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Clinical Trials on Familial Deafness
Total 2599 results
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Fundación Hipercolesterolemia FamiliarInstituto de Salud Carlos III; Fundación Centro Nacional de Investigaciones...RecruitingFamilial HypercholesterolaemiaSpain
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Kastle Therapeutics, LLCCompletedHypercholesterolemia | Heterozygous FamilialUnited States, Italy, Poland, Ukraine, United Kingdom, Germany, Hong Kong, Taiwan, Spain, Argentina, Belgium, Israel, Malaysia, South Africa, Turkey, Netherlands, Korea, Republic of, Canada, New Zealand, Russian Federation, Brazil, Austral... and more
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Kastle Therapeutics, LLCIonis Pharmaceuticals, Inc.CompletedHypercholesterolemia, FamilialUnited States, Netherlands
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University of MelbourneEnrolling by invitationICU Acquired Weakness | Intensive Care Unit Syndrome | Intensive Care Unit Acquired Weakness | Post Intensive Care Unit Syndrome | Post Intensive Care SyndromeAustralia
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Novartis PharmaceuticalsRecruitingHypercholesterolaemia | Familial HypercholesterolaemiaJapan
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AmgenCompletedFamilial HypercholesterolemiaCanada, Italy, Norway, Belgium, United States, Turkey, Australia, Austria, South Africa, Poland, Switzerland, Spain, Portugal, Slovenia, Brazil, Russian Federation, Hungary, United Kingdom, Colombia, Czechia, Netherlands, Greece, Ma...
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Regeneron PharmaceuticalsCompletedHomozygous Familial HypercholesterolemiaUnited States, Netherlands, South Africa, Australia, Austria, Canada, Czechia, France, Greece, Italy, Japan, Ukraine
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Shanghai Junshi Bioscience Co., Ltd.CompletedHeterozygous Familial HypercholesterolemiaChina
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Mirum Pharmaceuticals, Inc.CompletedProgressive Familial Intrahepatic Cholestasis (PFIC)United States, United Kingdom, Poland, France
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Daniel GaudetUltragenyx Pharmaceutical IncActive, not recruitingSafety and Effectiveness of Evinacumab for the Treatment of Homozygous Familial HypercholesterolemiaHomozygous Familial HypercholesterolemiaCanada
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Innovent Biologics (Suzhou) Co. Ltd.Completed
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Amryt PharmaActive, not recruitingHomozygous Familial Hypercholesterolaemia (HoFH)Germany, Israel, Italy, Saudi Arabia, Spain, Tunisia
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AkesoAD Pharmaceuticals Co., Ltd.CompletedHeterozygous Familial HypercholesterolemiaChina
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Nantes University HospitalCompletedFamilial HypobetalipoproteinemiaFrance
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Nantes University HospitalCompletedStudy of cardiovAscular Contrasted Phenotypes in Patients With FamIliaI hypercholesteRolemia (SAFIR)Homozygous Familial HypercholesterolemiaFrance
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The Medicines CompanyCompletedHomozygous Familial HypercholesterolemiaUnited States, Netherlands, South Africa
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Regeneron PharmaceuticalsCompletedHomozygous Familial HypercholesterolemiaUnited States, Netherlands, Canada
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Madrigal Pharmaceuticals, Inc.CompletedHeterozygous Familial HypercholesterolemiaDenmark
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Central South UniversityCompletedHomozygous Familial HypercholesterolemiaChina
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CymaBay Therapeutics, Inc.CompletedHomozygous Familial HypercholesterolemiaCanada, France, Netherlands, Norway
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Merck Sharp & Dohme LLCTerminatedHyperlipoproteinemia Type II | Homozygous Familial Hypercholesterolemia
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SensorionRecruitingSensorineural Hearing Loss, Bilateral | Congenital Deafness | AUNB1 | DFNB1A | DFNB9 | OTOF Gene Mutation | GJB2 Gene MutationFrance
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Zhuan ZhangRecruiting
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National Eye Institute (NEI)CompletedRetinitis Pigmentosa | Usher Syndrome | Retinitis Pigmentosa Syndromic | Congenital Deafness | Retinitis Pigmentosa and DeafnessUnited States
