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Clinical Trials on Familial Amyloid Polyneuropathies
Total 5649 results
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University Hospital, MontpellierCompleted
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Universitair Ziekenhuis BrusselRecruitingAmyloidosis | PolyneuropathyBelgium
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Kyoto UniversityOsaka University; Mie University; Tokushima University; Tokyo Metropolitan Geriatric... and other collaboratorsCompletedFamilial Alzheimer Disease (FAD) | PSEN1 MutationJapan
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University of PennsylvaniaWashington University School of MedicineCompleted
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Institute of Health Information and Statistics...Centre of Cardiovascular and Transplantation Surgery, Czech Republic; The Central... and other collaboratorsRecruitingFamilial HypercholesterolaemiaCzechia
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Vanderbilt University Medical CenterRecruitingIdiopathic Pulmonary Fibrosis | Familial Pulmonary Fibrosis | Familial Interstitial PneumoniaUnited States
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Fundación Hipercolesterolemia FamiliarInstituto de Salud Carlos III; Fundación Centro Nacional de Investigaciones...RecruitingFamilial HypercholesterolaemiaSpain
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Kastle Therapeutics, LLCCompletedHypercholesterolemia | Heterozygous FamilialUnited States, Italy, Poland, Ukraine, United Kingdom, Germany, Hong Kong, Taiwan, Spain, Argentina, Belgium, Israel, Malaysia, South Africa, Turkey, Netherlands, Korea, Republic of, Canada, New Zealand, Russian Federation, Brazil, Austral... and more
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Kastle Therapeutics, LLCIonis Pharmaceuticals, Inc.CompletedHypercholesterolemia, FamilialUnited States, Netherlands
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AmgenCompleted
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Otsuka Pharmaceutical, Inc., PhilippinesCompleted
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RwHealthNorthern Care Alliance NHS Foundation Trust; Alnylam PharmaceuticalsNot yet recruitingHereditary Amyloidosis | Guillain-Barre Syndrome | Chronic Inflammatory Demyelinating PolyneuropathyUnited Kingdom
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First Affiliated Hospital Xi'an Jiaotong UniversityRecruitingHomozygous Familial HypercholesterolemiaChina
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Beijing Suncadia Pharmaceuticals Co., LtdNot yet recruitingHomozygous Familial Hypercholesterolemia
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Organon and CoCompletedHypercholesterolemia | Heterozygous Familial Hypercholesterolemia
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Novartis PharmaceuticalsActive, not recruitingFamilial Hypercholesterolemia - HeterozygousUnited States, Germany, South Africa, Greece, Italy, Czechia, Taiwan, Slovakia, Turkey, France, Russian Federation, Canada, Spain, Jordan, Switzerland, Hungary, Poland, Netherlands, Norway, United Kingdom, Lebanon, Argentina, Brazil, ... and more
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Arrowhead PharmaceuticalsActive, not recruitingHomozygous Familial HypercholesterolemiaAustralia, Canada, United States, South Africa
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Novartis PharmaceuticalsCompletedHypercholesterolemia | Heterozygous Familial HypercholesterolemiaJapan
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AkesoAD Pharmaceuticals Co., Ltd.CompletedHomozygous Familial HypercholesterolemiaChina
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AmgenCompletedHeterozygous Familial HypercholesterolemiaUnited States, Canada, Italy, Norway, Belgium, Turkey, Australia, New Zealand, Austria, Czechia, South Africa, Poland, Spain, Switzerland, Netherlands, Taiwan, Finland, Brazil, Portugal, Slovenia, Russian Federation, Hungary, United... and more
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Akcea TherapeuticsIonis Pharmaceuticals, Inc.TerminatedFamilial Partial LipodystrophyUnited States, Netherlands, Belgium, Brazil, Canada, Germany, Russian Federation
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Regeneron PharmaceuticalsSanofiCompletedHomozygous Familial HypercholesterolemiaUnited States, South Africa, Canada, Greece, Japan, Ukraine, Austria, Czechia, France, Germany, Italy, Taiwan, Turkey
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Regeneron PharmaceuticalsCompletedHomozygous Familial HypercholesterolemiaUnited States, Netherlands, Australia, Austria, Canada, France, Greece, Italy, Japan, South Africa, Ukraine
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Austrian Academic Institute for Clinical NutritionMedical University of ViennaCompletedHeterozygous Familial HypercholesterolemiaAustria
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Aegerion Pharmaceuticals, Inc.WithdrawnHomozygous Familial Hypercholesterolemia
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Merck Sharp & Dohme LLCCompletedHeterozygous Familial Hypercholesterolemia (HeFH)
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Cerenis Therapeutics, SACompleted
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Novartis PharmaceuticalsRecruitingHypercholesterolaemia | Familial HypercholesterolaemiaJapan
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AmgenCompletedFamilial HypercholesterolemiaCanada, Italy, Norway, Belgium, United States, Turkey, Australia, Austria, South Africa, Poland, Switzerland, Spain, Portugal, Slovenia, Brazil, Russian Federation, Hungary, United Kingdom, Colombia, Czechia, Netherlands, Greece, Ma...
