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Clinical Trials on Fra(X) Syndrome in United Kingdom
Total 14804 results
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Tetra Discovery PartnersCompletedFragile X Syndrome | Fra(X) Syndrome | FXSUnited States
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University of California, DavisUniversity of Alberta; St. Justine's HospitalCompletedNeurobehavioral Manifestations | Genetic Diseases, X-Linked | Intellectual Disability | Fragile X Syndrome | Sex Chromosome Disorders | Fragile X Mental Retardation Syndrome | Trinucleotide Repeat Expansion | Fra(X) Syndrome | FXS | Mental Retardation, X LinkedUnited States, Canada
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Nova Mentis Life Science CorpFourthWall TestingRecruitingAutism Spectrum Disorder | Fra(X) SyndromeUnited States
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Queen Margaret UniversityUnknownCardiovascular Diseases | Metabolic Syndrome XUnited Kingdom
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University of DundeeCompleted
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Great Ormond Street Hospital for Children NHS Foundation...UnknownX-linked Severe Combined ImmunodeficiencyUnited Kingdom
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ClasadoUniversity of ReadingCompletedMetabolic Syndrome XUnited Kingdom
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University of East AngliaHarvard School of Public Health (HSPH)CompletedInsulin Resistance | Metabolic Syndrome XUnited Kingdom, United States
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GenethonInstitute of Child Health; Great Ormond Street Hospital for Children NHS Foundation...Completed
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Great Ormond Street Hospital for Children NHS Foundation...RecruitingSevere Combined Immunodeficiency, X-LinkedUnited Kingdom
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Bio Products LaboratoryCompletedCommon Variable Immunodeficiency | Primary Immune Deficiency Disorders | Hyper-IgM Syndrome | X-linked AgammaglobulinaemiaUnited States, United Kingdom, Hungary
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GenethonActive, not recruitingWiskott-Aldrich SyndromeUnited Kingdom, France
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Eunice Kennedy Shriver National Institute of Child...University of WashingtonUnknownWiskott-Aldrich Syndrome | Leukocyte Adhesion Deficiency Syndrome | X-Linked Agammaglobulinemia | X-Linked Hyper IgM SyndromeUnited States
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GenethonActive, not recruitingX-Linked Chronic Granulomatous DiseaseUnited Kingdom
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National Institute of Allergy and Infectious Diseases...CompletedImmunoproliferative DisorderUnited States
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Rare Thyroid Therapeutics International ABVitaccess LtdCompletedAllan-Herndon-Dudley Syndrome | Monocarboxylate Transporter 8 (MCT8) DeficiencyUnited Kingdom
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Great Ormond Street Hospital for Children NHS Foundation...WithdrawnGranulomatous Disease, Chronic, X-linked, VariantUnited Kingdom
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Rush University Medical CenterEmory UniversityEnrolling by invitationTuberous Sclerosis | Fragile X Syndrome | Rett Syndrome | Hamartoma Syndrome, Multiple | Angelman Syndrome | Creatine Deficiency, X-linked | Telomeric 22Q13 Monosomy Syndrome | Chromosome 15Q, Partial DeletionUnited States
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Anavex Life Sciences Corp.Completed
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Guido A. Davidzon, MD, SMWithdrawn
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SanofiBristol-Myers SquibbCompletedMetabolic Syndrome xUnited States
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University of GlasgowGlaxoSmithKline; British Heart FoundationTerminatedAngina Pectoris | Metabolic Syndrome XUnited Kingdom
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David WilliamsActive, not recruitingGene Therapy | Severe Combined Immunodeficiency, X LinkedUnited States, United Kingdom
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Taysha Gene Therapies, Inc.RecruitingRett SyndromeUnited States, United Kingdom
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Midwest Biomedical Research FoundationSuspended
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Anavex Life Sciences Corp.Anavex Australia Pty Ltd.; Anavex Germany GmbHCompletedRett SyndromeCanada, Australia, United Kingdom