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First Affiliated Hospital Xi'an Jiaotong UniversityRecruitingHomozygous Familial HypercholesterolemiaChina
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Beijing Suncadia Pharmaceuticals Co., LtdNot yet recruitingHomozygous Familial Hypercholesterolemia
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Novartis PharmaceuticalsCompletedHypercholesterolemia | Heterozygous Familial HypercholesterolemiaJapan
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Novartis PharmaceuticalsActive, not recruitingFamilial Hypercholesterolemia - HeterozygousUnited States, Germany, South Africa, Greece, Italy, Czechia, Taiwan, Slovakia, Turkey, France, Russian Federation, Canada, Spain, Jordan, Switzerland, Hungary, Poland, Netherlands, Norway, United Kingdom, Lebanon, Argentina, Brazil, ... and more
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Organon and CoCompletedHypercholesterolemia | Heterozygous Familial Hypercholesterolemia
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Arrowhead PharmaceuticalsActive, not recruitingHomozygous Familial HypercholesterolemiaAustralia, Canada, United States, South Africa
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AkesoAD Pharmaceuticals Co., Ltd.CompletedHomozygous Familial HypercholesterolemiaChina
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AmgenCompletedHeterozygous Familial HypercholesterolemiaUnited States, Canada, Italy, Norway, Belgium, Turkey, Australia, New Zealand, Austria, Czechia, South Africa, Poland, Spain, Switzerland, Netherlands, Taiwan, Finland, Brazil, Portugal, Slovenia, Russian Federation, Hungary, United... and more
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Akcea TherapeuticsIonis Pharmaceuticals, Inc.TerminatedFamilial Partial LipodystrophyUnited States, Netherlands, Belgium, Brazil, Canada, Germany, Russian Federation
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Regeneron PharmaceuticalsSanofiCompletedHomozygous Familial HypercholesterolemiaUnited States, South Africa, Canada, Greece, Japan, Ukraine, Austria, Czechia, France, Germany, Italy, Taiwan, Turkey
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Regeneron PharmaceuticalsCompletedHomozygous Familial HypercholesterolemiaUnited States, Netherlands, Australia, Austria, Canada, France, Greece, Italy, Japan, South Africa, Ukraine
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Austrian Academic Institute for Clinical NutritionMedical University of ViennaCompletedHeterozygous Familial HypercholesterolemiaAustria
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Aegerion Pharmaceuticals, Inc.WithdrawnHomozygous Familial Hypercholesterolemia
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Merck Sharp & Dohme LLCCompletedHeterozygous Familial Hypercholesterolemia (HeFH)
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Cerenis Therapeutics, SACompleted
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Damanhour UniversityCompletedNeuromuscular Electrical Stimulation | ICU Acquired Muscle WeaknessEgypt
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University Hospital Inselspital, BerneNestec Ltd.CompletedMuscle Weakness | Intensive Care Unit (ICU) Acquired Weakness (ICU - AW)Switzerland
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Pontificia Universidad Catolica de ChileRecruitingMechanical Ventilation Complication | Muscle Weakness or Atrophy | Electrical StimulationsChile
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Cairo UniversityRecruitingIntensive Care Unit Acquired WeaknessEgypt
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University of NottinghamUnknown
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University of PennsylvaniaCompletedHypercholesterolemia, Familial
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Kastle Therapeutics, LLCIonis Pharmaceuticals, Inc.CompletedHypercholesterolemia, FamilialUnited States, Netherlands
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AstraZenecaCompletedFamilial HypercholesterolaemiaUnited States, Netherlands, Norway, Canada, Belgium
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Umeå UniversityCompleted
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University of PennsylvaniaUniversity of Amsterdam; University of Cape Town; University of Witwatersrand...RecruitingHomozygous Familial HypercholesterolemiaUnited States, Netherlands, South Africa
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LIB Therapeutics LLCCompletedHomozygous Familial HypercholesterolemiaUnited States, Israel, Norway, South Africa, Turkey, India