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Clinical Trials on Familial Hypophosphatemic Rickets
Total 1332 results
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AstraZenecaCompletedHomozygous Familial Hypercholesterolemia (HoFH)Malaysia, Canada, Taiwan, Belgium, Denmark, Israel
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NYU Langone HealthRecruitingHereditary Sensory and Autonomic Neuropathies | Familial Dysautonomia (Riley-Day Syndrome) | Hereditary Sensory and Autonomic Neuropathy 3United States, Israel
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KK Women's and Children's HospitalUnknownEmotional Well-being of First-time Families | Nutritional Health of Mother and Child | Parenting Self-Efficacy for First-time Families | Experience of First-time FamiliesSingapore
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The Hospital for Sick ChildrenCompletedFamilial or Severe HypercholesterolemiaCanada
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Mayo ClinicCompleted
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Arrowhead PharmaceuticalsCompletedHypertriglyceridemia | Familial ChylomicronemiaAustralia, Canada, New Zealand
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M.D. Anderson Cancer CenterNot yet recruitingFamilial Platelet Disorder | HematopoieticUnited States
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Shenzhen People's HospitalRecruitingEvaluate the Efficacy and Safety of IBI306 in Subjects With Homozygous Familial HypercholesterolemiaLipid Metabolism Disorders | Familial Hypercholesterolemia - Homozygous | Proprotein Convertase Subtilisin/Kexin 9China
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Hospices Civils de LyonCompleted
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Arrowhead PharmaceuticalsActive, not recruitingFamilial ChylomicronemiaKorea, Republic of, Canada, Australia, Singapore, Belgium, Spain, Japan, United States, Austria, Germany, Ireland, Oman, Poland, Israel, New Zealand, Argentina, France, Croatia, Mexico, Serbia, Turkey
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Akcea TherapeuticsCaligorRx, Inc.No longer availableFamilial Chylomicronemia
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Madigan Army Medical CenterTriService Nursing Research ProgramCompleted
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Harokopio UniversityUniversity College Cork; FrieslandCampinaCompletedHypovitaminosis D | Deficiency of MicronutrientsGreece
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Istituto Ortopedico GaleazziCompletedCardiovascular Diseases | Hypovitaminosis DItaly
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University of ReadingUnknownCardiovascular Diseases | Hypovitaminosis DUnited Kingdom
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University Medical Center GroningenAstraZenecaCompletedHeart Failure | Cardiomyopathy, Familial | Phospholamban R14del CardiomyopathyNetherlands
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Jose L. CasadoRecruitingHypovitaminosis DSpain
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Hospital Regional 1o de OctubreUniversidad Nacional Autonoma de Mexico; National Polytechnic Institute, MexicoCompletedMenopause | Osteoporosis, Postmenopausal | Hypovitaminosis DMexico
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Ionis Pharmaceuticals, Inc.Akcea TherapeuticsCompletedFamilial Chylomicronemia SyndromeUnited States, Israel, Spain, Italy, United Kingdom, Netherlands, Canada, Hungary, Sweden, France, Norway, Portugal, Slovakia
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Ionis Pharmaceuticals, Inc.Active, not recruitingFamilial Chylomicronemia SyndromeUnited States, Canada, Sweden
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Institute of Cardiometabolism and Nutrition, FranceAmgenUnknownFamilial Hypercholesterolemia - HeterozygousFrance
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Mayo ClinicUniversity of California, San Francisco; University of MinnesotaCompletedFamilial Pancreatic CancerUnited States
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Mario Negri Institute for Pharmacological ResearchFondazione TelethonCompleted
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REGENXBIO Inc.Active, not recruitingHomozygous Familial Hypercholesterolemia (HoFH)United States, Canada, Netherlands
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Karo Bio ABTerminatedHeterozygous Familial Hypercholesterolaemia
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Charles Drew University of Medicine and ScienceNational Institute on Minority Health and Health Disparities (NIMHD); Morehouse...CompletedHypovitaminosis DUnited States
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Hospices Civils de LyonRecruiting
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University of ParmaUnknownAcute Renal Failure | Hypophosphatemia | Dialysis Related Complication | HypomagnesemiaItaly
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Massachusetts General HospitalBio-Tech Pharmacal, Inc.WithdrawnHypovitaminosis DUnited States
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Fundació Institut de Recerca de l'Hospital de la...Hospital Clinic of BarcelonaCompletedFamilial Hypocalciuric HypercalcemiaSpain
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Children's Hospital of Eastern OntarioCompletedHypovitaminosis DCanada, Austria, Chile
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University of MichiganAvailable
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NYU Langone HealthCompletedFamilial DysautonomiaUnited States
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NYU Langone HealthCompletedFamilial DysautonomiaUnited States
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Regeneron PharmaceuticalsCompletedGenetic Diseases, Inborn | Familial Cold Autoinflammatory Syndrome (FCAS) | Familial Cold Urticaria | Muckle-Wells Syndrome (MWS)United States
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NYU Langone HealthNot yet recruitingFamilial DysautonomiaUnited States
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NYU Langone HealthNot yet recruiting
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University of Texas Southwestern Medical CenterNational Heart, Lung, and Blood Institute (NHLBI); Columbia University; The Cleveland... and other collaboratorsRecruitingAmyloidosis, Familial | Amyloidosis, Hereditary | Amyloidosis Cardiac | Transthyretin-Related (ATTR) Familial Amyloid Cardiomyopathy | Transthyretin Gene MutationUnited States
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Regeneron PharmaceuticalsTerminatedFamilial Partial Lipodystrophy | Metabolic AbnormalitiesUnited States, France, Spain, Turkey
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NYU Langone HealthCompletedFamilial DysautonomiaUnited States
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Akcea TherapeuticsIonis Pharmaceuticals, Inc.CompletedFamilial Partial LipodystrophyUnited States
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IRCCS Policlinico S. MatteoCompletedTransthyretin AmyloidosisItaly
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Visirna Therapeutics HK LimitedNot yet recruitingFamilial Chylomicronemia Syndrome
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Ionis Pharmaceuticals, Inc.Active, not recruitingFamilial Chylomicronemia SyndromeSpain, United Kingdom, France, Canada, United States, Italy, Netherlands, Norway, Portugal, Slovakia, Sweden
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Ionis Pharmaceuticals, Inc.AvailableFamilial Chylomicronemia Syndrome
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Jiangsu HengRui Medicine Co., Ltd.CompletedMixed Hyperlipidemia | Non-familial HypercholesterolemiaChina
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Abhimanyu GargCompletedFamilial Partial LipodystrophyUnited States
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UniQure Biopharma B.V.CompletedLipoprotein Lipase Deficiency | Familial Hyperlipoproteinemia Type 1 | Familial HyperchylomicronemiaGermany
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Ionis Pharmaceuticals, Inc.Akcea TherapeuticsCompletedFamilial Chylomicronemia SyndromeUnited States, Brazil, Canada, France, Germany, Hungary, Israel, Italy, Netherlands, South Africa, Spain, United Kingdom
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Organon and CoCompletedPrimary Hypercholesterolemia and Homozygous Familial Hypercholesterolemia (HoFH)