- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Factor VIII Deficiency, Congenital
Total 543 results
-
BiotestAccovion GmbH; ICON plc; SYNLAB Analytics and Services Germany GmbH; Phoenix Clinical... and other collaboratorsCompletedCongenital Afibrinogenemia | Congenital HypofibrinogenemiaBulgaria, Egypt, Germany, Lebanon, Tunisia
-
Institute for Clinical and Experimental MedicineSahlgrenska University Hospital, Sweden; University Hospital, MotolRecruitingInfertility, Female | Mayer Rokitansky Kuster Hauser Syndrome | Absolute Uterine Factor Infertility | Mullerian Aplasia | Uterus; Absence, Congenital | Uterus Absence, AcquiredCzechia
-
HeartWorks, Inc.RecruitingCongenital Heart Disease | Univentricular Heart | Heart Failure NYHA Class III | Heart Failure NYHA Class IVUnited States
-
University Hospital, Clermont-FerrandTerminatedVisual Deficiency | Congenital Blindness | Acquired BlindnessFrance
-
Prometic Biotherapeutics, Inc.CompletedHypoplasminogenemia | Congenital Plasminogen DeficiencyUnited States, Norway
-
Rigshospitalet, DenmarkUnknownCarbohydrate Metabolism, Inborn Errors | Metabolism, Inborn Errors | Lipid Metabolism, Inborn Errors | Glycogen Storage Disease Type II | Glycogen Storage Disease Type V | VLCAD Deficiency | Glycogen Storage Disease Type III | Phosphoglycerate Kinase Deficiency | Neutral Lipid Storage Disease | Carnitine... and other conditionsDenmark
-
Novo Nordisk A/SCompletedHealthy | Congenital Bleeding Disorder | Congenital FXIII DeficiencyUnited Kingdom
-
OctapharmaNot yet recruiting
-
Catalyst BiosciencesTerminatedFactor VII Deficiency | Hemophilia A With Inhibitor | Glanzmann ThrombastheniaUnited States, India, Italy, Russian Federation, Ukraine
-
Steno Diabetes Center CopenhagenThe Novo Nordisk Foundation Center for Basic Metabolic Research; Department... and other collaboratorsCompletedDiabetes Mellitus, Type 2 | Metabolic Disease | Sucrase Isomaltase Deficiency | Sucrose Intolerance CongenitalGreenland
-
AryoGen Pharmed Co.CompletedFactor VII Deficiency | Hemophilia A With Inhibitor | Hemophilia B With Inhibitor | Glanzmann's ThrombastheniaIran, Islamic Republic of
-
Ludwig-Maximilians - University of MunichUnknownBrain Tumor | Pulmonary Embolism | Factor XIII Deficiency | Vascular LesionGermany
-
Jerry Vockley, MD, PhDUltragenyx Pharmaceutical IncNo longer availableBarth Syndrome | Mitochondrial Trifunctional Protein Deficiency | Very Long-chain acylCoA Dehydrogenase (VLCAD) Deficiency | Carnitine Palmitoyltransferase Deficiencies (CPT1, CPT2) | Long-chain Hydroxyacyl-CoA Dehydrogenase Deficiency | Glycogen Storage Disorders | Pyruvate Carboxylase Deficiency... and other conditionsUnited States
-
Eva Morava-KoziczChildren's Hospital of Philadelphia; Seattle Children's HospitalNot yet recruiting
-
Agios Pharmaceuticals, Inc.Active, not recruitingPediatric Pyruvate Kinase Deficiency | Pediatric Hemolytic AnemiaUnited States, Spain, Denmark, Turkey, Netherlands, Czechia, United Kingdom, Germany, Canada, Switzerland
-
Agios Pharmaceuticals, Inc.TerminatedAnemia | Anemia, Hemolytic | Pyruvate Kinase Deficiency | Pyruvate Kinase Deficiency AnemiaUnited States, United Kingdom, Italy, Spain, Netherlands
-
TakedaActive, not recruitingCongenital Protein C DeficiencyJapan
-
Boston Children's HospitalTerminatedFanconi Anemia | Dyskeratosis CongenitaUnited States
-
Mayo ClinicrEVO BiologicsWithdrawnAntithrombin Deficiency Type 2
-
Agios Pharmaceuticals, Inc.RecruitingPediatric Pyruvate Kinase Deficiency | Pediatric Hemolytic AnemiaUnited States, Spain, Germany, Netherlands, Canada, France, Israel, Switzerland, Italy
-
University of OxfordCompletedHealthy | G6PD Normal | G6PD DeficientThailand
-
University of PadovaNot yet recruitingHeart Failure | Iron-deficiency | Vitamin D Deficiency | Heart Failure, Systolic | Heart Failure NYHA Class II | Heart Failure NYHA Class III
-
Emory UniversityChildren's Healthcare of AtlantaTerminatedSickle Cell Disease | Fanconi Anemia | Thalassemia | Severe Congenital Neutropenia | Wiskott-Aldrich Syndrome | Diamond-Blackfan Anemia | Severe Aplastic Anemia | Glanzmann Thrombasthenia | Leukocyte Adhesion Deficiency | Dyskeratosis-congenita | Chediak-Higashi Syndrome | Chronic-granulomatous Disease | Schwachman-Diamond...United States
