda
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Laboratoire français de Fractionnement et de BiotechnologiesCompletedHypofibrinogenemia, Congenital | Afibrinogenemia, CongenitalFrance, Lebanon, Morocco, Turkey
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Wenzhou Medical UniversityUnknownThe Incidence and Risk Factors of Glaucoma After Congenital Cataract SurgeryChina
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Cure CMDCongenital Muscle Disease International RegistrWithdrawnLAMA2-MD (Merosin Deficient Congenital Muscular Dystrophy, MDC1A)United States
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Instituto Grifols, S.A.CompletedCoronary Artery Bypass | Acquired Antithrombin III DeficiencyItaly
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Mayo ClinicrEVO BiologicsTerminatedThrombophilia Due to Acquired Antithrombin III DeficiencyUnited States
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The University of Hong KongQueen Mary Hospital, Hong KongNot yet recruitingThalassemia | Folic Acid Deficiency Anemia
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Novo Nordisk A/SEnrolling by invitationCongenital Bleeding Disorder | Congenital FXIII DeficiencyJapan
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Congenital FXIII DeficiencySpain, United States, Canada, Italy, United Kingdom, Hungary
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Congenital FXIII DeficiencyUnited Kingdom, Israel, United States
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Congenital FXIII DeficiencyUnited States, Israel, United Kingdom
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Novo Nordisk A/SCompletedObservational Study on Safety and Efficacy of NovoSeven® in Subjects With Congenital FVII DeficiencyCongenital Bleeding Disorder | Congenital FVII DeficiencyJapan
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IpsenCompletedGrowth Disorders | Insulin-Like Growth Factor-1 DeficiencyUnited States
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Hospital Universitari Vall d'Hebron Research InstituteUnknownBurns | Coagulation Disorder | Endothelial Dysfunction | Factor XIII Deficiency | Cicatrization
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Novo Nordisk A/SCompletedHealthy | Congenital Bleeding Disorder | Congenital FXIII DeficiencyUnited Kingdom
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Novo Nordisk A/SCompletedHealthy | Congenital Bleeding Disorder | Congenital FXIII DeficiencyUnited Kingdom
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Rigshospitalet, DenmarkUltragenyx Pharmaceutical IncCompletedTarui Disease | Debrancher Deficiency | GYG1 DEFICIENCYDenmark
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Groupe Maladies hémorragiques de BretagneRecruitingDesmopressin | Hemophilia A, Mild | Factor VIIIFrance
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Hydrocephalus and Neuroscience InstituteCompletedFolic Acid Deficiency | Neural Tube Defects | Spina Bifida | Anencephaly-Spina BifidaUnited States
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RTI InternationalEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsEnrolling by invitationPrimary Hyperoxaluria Type 3 | Diabetes Mellitus | Hemophilia A | Hemophilia B | Hereditary Fructose Intolerance | Cystic Fibrosis | Factor VII Deficiency | Phenylketonurias | Sickle Cell Disease | Dravet Syndrome | Duchenne Muscular Dystrophy | Prader-Willi Syndrome | Fragile X Syndrome | Chronic Granulomatous Disease and other conditionsUnited States