- ICH GCP
- US Clinical Trials Registry
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Clinical Trials on Familial Aortopathies in United States
Total 569 results
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Arrowhead PharmaceuticalsActive, not recruitingFamilial ChylomicronemiaKorea, Republic of, Canada, Australia, Singapore, Belgium, Spain, Japan, United States, Austria, Germany, Ireland, Oman, Poland, Israel, New Zealand, Argentina, France, Croatia, Mexico, Serbia, Turkey
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Gmax Biopharm LLC.RecruitingPulmonary Arterial HypertensionUnited States, China
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Allegheny Singer Research Institute (also known...CompletedPulmonary Arterial HypertensionUnited States
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University of PennsylvaniaRegeneron PharmaceuticalsCompleted
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Novartis PharmaceuticalsCompletedFamilial Cold Autoinflammatory SyndromeUnited States, France, Germany
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Immunovia, Inc.CompletedPancreatic Ductal Adenocarcinoma | Familial Pancreatic Cancer | FAMMM - Familial Atypical Mole Malignant Melanoma SyndromeUnited States, Sweden, Canada, Spain, United Kingdom
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National Human Genome Research Institute (NHGRI)Merck Sharp & Dohme LLC; Duke University; University of Massachusetts, WorcesterRecruitingFever | Genetic Diseases | Familial Mediterranean Fever (FMF) | Autoinflammation | Periodic Fever | ROSAH | ALPK1United States
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Geno LLCWithdrawnPulmonary Arterial HypertensionUnited States
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American Medical Association FoundationWithdrawnIdiopathic Pulmonary Arterial Hypertension.United States
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Essentia HealthSt. Luke's Hospital of Duluth; WHITESIDE Institute for Clinical ResearchRecruitingFamilial Hypercholesterolemia | Genetic Disease | Cholesterol, ElevatedUnited States
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University of South FloridaWithdrawnPulmonary Arterial Hypertension | Familial Primary Pulmonary Hypertension | Idiopathic Pulmonary Arterial Hypertension | Primary Pulmonary HypertensionUnited States
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Kyowa Hakko Kirin Pharma, Inc.Completed
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National Institutes of Health Clinical Center (CC)CompletedSecondary Pulmonary Arterial HypertensionUnited States
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Lung Biotechnology PBCCompletedPulmonary Arterial HypertensionUnited States, Belgium, Ireland
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Verve Therapeutics, Inc.Not yet recruitingHypercholesterolemia | Atherosclerotic Cardiovascular Disease | Heterozygous Familial HypercholesterolemiaNew Zealand, United Kingdom
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Verve Therapeutics, Inc.Active, not recruitingHypercholesterolemia | Atherosclerotic Cardiovascular Disease | Heterozygous Familial HypercholesterolemiaNew Zealand, United Kingdom
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Yale UniversityCompleted
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Yale UniversityNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS)CompletedHyperparathyroidism | Hypophosphatemia, FamilialUnited States
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Intellia TherapeuticsRegeneron PharmaceuticalsRecruitingTransthyretin Amyloidosis (ATTR) With CardiomyopathyUnited States, Australia, United Kingdom, New Zealand, Canada
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Novartis PharmaceuticalsCompletedPulmonary Arterial HypertensionAustria, Germany, United States, United Kingdom
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Akcea TherapeuticsIonis Pharmaceuticals, Inc.CompletedFamilial Chylomicronemia Syndrome | Lipoprotein Lipase Deficiency | Hyperlipoproteinemia Type 1United States, Canada, Germany, Israel, Italy, South Africa, Spain, United Kingdom, Brazil, France, Netherlands
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V-Wave LtdRecruitingPulmonary Arterial HypertensionUnited States, Canada, Mexico
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The Cleveland ClinicActive, not recruitingAL Amyloidosis | Amyloidosis | Amyloid Neuropathies, Familial | Amyloid | Transthyretin Amyloidosis | Amyloid Cardiomyopathy | Amyloid - PrimaryUnited States
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GB002, Inc.Not yet recruitingPulmonary Arterial HypertensionUnited States
