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Clinical Trials on Familial Tumoral Calcinosis
Total 19887 results
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Westfälische Wilhelms-Universität MünsterICON plcUnknownPseudoxanthoma Elasticum | Generalized Arterial Calcification in Infancy | Autosomal Recessive Hypophosphatemic RicketsGermany
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The Rogosin InstituteRecruitingHomozygous Familial HypercholesterolemiaUnited States
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The Medicines CompanyCompletedElevated Cholesterol | Heterozygous Familial HypercholesterolemiaUnited States, Canada, Czechia, Denmark, Netherlands, South Africa, Spain, Sweden
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AstraZenecaCompletedHomozygous Familial Hypercholesterolemia (HoFH)Malaysia, Canada, Taiwan, Belgium, Denmark, Israel
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Genesis Medtech CorporationActive, not recruiting
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NYU Langone HealthRecruitingHereditary Sensory and Autonomic Neuropathies | Familial Dysautonomia (Riley-Day Syndrome) | Hereditary Sensory and Autonomic Neuropathy 3United States, Israel
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The Hospital for Sick ChildrenCompletedFamilial or Severe HypercholesterolemiaCanada
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KK Women's and Children's HospitalUnknownEmotional Well-being of First-time Families | Nutritional Health of Mother and Child | Parenting Self-Efficacy for First-time Families | Experience of First-time FamiliesSingapore
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Shenzhen People's HospitalRecruitingEvaluate the Efficacy and Safety of IBI306 in Subjects With Homozygous Familial HypercholesterolemiaLipid Metabolism Disorders | Familial Hypercholesterolemia - Homozygous | Proprotein Convertase Subtilisin/Kexin 9China
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Mayo ClinicCompleted
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Arrowhead PharmaceuticalsCompletedHypertriglyceridemia | Familial ChylomicronemiaAustralia, Canada, New Zealand
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University of UtahIntermountain Health Care, Inc.CompletedPrematurity | Hypercalciuria | NephrocalcinosisUnited States
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Elpiscience Biopharma, Ltd.CompletedNeoplasms | Solid Tumors | Malignant TumorChina
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Elpiscience Biopharma, Ltd.TerminatedNeoplasms | Solid Tumors | Malignant TumorChina
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M.D. Anderson Cancer CenterNot yet recruitingFamilial Platelet Disorder | HematopoieticUnited States
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Arrowhead PharmaceuticalsActive, not recruitingFamilial ChylomicronemiaKorea, Republic of, Canada, Australia, Singapore, Belgium, Spain, Japan, United States, Austria, Germany, Ireland, Oman, Poland, Israel, New Zealand, Argentina, France, Croatia, Mexico, Serbia, Turkey
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Akcea TherapeuticsCaligorRx, Inc.No longer availableFamilial Chylomicronemia
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University Medical Center GroningenAstraZenecaCompletedHeart Failure | Cardiomyopathy, Familial | Phospholamban R14del CardiomyopathyNetherlands
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Erasmus Medical CenterRecruitingVascular Calcification | Tomography, Optical Coherence | Treatment Outcome | Coronary Angiography | Humans | Vascular Calcification* / Diagnostic Imaging | Atherectomies, Coronary | Coronary Intervention, Percutaneous | Vascular Calcification* / TherapyNetherlands
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Mario Negri Institute for Pharmacological ResearchFondazione TelethonCompleted
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REGENXBIO Inc.Active, not recruitingHomozygous Familial Hypercholesterolemia (HoFH)United States, Canada, Netherlands
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Karo Bio ABTerminatedHeterozygous Familial Hypercholesterolaemia
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AstraZenecaCompletedRefractory Solid Tumors | Cancer TumorUnited States
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Dana-Farber Cancer InstituteBayer; NovartisCompletedNeuroendocrine Tumor | Carcinoid Tumor | Pancreatic Neuroendocrine TumorUnited States
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Ionis Pharmaceuticals, Inc.Akcea TherapeuticsCompletedFamilial Chylomicronemia SyndromeUnited States, Israel, Spain, Italy, United Kingdom, Netherlands, Canada, Hungary, Sweden, France, Norway, Portugal, Slovakia
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Ionis Pharmaceuticals, Inc.Active, not recruitingFamilial Chylomicronemia SyndromeUnited States, Canada, Sweden
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Institute of Cardiometabolism and Nutrition, FranceAmgenUnknownFamilial Hypercholesterolemia - HeterozygousFrance
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Roswell Park Cancer InstituteNeuroEndocrine Tumor Research Foundation (NETRF)RecruitingLung Atypical Carcinoid Tumor | Metastatic Pancreatic Neuroendocrine Tumor | Lung Typical Carcinoid TumorUnited States
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Vanquish Oncology, Inc.University of Illinois at ChicagoCompletedSolid Tumor | Neuroendocrine Tumors | Pancreatic Neuroendocrine TumorUnited States
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University Hospital TuebingenRecruitingRare Diseases | Genetic PredispositionGermany
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Dana-Farber Cancer InstituteMassachusetts General Hospital; Novartis; Beth Israel Deaconess Medical Center; Brigham and Women's HospitalCompletedNeuroendocrine Tumor | Carcinoid Tumor | Pancreatic Neuroendocrine TumorUnited States
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Stanford UniversityUnited TherapeuticsCompletedSystemic Sclerosis | CalcinosisUnited States
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Istanbul UniversityCompletedCardiovascular Diseases | Inflammation | Atherosclerosis | Renal DialysisTurkey
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Mayo ClinicUniversity of California, San Francisco; University of MinnesotaCompletedFamilial Pancreatic CancerUnited States
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Fundació Institut de Recerca de l'Hospital de la...Hospital Clinic of BarcelonaCompletedFamilial Hypocalciuric HypercalcemiaSpain
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NYU Langone HealthNot yet recruitingFamilial DysautonomiaUnited States
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NYU Langone HealthNot yet recruiting
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University of Texas Southwestern Medical CenterNational Heart, Lung, and Blood Institute (NHLBI); Columbia University; The Cleveland... and other collaboratorsRecruitingAmyloidosis, Familial | Amyloidosis, Hereditary | Amyloidosis Cardiac | Transthyretin-Related (ATTR) Familial Amyloid Cardiomyopathy | Transthyretin Gene MutationUnited States
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Regeneron PharmaceuticalsTerminatedFamilial Partial Lipodystrophy | Metabolic AbnormalitiesUnited States, France, Spain, Turkey
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NYU Langone HealthCompletedFamilial DysautonomiaUnited States
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Akcea TherapeuticsIonis Pharmaceuticals, Inc.CompletedFamilial Partial LipodystrophyUnited States
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IRCCS Policlinico S. MatteoCompletedTransthyretin AmyloidosisItaly
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University Hospital, Strasbourg, FranceCompletedAcute Coronary SyndromeFrance
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RWTH Aachen UniversityUnknownCalciphylaxis | Calcific Uremic Arteriolopathy (CUA)Germany
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University of MichiganAvailable
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NYU Langone HealthCompletedFamilial DysautonomiaUnited States
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NYU Langone HealthCompletedFamilial DysautonomiaUnited States
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First Affiliated Hospital of Guangxi Medical UniversityRecruiting
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Szeged UniversityResearch Centre for Natural Sciences; University of Debrecen Dept. of RheumatologyNot yet recruitingSystemic Sclerosis | Scleroderma
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National Institute on Aging (NIA)National Heart, Lung, and Blood Institute (NHLBI); USDA Beltsville Human Nutrition... and other collaboratorsCompletedInflammation | Osteoporosis | Vascular CalcificationUnited States