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Clinical Trials on Familial Hemophagocytic Lymphohistiocytosis in South Africa
Total 139 results
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Bellerophon Pulse TechnologiesWorldwide Clinical TrialsWithdrawnPulmonary Arterial HypertensionUnited States, Canada
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Regeneron PharmaceuticalsCompletedGenetic Diseases, Inborn | Familial Cold Autoinflammatory Syndrome (FCAS) | Familial Cold Urticaria | Muckle-Wells Syndrome (MWS)United States
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ActelionCompletedPulmonary Arterial HypertensionUnited States, Australia, Belarus, China, Czechia, France, Germany, Hungary, India, Israel, Italy, Mexico, Netherlands, Poland, Russian Federation, Serbia, South Africa, Spain, Ukraine
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Pfizer's Upjohn has merged with Mylan to form Viatris...TerminatedPulmonary Arterial HypertensionHong Kong, Malaysia, Serbia, United States, Germany, Latvia, Australia, Croatia, Greece, Czechia, Bosnia and Herzegovina, Singapore, Belgium, Israel, Mexico, Poland, Romania, Russian Federation, South Africa, Spain, Thailand, Turkey, Ukrai...
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PfizerTerminatedPulmonary Arterial Hypertension | Pulmonary HypertensionUnited States, Bulgaria, Argentina, Chile, China, Colombia, Costa Rica, Czech Republic, Dominican Republic, Guatemala, India, Malaysia, Mexico, Peru, Philippines, Romania, Russian Federation, Saudi Arabia, Serbia, Slovakia, South... and more
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Novartis PharmaceuticalsTerminatedPulmonary Arterial HypertensionGermany, Belgium, United Kingdom, United States, Lithuania, Italy, Australia
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Amryt PharmaRecruitingHomozygous Familial HypercholesterolemiaItaly, United States, Argentina, Canada, France, Greece, Netherlands, United Kingdom
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Eidos Therapeutics, a BridgeBio companyCompletedFamilial ATTR-CM (ATTRm-CM, or FAC) | Wild-type ATTR-CM (ATTRwt-CM)United States
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Arrowhead PharmaceuticalsActive, not recruitingFamilial ChylomicronemiaKorea, Republic of, Canada, Australia, Singapore, Belgium, Spain, Japan, United States, Austria, Germany, Ireland, Oman, Poland, Israel, New Zealand, Argentina, France, Croatia, Mexico, Serbia, Turkey
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PfizerTerminatedPulmonary Arterial Hypertension | Pulmonary HypertensionUnited States, Bulgaria, Argentina, Chile, China, Colombia, Czech Republic, India, Malaysia, Mexico, Peru, Romania, Russian Federation, Serbia, South Africa, Thailand, Turkey, Ukraine
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Novartis PharmaceuticalsCompletedPulmonary Arterial HypertensionGermany, Belgium, United States, Lithuania, United Kingdom, Italy, Australia
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Acceleron Pharma Inc. (a wholly owned subsidiary...CompletedPulmonary Arterial HypertensionSpain, United States, Israel, Australia, Germany, United Kingdom, France, Brazil
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Aerovate TherapeuticsRecruitingPulmonary Arterial HypertensionUnited States, Belgium, Italy, Spain, Australia, Canada, China, Singapore, France, United Kingdom, Latvia, Mexico, Argentina, Israel, South Africa, Chile, Poland, Germany, Portugal, Colombia
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Novartis PharmaceuticalsCompletedPulmonary Arterial HypertensionSpain, Germany, Poland, United Kingdom, Netherlands, Argentina, United States
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SanofiRegeneron PharmaceuticalsCompletedHypercholesterolaemiaCzechia, France, Denmark, Netherlands, Austria, Mexico, Spain, United States, Argentina, Brazil, Bulgaria, Canada, Finland, Hungary, Italy, Lebanon, Norway, Poland, Russian Federation, Slovenia, South Africa, Sweden, Taiwan, Turkey
