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Clinical Trials on Familial Amyloid Polyneuropathy
Total 5393 results
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Shenzhen People's HospitalInnovent Biopharmaceutical Co., Ltd.Active, not recruitingEfficacy and Safety | Heterozygous Familial Hypercholesterolemia | PCSK9China
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Danish Headache CenterEUROHEADCompletedHealthy Volunteers | Familial Hemiplegic Migraine Type 1 and 2Denmark
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Assistance Publique - Hôpitaux de ParisInstitute of Cardiometabolism and Nutrition, FranceCompletedFamilial Hypercholesterolemia - HeterozygousFrance
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Catabasis PharmaceuticalsCompletedHypertriglyceridemia | Hyperlipoproteinemia Type I | Lipoprotein Lipase Deficiency, Familial | Chylomicronemia, FamilialCanada
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University of MichiganNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)Active, not recruitingObesity | Polyneuropathies | Bariatric Surgery CandidateUnited States
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Washington University School of MedicineNational Institute of Neurological Disorders and Stroke (NINDS)WithdrawnPolyneuropathy | HIV-associated NeuropathyUnited States
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Akcea TherapeuticsRecruitingPregnancy | Hereditary Transthyretin-mediated Amyloidosis With PolyneropathyUnited States
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Virginia Commonwealth UniversityNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); University... and other collaboratorsUnknown
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Università degli Studi di BresciaUnknownCritical Illness Myopathy | Critical Illness PolyneuropathyItaly
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The Rogosin InstituteRecruitingHomozygous Familial HypercholesterolemiaUnited States
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The Medicines CompanyCompletedElevated Cholesterol | Heterozygous Familial HypercholesterolemiaUnited States, Canada, Czechia, Denmark, Netherlands, South Africa, Spain, Sweden
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AstraZenecaCompletedHomozygous Familial Hypercholesterolemia (HoFH)Malaysia, Canada, Taiwan, Belgium, Denmark, Israel
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Apurano Pharmaceuticals GmbHRecruitingPain | Diabetes | Diabetic Neuropathies | Chronic Pain | Peripheral Neuropathy | Pain, Chronic | Chronic Pain Syndrome | Diabetic Polyneuropathy | Pain Syndrome | Peripheral Neuralgia | Peripheral Neuropathy With Type 2 DiabetisGermany
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NYU Langone HealthRecruitingHereditary Sensory and Autonomic Neuropathies | Familial Dysautonomia (Riley-Day Syndrome) | Hereditary Sensory and Autonomic Neuropathy 3United States, Israel
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The Hospital for Sick ChildrenCompletedFamilial or Severe HypercholesterolemiaCanada
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KK Women's and Children's HospitalUnknownEmotional Well-being of First-time Families | Nutritional Health of Mother and Child | Parenting Self-Efficacy for First-time Families | Experience of First-time FamiliesSingapore
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Centre Hospitalier Universitaire de NiceCompletedPolyradiculoneuropathy, Chronic Inflammatory DemyelinatingFrance
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Maastricht UniversityUnknownDiabetes Mellitus | PolyneuropathiesNetherlands
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Shenzhen People's HospitalRecruitingEvaluate the Efficacy and Safety of IBI306 in Subjects With Homozygous Familial HypercholesterolemiaLipid Metabolism Disorders | Familial Hypercholesterolemia - Homozygous | Proprotein Convertase Subtilisin/Kexin 9China
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Mayo ClinicCompleted
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Arrowhead PharmaceuticalsCompletedHypertriglyceridemia | Familial ChylomicronemiaAustralia, Canada, New Zealand
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Apurano Pharmaceuticals GmbHRecruitingPain | Diabetes | Diabetic Neuropathies | Chronic Pain | Peripheral Neuropathy | Pain, Chronic | Chronic Pain Syndrome | Diabetic Polyneuropathy | Pain Syndrome | Peripheral Neuralgia | Peripheral Neuropathy With Type 2 DiabetisGermany
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POLYSAN Scientific & Technological Pharmaceutical...CompletedDiabetic NeuropathiesRussian Federation
