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- US Clinical Trials Registry
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Clinical Trials on Families in United States
Total 571 results
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Regeneron PharmaceuticalsCompletedHomozygous Familial HypercholesterolemiaUnited States, Netherlands, South Africa, Australia, Austria, Canada, Czechia, France, Greece, Italy, Japan, Ukraine
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Insmed IncorporatedTerminatedPulmonary Arterial HypertensionUnited States
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Mayo ClinicUnited TherapeuticsCompletedPulmonary Arterial HypertensionUnited States
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Geno LLCWithdrawnPulmonary Arterial HypertensionUnited States
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AmgenCompletedSevere Familial HypercholesterolemiaItaly, Czechia, United States, Israel, New Zealand, South Africa, France, Spain, Australia, Belgium, Canada, Netherlands, Hong Kong, Brazil, United Kingdom, Greece, Japan, Lebanon
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National Human Genome Research Institute (NHGRI)Merck Sharp & Dohme LLC; Duke University; University of Massachusetts, WorcesterRecruitingFever | Genetic Diseases | Familial Mediterranean Fever (FMF) | Autoinflammation | Periodic Fever | ROSAH | ALPK1United States
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Gmax Biopharm LLC.RecruitingPulmonary Arterial HypertensionUnited States, China
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AmgenCompletedHeterozygous Familial HypercholesterolemiaUnited States, Canada, Italy, Norway, Belgium, Turkey, Australia, New Zealand, Austria, Czechia, South Africa, Poland, Spain, Switzerland, Netherlands, Taiwan, Finland, Brazil, Portugal, Slovenia, Russian Federation, Hungary, United... and more
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GB002, Inc.Not yet recruitingPulmonary Arterial HypertensionUnited States
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Vanderbilt University Medical CenterJohns Hopkins UniversityCompletedPulmonary Arterial Hypertension | Idiopathic Pulmonary Arterial Hypertension | Associated Pulmonary Arterial Hypertension | Heritable Pulmonary Arterial HypertensionUnited States
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National Cancer Institute (NCI)Completed
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State University of New York - Upstate Medical...TerminatedFamilial Encephalopathy With Neuroserpin Inclusion Bodies | X-linked Mental Retardation | Congenital Vertical Talus | Idiopathic Generalised Epilepsy | Familial DementiaUnited States
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Memorial Sloan Kettering Cancer CenterUniversity of Southern California; Weill Medical College of Cornell University and other collaboratorsActive, not recruiting
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Yale UniversityCompleted
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Yale UniversityNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS)CompletedHyperparathyroidism | Hypophosphatemia, FamilialUnited States
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Ionis Pharmaceuticals, Inc.Active, not recruitingFamilial Chylomicronemia SyndromeSpain, United Kingdom, France, Canada, United States, Italy, Netherlands, Norway, Portugal, Slovakia, Sweden
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Novartis PharmaceuticalsCompletedFamilial Cold Autoinflammatory SyndromeUnited States, France, Germany
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PfizerCompletedHeterozygous Familial HypercholesterolemiaCanada, Netherlands, United Kingdom, United States, Spain, Poland, Finland, Norway, South Africa, Italy, Bulgaria
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Kyowa Hakko Kirin Pharma, Inc.Completed
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National Heart, Lung, and Blood Institute (NHLBI)Completed
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University of PennsylvaniaCompletedPulmonary Arterial HypertensionUnited States
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Kastle Therapeutics, LLCCompletedHypercholesterolemia | Heterozygous FamilialUnited States, Italy, Poland, Ukraine, United Kingdom, Germany, Hong Kong, Taiwan, Spain, Argentina, Belgium, Israel, Malaysia, South Africa, Turkey, Netherlands, Korea, Republic of, Canada, New Zealand, Russian Federation, Brazil, Austral... and more
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Vanderbilt University Medical CenterCompletedLung Diseases | Hypertension | Pulmonary Arterial Hypertension | Familial Primary Pulmonary Hypertension | Primary Pulmonary Hypertension | Estrogens | Tamoxifen | Estrogen Receptor Antagonist | Hormone AntagonistsUnited States
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National Institute of Diabetes and Digestive and...CompletedHypercalcemia | Familial Primary HyperparathyroidismUnited States
