- ICH GCP
- US Clinical Trials Registry
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Clinical Trials on Familial Deafness
Total 2553 results
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AmgenCompletedHomozygous Familial Hypercholesterolemia HoFHIndia
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Regeneron PharmaceuticalsSanofiCompletedHypercholesterolemia | Heterozygous Familial HypercholesterolemiaUnited States, Canada
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Regeneron PharmaceuticalsSanofiCompletedHeterozygous Familial HypercholesterolemiaUnited States, Germany
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Laval UniversityAmgenCompleted
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Akcea TherapeuticsIonis Pharmaceuticals, Inc.WithdrawnHomozygous Familial HypercholesterolemiaCanada
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AmgenCompletedHomozygous Familial HypercholesterolemiaNew Zealand, South Africa, France, United States, Spain, Belgium, Czechia, Italy, Netherlands, Hong Kong, Canada, Lebanon
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Aegerion Pharmaceuticals, Inc.CompletedFamilial Hypercholesterolemia - HomozygousJapan
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Aegerion Pharmaceuticals, Inc.FDA Office of Orphan Products DevelopmentCompletedHomozygous Familial HypercholesterolemiaUnited States, Canada, Italy, South Africa
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National Eye Institute (NEI)CompletedEye Diseases | Exudatiaon | Avascular Retina | Retina Fold | Familial Exudative Vitreoretinopathy | FEVRCanada, United Kingdom
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PfizerCompletedHeterozygous Familial HypercholesterolemiaCanada, Netherlands, United Kingdom, United States, Spain, Poland, Finland, Norway, South Africa, Italy, Bulgaria
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Laval UniversityCompletedHomozygous Familial HypercholesterolemiaCanada
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Regeneron PharmaceuticalsSanofiCompletedHeterozygous Familial HypercholesterolemiaUnited Kingdom, Netherlands, Czech Republic, Norway
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Cerenis Therapeutics, SACompletedHomozygous Familial HypercholesterolemiaUnited States, Canada, Italy, Netherlands, United Kingdom
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Aegerion Pharmaceuticals, Inc.University of Pennsylvania; Doris Duke Charitable FoundationCompletedHomozygous Familial HypercholesterolemiaUnited States
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The University of Western AustraliaNational Health and Medical Research Council, AustraliaUnknownFamilial Hypercholesterolaemia | HypertriglyceridaemiaAustralia
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Pontificia Universidad Catolica de ChileRecruitingMechanical Ventilation Complication | Muscle Weakness or Atrophy | Electrical StimulationsChile
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Federal University of Health Science of Porto AlegreCompletedMuscle Weakness | Muscle Weakness Condition | Neck; AnomalyBrazil
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Umeå UniversityCompleted
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Cairo UniversityRecruitingIntensive Care Unit Acquired WeaknessEgypt
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University of NottinghamUnknown
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Organon and CoCompletedPrimary Hypercholesterolemia | Homozygous Familial Hypercholesterolemia
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HDL TherapeuticsMedStar Heart and Vascular InstituteUnknownHomozygous Familial Hypercholesterolemia | HoFHUnited States
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Mayo ClinicRecruitingStroke | Upper Extremity WeaknessUnited States
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Herzog HospitalJoint Distribution Committee (JDC)Unknown
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PfizerCompletedTransthyretin Familial Amyloid Poluneuropathy
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University of PennsylvaniaUniversity of Amsterdam; University of Cape Town; University of Witwatersrand...RecruitingHomozygous Familial HypercholesterolemiaUnited States, Netherlands, South Africa
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LIB Therapeutics LLCCompletedHomozygous Familial HypercholesterolemiaUnited States, Israel, Norway, South Africa, Turkey, India
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AstraZenecaCompletedHomozygous Familial Hypercholesterolemia (HoFH)Malaysia, Canada, Israel, Netherlands, Taiwan, Belgium, Denmark
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NovartisCompletedMixed Dyslipidemia | Heterozygous Familial HypercholesterolemiaSwitzerland
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The Rogosin InstituteRecruitingHomozygous Familial HypercholesterolemiaUnited States
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The Medicines CompanyCompletedElevated Cholesterol | Heterozygous Familial HypercholesterolemiaUnited States, Canada, Czechia, Denmark, Netherlands, South Africa, Spain, Sweden
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AstraZenecaCompletedHomozygous Familial Hypercholesterolemia (HoFH)Malaysia, Canada, Taiwan, Belgium, Denmark, Israel
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NYU Langone HealthRecruitingHereditary Sensory and Autonomic Neuropathies | Familial Dysautonomia (Riley-Day Syndrome) | Hereditary Sensory and Autonomic Neuropathy 3United States, Israel
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KK Women's and Children's HospitalUnknownEmotional Well-being of First-time Families | Nutritional Health of Mother and Child | Parenting Self-Efficacy for First-time Families | Experience of First-time FamiliesSingapore
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Kirby MayerNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS) and other collaboratorsRecruitingCritical Illness | Muscle Weakness | ICU Acquired Weakness | Post Intensive Care Unit SyndromeUnited States
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VIVE - The Danish Center for Social Science ResearchKFUMs Sociale Arbejde; FDF; KFUM spejderneCompleted
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GCS IHFB Cognacq-JayFondation de FranceCompletedBereaved FamiliesFrance
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National Institute of Diabetes and Digestive and...RecruitingLipodystrophyUnited States
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Chinese Medical AssociationRecruitingAortic Dissection | Family Research | Aortic Dissection, Familial, With or Without Aortic AneurysmChina
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Shenzhen People's HospitalInnovent Biopharmaceutical Co., Ltd.Active, not recruitingEfficacy and Safety | Heterozygous Familial Hypercholesterolemia | PCSK9China
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Danish Headache CenterEUROHEADCompletedHealthy Volunteers | Familial Hemiplegic Migraine Type 1 and 2Denmark
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University of MilanCompleted
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Centro Universitário Augusto MottaUnknownICU Acquired Weakness | Diaphragmatic InjuryBrazil
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M.D. Anderson Cancer CenterNot yet recruitingFamilial Platelet Disorder | HematopoieticUnited States
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Assistance Publique - Hôpitaux de ParisInstitute of Cardiometabolism and Nutrition, FranceCompletedFamilial Hypercholesterolemia - HeterozygousFrance
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Catabasis PharmaceuticalsCompletedHypertriglyceridemia | Hyperlipoproteinemia Type I | Lipoprotein Lipase Deficiency, Familial | Chylomicronemia, FamilialCanada
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Arrowhead PharmaceuticalsActive, not recruitingFamilial ChylomicronemiaKorea, Republic of, Canada, Australia, Singapore, Belgium, Spain, Japan, United States, Austria, Germany, Ireland, Oman, Poland, Israel, New Zealand, Argentina, France, Croatia, Mexico, Serbia, Turkey
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Akcea TherapeuticsCaligorRx, Inc.No longer availableFamilial Chylomicronemia
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Riphah International UniversityCompletedMuscle Weakness ConditionPakistan
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Eli Lilly and CompanyCompletedMuscle WeaknessFrance, United States, Argentina, Australia, Germany, Sweden