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Alnylam PharmaceuticalsActive, not recruitingTransthyretin Amyloidosis | Amyloidosis, HereditaryUnited States, Argentina, Australia, Belgium, Brazil, Bulgaria, Canada, Cyprus, France, Germany, Greece, Italy, Japan, Korea, Republic of, Malaysia, Mexico, Netherlands, Portugal, Spain, Sweden, Taiwan, United Kingdom
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National Heart, Lung, and Blood Institute (NHLBI)Completed
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University of PennsylvaniaCompletedPulmonary Arterial HypertensionUnited States
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Vanderbilt University Medical CenterJohns Hopkins UniversityCompletedPulmonary Arterial Hypertension | Idiopathic Pulmonary Arterial Hypertension | Associated Pulmonary Arterial Hypertension | Heritable Pulmonary Arterial HypertensionUnited States
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National Cancer Institute (NCI)Completed
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PfizerCompletedCerebral Amyloid AngiopathyCanada, United States, Netherlands, France, United Kingdom
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ActelionCompletedPulmonary Arterial HypertensionUnited States, France, Netherlands, Italy, Germany, Switzerland, United Kingdom
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Novartis PharmaceuticalsTerminatedPulmonary Arterial HypertensionGermany, Belgium, United Kingdom, United States, Lithuania, Italy, Australia
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Insmed IncorporatedTerminatedPulmonary Arterial HypertensionUnited States
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PfizerTerminatedPulmonary Arterial Hypertension | Pulmonary HypertensionUnited States, Romania, Ukraine
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Bellus Health IncNational Institute of Neurological Disorders and Stroke (NINDS)CompletedStroke | Neurologic Diseases, GeneralUnited States
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United TherapeuticsTerminatedPulmonary Arterial HypertensionUnited States
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Idorsia Pharmaceuticals Ltd.TerminatedPulmonary Arterial HypertensionUnited States, France, Switzerland
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State University of New York - Upstate Medical...TerminatedFamilial Encephalopathy With Neuroserpin Inclusion Bodies | X-linked Mental Retardation | Congenital Vertical Talus | Idiopathic Generalised Epilepsy | Familial DementiaUnited States
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Massachusetts General HospitalNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS)RecruitingX-linked Hypophosphatemia | Hypophosphatemic Rickets | Hypophosphatemic Rickets, X-Linked DominantUnited States
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AlbireoActive, not recruitingProgressive Familial Intrahepatic CholestasisUnited States, Spain, Netherlands, United Kingdom, Turkey, Canada, Italy, Germany, France, Israel, Australia, Belgium, Poland, Saudi Arabia, Sweden
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ActelionCompletedPulmonary Arterial HypertensionUnited States
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Vanderbilt University Medical CenterCompletedLung Diseases | Hypertension | Pulmonary Arterial Hypertension | Familial Primary Pulmonary Hypertension | Primary Pulmonary Hypertension | Estrogens | Tamoxifen | Estrogen Receptor Antagonist | Hormone AntagonistsUnited States
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National Institute of Diabetes and Digestive and...CompletedHypercalcemia | Familial Primary HyperparathyroidismUnited States
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Geisinger ClinicCompletedHypercholesterolemia | Hypercholesterolemia, Familial | Hypercholesteremia in Children | Hyperlipidemia in ChildrenUnited States
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Edward KasaraskisCompletedFamilial Amyotrophic Lateral SclerosisUnited States
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University of Texas Southwestern Medical CenterWithdrawnFamilial HypercholesterolemiaUnited States
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Medical Research Laboratories InternationalTerminatedFamilial HypercholesterolemiaNetherlands, United States, Norway
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ActelionCompletedPulmonary Arterial HypertensionUnited States, France, Netherlands, Italy, Germany, Switzerland, United Kingdom
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ActelionCompletedPulmonary Arterial HypertensionUnited States
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Northwell HealthCompletedPulmonary Arterial Hypertension | Pulmonary Hypertension | Interstitial Lung DiseaseUnited States