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Kastle Therapeutics, LLCIonis Pharmaceuticals, Inc.CompletedMetabolic Diseases | Congenital Abnormalities | Infant, Newborn, Diseases | Genetic Diseases, Inborn | Dyslipidemias | Metabolism, Inborn Errors | Lipid Metabolism Disorders | Hypercholesterolemia | Hyperlipidemias | Hyperlipoproteinemias | Lipid Metabolism, Inborn Errors | Hyperlipoproteinemia Type II | Metabolic... and other conditionsUnited States, Canada, Brazil, Taiwan, Singapore, South Africa, United Kingdom
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Aria CV, IncRecruitingPulmonary Arterial Hypertension | Pulmonary Hypertension | Right Heart DysfunctionUnited States
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Lung Biotechnology PBCTerminatedPulmonary Arterial HypertensionUnited States, Israel
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Washington University School of MedicineAlzheimer's Association; Eisai Inc.Not yet recruitingDementia | Alzheimer's Disease | Alzheimer's Disease, FamilialUnited States, Australia, United Kingdom
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ActelionRecruitingPulmonary Arterial HypertensionUnited States, Korea, Republic of, Spain, Malaysia, China, Hungary, Mexico, Poland, Australia, Austria, Brazil, Canada, Colombia, France, Israel, Philippines, Portugal, Russian Federation, South Africa, Thailand, Ukraine, Vietnam, F...
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Alnylam PharmaceuticalsCompletedFamilial Amyloidotic Cardiomyopathy (FAC)United States, France, Spain, United Kingdom, Belgium, Brazil
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Kyowa Kirin, Inc.Kyowa Kirin Co., Ltd.CompletedX-Linked HypophosphatemiaKorea, Republic of, Canada, United States, Australia, Japan, United Kingdom, Sweden
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GB002, Inc., a wholly owned subsidiary of Gossamer...CompletedPulmonary Arterial HypertensionUnited States, United Kingdom
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SanofiRegeneron PharmaceuticalsCompletedHypercholesterolemiaUnited States, Austria, Canada, Czech Republic, Denmark, France, Israel, Netherlands, Norway, Russian Federation, South Africa, Spain, Sweden, United Kingdom
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Western Sydney Local Health DistrictRecruitingFamilial Adenomatous PolyposisAustralia
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Eiger BioPharmaceuticalsCompletedPulmonary Arterial HypertensionUnited States, Canada
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Pfizer's Upjohn has merged with Mylan to form Viatris...CompletedPulmonary Arterial HypertensionUnited States, Czechia, Germany, Israel, France, Australia, Taiwan, Greece, Italy, United Kingdom
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Eiger BioPharmaceuticalsTerminatedPulmonary Arterial HypertensionUnited States, Canada
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Aires Pharmaceuticals, Inc.TerminatedPulmonary Arterial HypertensionUnited States, Australia, Hungary
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UK Kidney AssociationRecruitingVasculitis | AL Amyloidosis | Tuberous Sclerosis | Fabry Disease | Cystinuria | Focal Segmental Glomerulosclerosis | IgA Nephropathy | Bartter Syndrome | Pure Red Cell Aplasia | Membranous Nephropathy | Atypical Hemolytic Uremic Syndrome | Autosomal Dominant Polycystic Kidney Disease | Cystinosis | Nephronophthisis | BK Nephropathy and other conditionsUnited Kingdom
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Aerovate TherapeuticsRecruitingPulmonary Arterial HypertensionUnited States, Belgium, Italy, Spain, Australia, Canada, China, Poland, Singapore, Argentina, United Kingdom, France, Israel, Latvia, Austria, Mexico, Puerto Rico, Sweden, South Africa, Netherlands, Chile, Germany, Greece, Portugal, Cze... and more
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ActelionCompletedPulmonary Arterial HypertensionUnited States, United Kingdom, Belarus, Argentina, Australia, Austria, Belgium, Bulgaria, Canada, Chile, China, Colombia, Croatia, France, Germany, Hong Kong, Hungary, India, Israel, Italy, Malaysia, Mexico, Netherlands, Norway, Peru, Poland and more
