- ICH GCP
- US Clinical Trials Registry
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Clinical Trials on Familial Aortopathies in United States
Total 569 results
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Kyowa Kirin, Inc.Kyowa Kirin Co., Ltd.CompletedX-linked HypophosphatemiaNetherlands, United States, United Kingdom, France
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Rajan SaggarUnited TherapeuticsCompletedIdiopathic Pulmonary Fibrosis | Pulmonary Arterial Hypertension | Interstitial Lung DiseaseUnited States
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University of FloridaUnited TherapeuticsTerminatedChronic Obstructive Pulmonary Disease | Pulmonary Arterial HypertensionUnited States
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Daiichi Sankyo, Inc.CompletedHypercholesterolemia | Hyperlipidemia, Familial CombinedUnited States
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VentriPoint Diagnostics Ltd.CompletedPulmonary Arterial HypertensionUnited States, Canada
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Papworth Hospital NHS Foundation TrustRoche Pharma AG; National Institute for Health Research, United KingdomCompletedPulmonary Arterial HypertensionUnited Kingdom
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Baylor College of MedicineThe Methodist Hospital Research Institute; Center for Cell and Gene Therapy...CompletedAcute Myeloid Leukemia | Acute Lymphoblastic Leukemia | Myelodysplastic Syndrome | Chronic Myelogenous Leukemia | Hemophagocytic Lymphohistiocytosis (HLH) | Non Hodgkins Lymphoma | Familial Hemophagocytic Lymphohistiocytosis (FLH) | Viral-associated Hemophagocytic Syndrome (VAHS) | X-linked Lymphoproliferative...United States
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Inozyme PharmaRecruitingGeneralized Arterial Calcification of Infancy | Autosomal Recessive Hypophosphatemic Rickets | Ectonucleotide Pyrophosphatase/Phosphodiesterase1 DeficiencyUnited States, United Kingdom, Canada
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Alnylam PharmaceuticalsActive, not recruitingTransthyretin Amyloidosis (ATTR) With CardiomyopathyUnited States, Australia, Brazil, Bulgaria, France, Italy, Japan, Mexico, Netherlands, Taiwan, United Kingdom, Belgium, Czechia, Denmark, New Zealand, Sweden, Korea, Republic of, Argentina, Chile, Hong Kong, Portugal
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Kyowa Kirin, Inc.Kyowa Kirin Co., Ltd.CompletedX-Linked HypophosphatemiaKorea, Republic of, Canada, United States, Australia, Japan, United Kingdom, Sweden
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United TherapeuticsCompletedPulmonary HypertensionUnited States
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Lung Biotechnology PBCCompletedPulmonary Arterial HypertensionUnited States, Belgium, Czechia, Germany, Ireland, Romania
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Alnylam PharmaceuticalsActive, not recruitingTransthyretin Amyloidosis (ATTR) With CardiomyopathyUnited States, Poland, Argentina, Australia, Belgium, France, Germany, Japan, Netherlands, Portugal, Spain, Sweden, United Kingdom, Canada, Czechia, Denmark, Hungary, Ireland, Norway, Korea, Republic of, Austria, Croatia, Israel, Latvia, Lithuan... and more
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Washington University School of MedicineAlzheimer's Association; Eisai Inc.Not yet recruitingDementia | Alzheimer's Disease | Alzheimer's Disease, FamilialUnited States, Australia, United Kingdom
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Vanderbilt University Medical CenterRecruitingIdiopathic Pulmonary Arterial Hypertension | Heritable Pulmonary Arterial Hypertension | Scleroderma Associated Pulmonary Arterial Hypertension | Appetite Suppressant Associate PAHUnited States
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Aegerion Pharmaceuticals, Inc.CompletedFamilial HypercholesterolemiaUnited States, Canada, Italy, South Africa
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Kastle Therapeutics, LLCIonis Pharmaceuticals, Inc.CompletedCoronary Artery Disease | Heterozygous Familial HypercholesterolemiaUnited States, Canada
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Imperial College LondonUniversity of Sheffield; Medical Research Council; University of Cambridge; National...Active, not recruitingPulmonary Arterial HypertensionUnited Kingdom
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PhaseBio Pharmaceuticals Inc.TerminatedPulmonary Arterial HypertensionUnited States
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PfizerTerminatedFamilial Adenomatous Polyposis (FAP)United States, Spain, Canada, Denmark
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Pfizer's Upjohn has merged with Mylan to form Viatris...CompletedPulmonary Arterial HypertensionUnited States, Czechia, Germany, Israel, France, Australia, Taiwan, Greece, Italy, United Kingdom
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National Health Service, United KingdomCompletedPulmonary Arterial HypertensionUnited Kingdom
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GB002, Inc., a wholly owned subsidiary of Gossamer...CompletedPulmonary Arterial HypertensionUnited States, United Kingdom
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National Institute of Diabetes and Digestive and...RecruitingNon-Medullary Thyroid CancerUnited States