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Lung Biotechnology PBCCompletedPulmonary Arterial HypertensionUnited States, Belgium, Ireland
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Massachusetts General HospitalNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS)RecruitingX-linked Hypophosphatemia | Hypophosphatemic Rickets | Hypophosphatemic Rickets, X-Linked DominantUnited States
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Ionis Pharmaceuticals, Inc.Akcea TherapeuticsCompletedFamilial Chylomicronemia SyndromeUnited States, Israel, Spain, Italy, United Kingdom, Netherlands, Canada, Hungary, Sweden, France, Norway, Portugal, Slovakia
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The Medicines CompanyCompletedElevated Cholesterol | Heterozygous Familial HypercholesterolemiaUnited States, Canada, Czechia, Denmark, Netherlands, South Africa, Spain, Sweden
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Regeneron PharmaceuticalsCompletedGenetic Diseases, Inborn | Familial Cold Autoinflammatory Syndrome (FCAS) | Familial Cold Urticaria | Muckle-Wells Syndrome (MWS)United States
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Northwell HealthCompletedPulmonary Arterial Hypertension | Pulmonary Hypertension | Interstitial Lung DiseaseUnited States
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Novartis PharmaceuticalsCompletedPulmonary Arterial HypertensionAustria, Germany, United States, United Kingdom
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Amryt PharmaRecruitingHomozygous Familial HypercholesterolemiaItaly, United States, Argentina, Canada, France, Greece, Netherlands, United Kingdom
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United TherapeuticsTerminatedPulmonary Arterial HypertensionUnited States
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Geisinger ClinicCompletedHypercholesterolemia | Hypercholesterolemia, Familial | Hypercholesteremia in Children | Hyperlipidemia in ChildrenUnited States
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Edward KasaraskisCompletedFamilial Amyotrophic Lateral SclerosisUnited States
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University of Texas Southwestern Medical CenterWithdrawnFamilial HypercholesterolemiaUnited States
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Immunovia, Inc.CompletedPancreatic Ductal Adenocarcinoma | Familial Pancreatic Cancer | FAMMM - Familial Atypical Mole Malignant Melanoma SyndromeUnited States, Sweden, Canada, Spain, United Kingdom
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V-Wave LtdRecruitingPulmonary Arterial HypertensionUnited States, Canada, Mexico
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ActelionCompletedPulmonary Arterial HypertensionUnited States, France, Netherlands, Italy, Germany, Switzerland, United Kingdom
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Novartis PharmaceuticalsTerminatedPulmonary Arterial HypertensionGermany, Belgium, United Kingdom, United States, Lithuania, Italy, Australia
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Bellus Health IncNational Institute of Neurological Disorders and Stroke (NINDS)CompletedStroke | Neurologic Diseases, GeneralUnited States
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Rajan SaggarActelionWithdrawnIdiopathic Pulmonary Fibrosis | Pulmonary Arterial HypertensionUnited States
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Medical Research Laboratories InternationalTerminatedFamilial HypercholesterolemiaNetherlands, United States, Norway
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PfizerTerminatedPulmonary Arterial Hypertension | Pulmonary HypertensionUnited States, Romania, Ukraine
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White Plains HospitalActive, not recruitingPancreatic Cancer | Pancreatic Adenocarcinoma | Lynch Syndrome | Pancreas Cancer | HNPCC | Familial Pancreatic Cancer | Hereditary Pancreatitis | BRCA 1/2 | FAMMM | Familial Atypical Multiple Mole Melanoma | Peutz Jeghers SyndromeUnited States
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Ionis Pharmaceuticals, Inc.Akcea TherapeuticsCompletedFamilial Chylomicronemia SyndromeUnited States, Brazil, Canada, France, Germany, Hungary, Israel, Italy, Netherlands, South Africa, Spain, United Kingdom
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PfizerCompletedCerebral Amyloid AngiopathyCanada, United States, Netherlands, France, United Kingdom
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Regeneron PharmaceuticalsSanofiCompletedHeterozygous Familial HypercholesterolemiaUnited Kingdom, Netherlands, Czech Republic, Norway
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Novartis PharmaceuticalsTerminatedPulmonary Arterial HypertensionGermany, United Kingdom, United States
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Idorsia Pharmaceuticals Ltd.TerminatedPulmonary Arterial HypertensionUnited States, France, Switzerland