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Marinus PharmaceuticalsUniversity of California, Davis; U.S. Army Medical Research and Development...Completed
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RTI InternationalEunice Kennedy Shriver National Institute of Child Health and Human Development...CompletedFragile X Syndrome (FXS)United States
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Ovid Therapeutics Inc.CompletedFragile X Syndrome (FXS)United States
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ShireCompleted
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Newcastle-upon-Tyne Hospitals NHS TrustRecruitingX-linked Myotubular Myopathy | Centronuclear Myopathy | Myotubular Myopathy | Myotubular Myopathy 1 | Myotubular (Centronuclear) Myopathy | Centronuclear Myopathy, X-LinkedUnited Kingdom
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Wake Forest University Health SciencesBrigham and Women's HospitalCompletedDiabetes | Metabolic Syndrome xUnited States
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ShireCompleted
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Novartis PharmaceuticalsTerminatedFragile X SyndromeGermany, United States, Switzerland, Australia, Canada, Denmark, France, Italy, United Kingdom, Spain
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Zynerba Pharmaceuticals, Inc.RecruitingFragile X SyndromeUnited States, Australia, United Kingdom, Ireland
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Zynerba Pharmaceuticals, Inc.Enrolling by invitationFragile X SyndromeUnited States, United Kingdom, New Zealand, Australia
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University of PennsylvaniaAbbottCompletedMetabolic Syndrome xUnited States
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Novartis PharmaceuticalsCompletedFragile X SyndromeUnited States, Switzerland, Germany, Australia, Canada, Denmark, France, Italy, Spain, United Kingdom
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University of California, DavisNational Institute on Aging (NIA); Forest LaboratoriesCompletedFragile X-Associated Tremor/Ataxia Syndrome | Fragile X Premutation CarriersUnited States
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Novartis PharmaceuticalsTerminatedFragile X SyndromeUnited States, Belgium, Australia, Israel, Switzerland, Germany, Denmark, Italy, Netherlands, Spain, Sweden, United Kingdom, France
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University of AberdeenCompletedType 2 Diabetes Mellitus | Sarcopenia | Metabolic Syndrome XUnited Kingdom
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Newron Pharmaceuticals SPATerminatedRett SyndromeUnited States, India, United Kingdom, Australia, Italy
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Virginia Commonwealth UniversityCompletedCardiovascular Diseases | Obesity | Insulin Resistance | Metabolic Syndrome XUnited States
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St. Bartholomew's HospitalUnknownMyelodysplastic SyndromesUnited Kingdom
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James DowlingCanadian Institutes of Health Research (CIHR); Cures Within Reach; The Joshua... and other collaboratorsRecruitingX Linked Myotubular MyopathyUnited Kingdom, Canada, United States
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Brighton and Sussex University Hospitals NHS TrustMedtronic VascularCompletedAcute Coronary SyndromesUnited Kingdom
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Rare Thyroid Therapeutics International ABPremier Research Group plc; Egetis TherapeuticsRecruitingMonocarboxylate Transporter 8 Deficiency | Allan-Herndon-Dudley SyndromeUnited States, United Kingdom, Netherlands
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Fairview University Medical CenterTerminatedImmunologic Deficiency Syndromes | Common Variable Immunodeficiency | Severe Combined Immunodeficiency | Chronic Granulomatous Disease | Hemophagocytic Lymphohistiocytosis | Wiskott-Aldrich Syndrome | Graft Versus Host Disease | X-linked Agammaglobulinemia | Chediak-Higashi Syndrome | Virus-Associated... and other conditionsUnited States
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University College, LondonKing's College London; King's College Hospital NHS Trust; University of Oxford; Great Ormond Street Hospital for Children NHS Foundation TrustRecruitingEpilepsy | Lennox-Gastaut Syndrome, IntractableUnited Kingdom
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Baylor College of MedicineCompletedMetabolic Syndrome X | Heart Failure, CongestiveUnited States