-
Institut PasteurInstitut Pasteur de la Guyane; Centre Hospitalier Andrée Rosemon de CayenneRecruiting
-
University of Alabama at BirminghamGrifols Biologicals, LLCCompletedCongenital Heart Disease | HypogammaglobulinemiaUnited States
-
OctapharmaRecruitingCongenital Fibrinogen DeficiencyGermany, Czechia
-
OctapharmaCompletedCongenital Fibrinogen Deficiency | AfibrinogenemiaIran, Islamic Republic of, United States, Bulgaria, India, Switzerland, United Kingdom
-
Origin BiosciencesCompletedMolybdenum Cofactor Deficiency | Isolated Sulfite Oxidase DeficiencySpain, Israel, United States, United Kingdom, Canada, Netherlands, Germany, Saudi Arabia, Tunisia, Japan, Italy, Malaysia, Poland, Turkey
-
Masaryk Hospital Krajská zdravotní a.s.CompletedCoagulation Disorder | Multiple Trauma | Coagulation Defect; Acquired | Coagulation Factor DeficiencyCzechia
-
Bio Products LaboratoryTerminatedFactor X DeficiencyUnited Kingdom, United States, Spain, Turkey
-
Bio Products LaboratoryCompletedFactor X DeficiencyUnited States, Turkey, Germany, Spain, United Kingdom
-
Children's National Research InstituteEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsEnrolling by invitationChild Development | Congenital Zika Syndrome | Zika Virus | Congenital InfectionUnited States, Colombia
-
University of California, DavisHelen Keller International; Thrasher Research Fund; Université Polytechnique... and other collaboratorsCompletedDiarrhea | Malaria | Zinc DeficiencyBurkina Faso
-
Ain Shams UniversityUnknownGlucose-6-Phosphate Dehydrogenase DeficiencyEgypt
-
Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Congenital FXIII DeficiencyUnited States
-
BioMarin PharmaceuticalRecruitingHemophilia A With Inhibitor | Hemophilia A With Anti Factor VIIIUnited States, United Kingdom, Taiwan, Israel, Korea, Republic of, South Africa, Brazil, Italy, Germany
-
University of California, San FranciscoCompletedSickle Cell Disease | Hemoglobinopathies | Fanconi Anemia | Thalassemia | Hematologic Malignancies | Immune Deficiency | Nonmalignant Diseases | Genetic Inborn Errors of MetabolismUnited States
-
University of Mississippi, OxfordCompletedMalaria | Glucose 6 Phosphate Dehydrogenase DeficiencyUnited States
-
PATHUniversity of Oxford; Mahidol UniversityCompletedGlucose-6 Phosphate Dehydrogenase DeficiencyThailand
-
PATHEijkman Institute for Molecular BiologyCompletedGlucose-6-Phosphate Dehydrogenase DeficiencyIndonesia
-
Tannhelsetjenestens Kompetansesenter Midt-NorgeCompletedVitamin D Deficiency | Dental Caries | Dental Enamel Hypoplasia
-
University of CatanzaroUnknownAndrogen Receptor Abnormal | Insulin-Like Growth Factor I Deficiency | Insulin Receptor, Defect inItaly
-
University of North Carolina, Chapel HillCompletedMalaria | Iron Deficiency AnemiaUnited States
-
Columbia UniversityEunice Kennedy Shriver National Institute of Child Health and Human Development...Completed
-
Emory UniversityCompletedSickle Cell Disease | Fanconi Anemia | Hurler Syndrome | Chronic Granulomatous Disease | Severe Congenital Neutropenia | Hemophagocytic Lymphohistiocytosis | Wiskott-Aldrich Syndrome | Diamond-Blackfan Anemia | Severe Aplastic Anemia | Glanzmann Thrombasthenia | Shwachman-Diamond Syndrome | Thalassemia Major | Leukocyte... and other conditionsUnited States
-
Rhythm Pharmaceuticals, Inc.CompletedBardet-Biedl Syndrome | POMC Deficiency Obesity | PCSK1 Deficiency Obesity | LEPR Deficiency ObesityUnited States, Australia, Spain, United Kingdom
-
Duke UniversityGrifols Biologicals, LLCCompletedATIII DeficiencyUnited States
-
Maria I. NewNational Center for Research Resources (NCRR); Office of Rare Diseases (ORD)Completed21-hydroxylase DeficiencyUnited States, Brazil
-
Johnson & Johnson Pharmaceutical Research & Development...Completed21-hydroxylase DeficiencyUnited States
-
Khalifa University for Science and TechnologySheikh Khalifa Medical City; Zayed Military Hospital; Cleveland Clinic Abu Dhabi and other collaboratorsUnknownBurnout | Cardiovascular Risk Factor | Immune DeficiencyUnited Arab Emirates