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Regeneron PharmaceuticalsCompletedHomozygous Familial HypercholesterolemiaUnited States, Netherlands, South Africa, Australia, Austria, Canada, Czechia, France, Greece, Italy, Japan, Ukraine
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Shanghai Junshi Bioscience Co., Ltd.CompletedHeterozygous Familial HypercholesterolemiaChina
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Mirum Pharmaceuticals, Inc.CompletedProgressive Familial Intrahepatic Cholestasis (PFIC)United States, United Kingdom, Poland, France
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Daniel GaudetUltragenyx Pharmaceutical IncActive, not recruitingSafety and Effectiveness of Evinacumab for the Treatment of Homozygous Familial HypercholesterolemiaHomozygous Familial HypercholesterolemiaCanada
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Innovent Biologics (Suzhou) Co. Ltd.Completed
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Amryt PharmaActive, not recruitingHomozygous Familial Hypercholesterolaemia (HoFH)Germany, Israel, Italy, Saudi Arabia, Spain, Tunisia
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AkesoAD Pharmaceuticals Co., Ltd.CompletedHeterozygous Familial HypercholesterolemiaChina
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Nantes University HospitalCompletedFamilial HypobetalipoproteinemiaFrance
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Nantes University HospitalCompletedStudy of cardiovAscular Contrasted Phenotypes in Patients With FamIliaI hypercholesteRolemia (SAFIR)Homozygous Familial HypercholesterolemiaFrance
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The Medicines CompanyCompletedHomozygous Familial HypercholesterolemiaUnited States, Netherlands, South Africa
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Regeneron PharmaceuticalsCompletedHomozygous Familial HypercholesterolemiaUnited States, Netherlands, Canada
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Madrigal Pharmaceuticals, Inc.CompletedHeterozygous Familial HypercholesterolemiaDenmark
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Central South UniversityCompletedHomozygous Familial HypercholesterolemiaChina
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CymaBay Therapeutics, Inc.CompletedHomozygous Familial HypercholesterolemiaCanada, France, Netherlands, Norway
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Merck Sharp & Dohme LLCTerminatedHyperlipoproteinemia Type II | Homozygous Familial Hypercholesterolemia
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David J. KopskyPrincess Beatrix Muscle Foundation; Dr. C.J. Vaillant FondsCompletedChronic Idiopathic Axonal PolyneuropathyNetherlands
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University of Sao PauloPfizerCompletedPain | Neuropathic Pain | PolyneuropathyBrazil
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Odense University HospitalCompleted
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Umeå UniversityCompleted
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Organon and CoCompletedPrimary Hypercholesterolemia | Homozygous Familial Hypercholesterolemia
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HDL TherapeuticsMedStar Heart and Vascular InstituteUnknownHomozygous Familial Hypercholesterolemia | HoFHUnited States