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United TherapeuticsCompletedPulmonary Arterial HypertensionUnited States, Australia, Bulgaria, Czechia, Hungary, Poland, Romania, Serbia, Slovakia, Spain
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ActelionActive, not recruitingPulmonary Arterial Hypertension (PAH) (WHO Group 1 PH)United States, Japan, Taiwan, Turkey, Canada, China, Germany, Spain, Italy, Malaysia, Hungary, Russian Federation, Brazil, Australia, Bulgaria, Czechia, Mexico, Poland, South Africa
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ActelionCanadian Heart Research CentreCompletedPulmonary Arterial HypertensionUnited States, Puerto Rico
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Acceleron Pharma, Inc., a wholly-owned subsidiary...Active, not recruitingPulmonary Arterial HypertensionFrance, Germany, United States, Australia, Belgium, Canada, Israel, Italy, Mexico, Netherlands, Spain, United Kingdom
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PfizerTerminatedPulmonary Arterial HypertensionUnited States, Netherlands, Canada, Belgium, France, Germany, Italy, Spain, United Kingdom, Australia, Poland, Austria, Brazil, Israel, Argentina, Mexico
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Aires Pharmaceuticals, Inc.TerminatedPulmonary Arterial HypertensionUnited States, Australia, Hungary
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Washington University School of MedicineHoffmann-La Roche; National Institute on Aging (NIA); Alzheimer's AssociationTerminatedDementia | Alzheimers Disease | Alzheimers Disease, FamilialUnited States, France, Spain, Ireland, Canada, Australia, Puerto Rico, United Kingdom
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Merck Sharp & Dohme LLCActive, not recruitingHypercholesterolemia | Familial HypercholesterolemiaColombia, Israel, Taiwan, United States, Argentina, China, Germany, Italy, Japan, Korea, Republic of, Mexico, South Africa, Spain, Turkey
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Washington University School of MedicineEli Lilly and Company; Hoffmann-La Roche; Avid Radiopharmaceuticals; National Institute... and other collaboratorsCompletedDementia | Alzheimers Disease | Alzheimers Disease, FamilialUnited States, Canada, France, Spain, Ireland, Australia, Puerto Rico, United Kingdom
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Keros Therapeutics, Inc.RecruitingPulmonary Arterial HypertensionUnited States, Australia, Germany, Korea, Republic of, Poland, Portugal, Spain, Taiwan, United Kingdom
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ActelionCompletedPulmonary Arterial HypertensionUnited States, United Kingdom, Taiwan, Finland, Canada, Belarus, Belgium, Argentina, Australia, China, Colombia, Croatia, Germany, Hong Kong, India, Israel, Italy, Malaysia, Netherlands, Poland, Russian Federation, South Africa, Tha... and more
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Lung Biotechnology PBCCompletedPulmonary Arterial HypertensionUnited States, Israel
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ActelionRecruitingPulmonary Arterial HypertensionBelgium, United States, Italy, Canada, Taiwan, Greece, China, Korea, Republic of, Germany, Israel, Austria, Russian Federation, Australia, Thailand, United Kingdom, Brazil, Spain, Ukraine, Bulgaria, Colombia, Mexico, Turkey, Vietnam, ... and more
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ActelionTerminatedPulmonary Arterial HypertensionUnited States
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BayerXcenda, LLCActive, not recruitingPulmonary Arterial HypertensionUnited States, Puerto Rico
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United TherapeuticsLung Biotechnology PBCRecruiting
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ActelionCompletedPulmonary Arterial HypertensionUnited States
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Gilead SciencesTerminatedPulmonary Arterial HypertensionUnited States, Israel, Australia, Canada, Mexico, Spain, Belgium, Austria, Germany, United Kingdom