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Clinical Trials on Fascioscapulohumeral Muscular Dystrophy Type 2
Total 14850 results
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Astellas Pharma IncTerminatedDuchenne Muscular Dystrophy (DMD)United States
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Nippon Shinyaku Co., Ltd.Active, not recruiting
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PfizerTerminatedA Low Interventional Study to Monitor Activity Using Wearable Sensors in Duchenne Muscular DystrophyDuchenne Muscular Dystrophy (DMD)United States
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Sarepta Therapeutics, Inc.Completed
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University Children's Hospital, ZurichUnknownDuchenne / Becker Muscular DystrophySwitzerland
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University Hospital, Basel, SwitzerlandCompletedDuchenne's Muscular Dystrophy (DMD)Switzerland
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Santhera PharmaceuticalsCompletedDuchenne Muscular Dystrophy (DMD)Belgium
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University of MalagaNot yet recruitingMuscular Dystrophy | Duchenne Muscular Dystrophy | Becker Muscular DystrophySpain
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University of FloridaNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS)Not yet recruitingMuscular Dystrophy | Exercise | Duchenne Muscular Dystrophy | Vasodilation | DMD | Muscular Dystrophy in Children | Duchenne Disease
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Gaziosmanpasa Research and Education HospitalCompletedDuchenne or Becker Muscular DystrophyTurkey
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PepGen IncRecruitingMyotonic Dystrophy 1United States, Canada
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Norwegian School of Sport SciencesUniversity of Oslo; Oslo University Hospital; University of Copenhagen; University... and other collaboratorsCompleted
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ItalfarmacoCompletedDuchenne and Becker Muscular Dystrophy | Polycytemia VeraCanada
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PTC TherapeuticsCompletedDuchenne Muscular Dystrophy | Becker Muscular DystrophyUnited States, Germany, Spain, Sweden, Canada, Italy, Australia, Belgium, France, Israel, United Kingdom
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Children's Healthcare of AtlantaWithdrawnScoliosis | Duchenne's Muscular DystrophyUnited States
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Hillel Yaffe Medical CenterRecruiting
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Bioblast Pharma Ltd.CompletedMuscular Dystrophy, Oculopharyngeal (OPMD)Canada
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Rigshospitalet, DenmarkUnknownOculopharyngeal Muscular DystrophyDenmark
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PTC TherapeuticsCompletedDuchenne Muscular Dystrophy | Becker Muscular Dystrophy | DystrophinopathyUnited Kingdom, Canada, Germany, Spain, Sweden, Italy, Australia, Belgium, France, Israel
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InCor Heart InstituteUniversity of Sao Paulo; Federal University of Minas GeraisCompletedMyocardial Fibrosis | Muscular Dystrophies
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Great Ormond Street Hospital for Children NHS Foundation...Catholic University of the Sacred Heart; Università degli Studi di Ferrara; Universidad... and other collaboratorsRecruitingDuchenne Muscular Dystrophy | Becker Muscular DystrophyDenmark, France, Italy, Spain, United Kingdom, Netherlands
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Nationwide Children's HospitalBoston Children's Hospital; University of California, Davis; University of Minnesota and other collaboratorsCompletedCardiomyopathy | Duchenne Muscular Dystrophy (DMD)United States
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PTC TherapeuticsGenzyme, a Sanofi CompanyTerminatedDuchenne Muscular Dystrophy | Becker Muscular DystrophyUnited States, United Kingdom
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PTC TherapeuticsGenzyme, a Sanofi CompanyTerminatedDuchenne Muscular Dystrophy | Becker Muscular DystrophyUnited States, Belgium, Australia, Canada, France, Germany, Israel, Italy, Spain, Sweden, United Kingdom
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University of New MexicoUniversity of FloridaWithdrawnOculopharyngeal Muscular Dystrophy
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Bioblast Pharma Ltd.CompletedOculopharyngeal Muscular DystrophyUnited States, Israel, Canada
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Institut de Myologie, FranceAssociation Française contre les Myopathies (AFM), ParisNot yet recruitingMerosin Deficient Congenital Muscular DystrophyFrance
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Prothelia, Inc.Cure CMD; The Bönnemann Laboratory, NINDS, National Institutes of Health; Oscar... and other collaboratorsCompletedMerosin Deficient Congenital Muscular DystrophyUnited States
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Radboud University Medical CenterUnknownMyotonic Dystrophy Type 2 | McArdle Disease | Nemaline Myopathy Type 6
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IRCCS San RaffaeleRecruiting
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ENCellNot yet recruitingDuchenne Muscular DystrophyKorea, Republic of
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NS Pharma, Inc.Nippon Shinyaku Co., Ltd.Not yet recruiting
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Sqy TherapeuticsBiotrialRecruitingDuchenne Muscular DystrophyFrance
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The Emmes Company, LLCUltragenyx Pharmaceutical Inc; Parent Project Muscular Dystrophy; Department...RecruitingDuchenne Muscular DystrophyUnited States
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REGENXBIO Inc.RecruitingDuchenne Muscular DystrophyUnited States
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PfizerRecruitingDuchenne Muscular DystrophyUnited States
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Gülsena UtkuRecruiting
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Anne M. ConnollyAnn & Robert H Lurie Children's Hospital of Chicago; Children's Hospital Medical... and other collaboratorsRecruiting
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Samsung Medical CenterRecruitingDuchenne Muscular DystrophyKorea, Republic of
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Sohag UniversityNot yet recruitingDuchenne Muscular DystrophyEgypt
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Massachusetts General HospitalBoston Children's HospitalRecruitingDuchenne Muscular DystrophyUnited States
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University of PittsburghRecruitingDuchenne Muscular DystrophyUnited States
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Ning Wang, MD., PhD.Recruiting
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CHU de Quebec-Universite LavalRecruitingDuchenne Muscular DystrophyCanada
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Percheron TherapeuticsActive, not recruitingDuchenne Muscular DystrophyUnited Kingdom, Australia, Serbia, Turkey, Bulgaria
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Sarepta Therapeutics, Inc.CompletedDuchenne Muscular DystrophyUnited States
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Sarepta Therapeutics, Inc.Hoffmann-La RocheEnrolling by invitationDuchenne Muscular DystrophyUnited States
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FibroGenTerminatedDuchenne Muscular DystrophyUnited States, Belgium, Israel, Spain, Canada, Australia, Switzerland, United Kingdom, France, China, Netherlands, Italy, Austria, Czechia
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Daiichi Sankyo Co., Ltd.Orphan Disease Treatment Institute Co., Ltd.Completed
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Sarepta Therapeutics, Inc.Active, not recruitingDuchenne Muscular DystrophyUnited States, Belgium, Spain, United Kingdom, Netherlands, Germany, Canada, Italy