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Sumitomo Pharma Co., Ltd.CompletedDiabetic NeuropathyCanada
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M.D. Anderson Cancer CenterNot yet recruitingFamilial Platelet Disorder | HematopoieticUnited States
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Arrowhead PharmaceuticalsActive, not recruitingFamilial ChylomicronemiaKorea, Republic of, Canada, Australia, Singapore, Belgium, Spain, Japan, United States, Austria, Germany, Ireland, Oman, Poland, Israel, New Zealand, Argentina, France, Croatia, Mexico, Serbia, Turkey
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Akcea TherapeuticsCaligorRx, Inc.No longer availableFamilial Chylomicronemia
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University Medical Center GroningenAstraZenecaCompletedHeart Failure | Cardiomyopathy, Familial | Phospholamban R14del CardiomyopathyNetherlands
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Mario Negri Institute for Pharmacological ResearchFondazione TelethonCompleted
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REGENXBIO Inc.Active, not recruitingHomozygous Familial Hypercholesterolemia (HoFH)United States, Canada, Netherlands
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Karo Bio ABTerminatedHeterozygous Familial Hypercholesterolaemia
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Ionis Pharmaceuticals, Inc.Akcea TherapeuticsCompletedFamilial Chylomicronemia SyndromeUnited States, Israel, Spain, Italy, United Kingdom, Netherlands, Canada, Hungary, Sweden, France, Norway, Portugal, Slovakia
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Ionis Pharmaceuticals, Inc.Active, not recruitingFamilial Chylomicronemia SyndromeUnited States, Canada, Sweden
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Institute of Cardiometabolism and Nutrition, FranceAmgenUnknownFamilial Hypercholesterolemia - HeterozygousFrance
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Oslo University HospitalDanish Pain Research Center; University Hospital of North Norway; University... and other collaboratorsRecruitingNeuropathic Pain | Polyneuropathies | Genetic PredispositionNorway
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Neuroscience Technologies SLP, BarcelonaInstitut National de la Santé Et de la Recherche Médicale, France; University... and other collaboratorsUnknownPeripheral Nervous System Diseases | Neuralgia | Polyneuropathies | Peripheral Nerve Injuries | Chemotherapy EffectsSpain
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University of TriestePfizerUnknownAmyloid CardiomyopathyItaly
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Mayo ClinicUniversity of California, San Francisco; University of MinnesotaCompletedFamilial Pancreatic CancerUnited States
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Beth Israel Deaconess Medical CenterNational Institute of Neurological Disorders and Stroke (NINDS)CompletedAmyotrophic Lateral Sclerosis | Muscular Dystrophy | Radiculopathy | Trauma Injury | Orthopedic Disorder | Myopathy | Polyneuropathy and MononeuropathiesUnited States
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Fundació Institut de Recerca de l'Hospital de la...Hospital Clinic of BarcelonaCompletedFamilial Hypocalciuric HypercalcemiaSpain
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Universität des SaarlandesCompleted
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University of KielUnknownNeuropathic Pain | Peripheral Nerve Injury | Polyneuropathy
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Alnylam PharmaceuticalsRecruitingPolyneuropathy | Hereditary Transthyretin-mediated (hATTR) AmyloidosisNetherlands, Spain, United States, Germany, France, Italy, Portugal
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Azienda Socio Sanitaria Territoriale degli Spedali...Active, not recruitingCritical Illness Myopathy | Neuromuscular Blockade | Critical Illness Polyneuropathy | Weakness Due to DiseaseItaly
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NYU Langone HealthNot yet recruitingFamilial DysautonomiaUnited States
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NYU Langone HealthNot yet recruiting
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Regeneron PharmaceuticalsTerminatedFamilial Partial Lipodystrophy | Metabolic AbnormalitiesUnited States, France, Spain, Turkey
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NYU Langone HealthCompletedFamilial DysautonomiaUnited States
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Akcea TherapeuticsIonis Pharmaceuticals, Inc.CompletedFamilial Partial LipodystrophyUnited States
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University of MichiganAvailable