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Inozyme PharmaRecruitingGeneralized Arterial Calcification of Infancy | Autosomal Recessive Hypophosphatemic Rickets | Ectonucleotide Pyrophosphatase/phosphodiesterase1 DeficiencyUnited States, United Kingdom, Canada, France, Germany
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National Human Genome Research Institute (NHGRI)CompletedGeneralized Arterial Calcification of Infancy | Autosomal Recessive Hypophosphatemic Rickets Type2United States
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ActelionActive, not recruitingPulmonary Arterial HypertensionBelgium, Taiwan, Israel, United States, France, China, United Kingdom, Malaysia, Belarus, Canada, Germany, Hungary, Russian Federation, Serbia, Ukraine, Poland
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Kyowa Kirin, Inc.Kyowa Kirin Co., Ltd.CompletedX-linked HypophosphatemiaUnited States, Korea, Republic of, Canada, Japan, France, Denmark
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GlaxoSmithKlineCompleted
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Quadram Institute BioscienceEarlham Institute; Norwich and Norfolk University Hospital; Quadram Institute...Enrolling by invitationMicrobial Transfers in the Gut of Multigenerational Families and Stability and Adaptation of These Microbes After ColonizationUnited Kingdom
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Imperial College LondonCompletedIdiopathic Pulmonary Arterial HypertensionUnited Kingdom
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Vanderbilt University Medical CenterNational Heart, Lung, and Blood Institute (NHLBI)RecruitingIdiopathic Pulmonary Arterial Hypertension | Heritable Pulmonary Arterial Hypertension | Pulmonary Arterial Hypertension Associated With Connective Tissue DiseaseUnited States
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Vanderbilt University Medical CenterEnrolling by invitationFamilial Adenomatous PolyposisUnited States
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M.D. Anderson Cancer CenterNational Cancer Institute (NCI)CompletedFamilial Adenomatous PolyposisUnited States
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National Cancer Institute (NCI)RecruitingFamilial Adenomatous Polyposis | Colorectal Carcinoma | Attenuated Familial Adenomatous Polyposis | Duodenal CarcinomaUnited States, Puerto Rico
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ActelionCompletedPulmonary Arterial HypertensionUnited States, United Kingdom, Ireland, Germany, Austria, France, Norway, Portugal, Sweden, Switzerland
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Bastiaan DriehuysAmerican Heart AssociationNot yet recruitingConnective Tissue Diseases | Pulmonary Arterial Hypertension | Idiopathic Pulmonary Arterial Hypertension | Pulmonary Arterial Hypertension Associated With Connective Tissue Disease (Disorder)United States
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Aria CV, IncRecruitingPulmonary Arterial Hypertension | Pulmonary Hypertension | Right Heart DysfunctionUnited States
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University of NottinghamUniversity College, London; Newcastle University; University of ManchesterUnknownFamilial HypercholesterolemiaUnited Kingdom
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ActelionCompletedPulmonary Arterial HypertensionUnited States
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Weill Medical College of Cornell UniversityMuscular Dystrophy AssociationCompletedFamilial Amyotrophic Lateral SclerosisUnited States, Germany, Italy, Sweden
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University of ExeterWithdrawnHealthy | Lipodystrophy, Familial PartialUnited Kingdom
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United TherapeuticsCompletedPulmonary Arterial HypertensionUnited States, Australia, Hungary, Bulgaria, Czechia, Poland, Romania, Serbia, Spain
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Washington University School of MedicineHoffmann-La Roche; National Institute on Aging (NIA); Alzheimer's AssociationTerminatedDementia | Alzheimers Disease | Alzheimers Disease, FamilialUnited States, France, Spain, Ireland, Canada, Australia, Puerto Rico, United Kingdom
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United TherapeuticsCompletedPulmonary Arterial HypertensionUnited States
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Ionis Pharmaceuticals, Inc.ALS Association; Muscular Dystrophy AssociationCompletedFamilial Amyotrophic Lateral SclerosisUnited States
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Inozyme PharmaRecruitingGeneralized Arterial Calcification of Infancy | Autosomal Recessive Hypophosphatemic Rickets | Ectonucleotide Pyrophosphatase/phosphodiesterase1 DeficiencyUnited States, United Kingdom
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University of Wisconsin, MadisonUnited TherapeuticsTerminatedPulmonary Arterial Hypertension | Right-Sided Heart FailureUnited States
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Indiana UniversityCompletedChronic Kidney DiseaseUnited States
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Imperial College London Diabetes CentreUnknownFamilial HypercholesterolemiaUnited Arab Emirates