- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Fructose Metabolism, Inborn Errors
Total 4337 results
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AM-PharmaCompleted
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Sheffield Teaching Hospitals NHS Foundation TrustCompleted
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Wuerzburg University HospitalCompleted
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Monash University MalaysiaRecruiting
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National Human Genome Research Institute (NHGRI)CompletedPregnancy | Inborn Errors of Metabolism | AcidemiasUnited States
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Eva Morava-KoziczChildren's Hospital of Philadelphia; Seattle Children's HospitalNot yet recruiting
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Alexion Pharmaceuticals, Inc.Enrolling by invitationHypophosphatasia (HPP)United States, Italy, Russian Federation, Spain, United Kingdom, Germany, Canada, France, Saudi Arabia, Poland, Australia
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Alexion PharmaceuticalsApproved for marketingHypophosphatasiaUnited States, France
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Origin BiosciencesCompletedMolybdenum Cofactor DeficiencyUnited States, Australia, United Kingdom, Germany, Netherlands, Turkey
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Alexion PharmaceuticalsCompletedHypophosphatasiaUnited States, Spain, Australia, United Kingdom, Italy, France, Canada, Germany, Japan, Russian Federation, Saudi Arabia, Turkey
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Nutricia ResearchCompletedInborn Errors of Metabolism | Urea Cycle DisorderUnited States
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University of PittsburghCompleted
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LogicBio Therapeutics, IncAlexion Pharmaceuticals, Inc.Active, not recruitingMethylmalonic AcidemiaUnited States
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Hvidovre University HospitalOdense University HospitalActive, not recruitingHypophosphatasia (HPP)Denmark
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PTC TherapeuticsGenzyme, a Sanofi CompanyTerminatedAmino Acid Metabolism, Inborn ErrorsFrance, United Kingdom, Italy, Belgium, Germany, Switzerland
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University of FloridaCompleted
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Eunice Kennedy Shriver National Institute of Child...Completed
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ModernaTX, Inc.RecruitingPropionic AcidemiaUnited States, Spain, Netherlands, France, United Kingdom, Australia, Canada, Italy
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ModernaTX, Inc.RecruitingPropionic AcidemiaUnited States, Canada, United Kingdom
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AlexionWithdrawn
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CENTOGENE GmbH RostockWithdrawnDefective MineralizationGermany, Sri Lanka, India
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Alexion PharmaceuticalsCompletedHypophosphatasiaUnited States, Canada
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Alexion PharmaceuticalsCompletedHypophosphatasiaUnited States, United Arab Emirates, United Kingdom
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Alexion PharmaceuticalsCompleted
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University of FloridaDiabetes SentryTerminatedClinical Evaluation of a Non-Invasive Hypoglycemia Detector in a Glycogen Storage Disease PopulationGlycogen Storage DiseaseUnited States
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Eunice Kennedy Shriver National Institute of Child...Completed
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Krzysztof BankiewiczNational Institute of Neurological Disorders and Stroke (NINDS); University...Recruiting
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University of British ColumbiaCanadian Institutes of Health Research (CIHR); Saudi Arabian Cultural Bureau...Unknown
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Istanbul UniversityBiruni UniversityNot yet recruitingLipid Storage DiseaseTurkey
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National Institutes of Health Clinical Center (CC)Active, not recruiting
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Nantes University HospitalActive, not recruitingHYPOCHOL : A Genetically-based Strategy to Identify New Targets in Cholesterol Metabolism (HYPOCHOL)HypobetalipoproteinemiaFrance
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Rennes University HospitalCompleted
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University of Campinas, BrazilCompletedHypoalphalipoproteinemiaBrazil
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Sanquin Research & Blood Bank DivisionsRadboud University Medical Center; Maastricht University Medical Center; Atrium...Completed
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University of Wisconsin, MadisonJohns Hopkins University; National Institute of Diabetes and Digestive and... and other collaboratorsEnrolling by invitationIron Overload | Hemosiderosis | HemochromatosisUnited States
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University of Wisconsin, MadisonCompleted
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Hospices Civils de LyonCompleted
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Seoul National University HospitalCompleted
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Instituto Nacional de Ciencias Medicas y Nutricion...Instituto Nacional de Cardiologia Ignacio ChavezCompleted
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Maastricht University Medical CenterAnnadal stichtingUnknownHemochromatosisNetherlands, Belgium
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University of BergenHaukeland University Hospital; Helse Fonna; University Hospital, AkershusUnknown
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CENTOGENE GmbH RostockWithdrawnFructose Metabolism, Inborn Errors | Glycogen Storage Disease Type II | Glycogen Storage Disease | Glycogen Storage Disease Type V | Glycogen Storage Disease Type I | Glycogen Storage Disease Type III | Glycogen Storage Disease Type VII | Glycogen Storage Disease Type IV | Glycogen Storage Disease Type... and other conditionsGermany, India, Sri Lanka
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Ultragenyx Pharmaceutical IncCompletedGSD1Netherlands, United States, Canada, Spain
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Mendel TuchmanEunice Kennedy Shriver National Institute of Child Health and Human Development...UnknownInborn Errors of MetabolismUnited States
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Alexion PharmaceuticalsCompletedHypophosphatasia (HPP)United States, Canada
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Oregon Health and Science UniversityNational Heart, Lung, and Blood Institute (NHLBI)TerminatedSmith-Lemli-Opitz SyndromeUnited States
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TRPHARMKlinar CRO; Damagen Genetic Diagnostic CenterEnrolling by invitationXanthomatosis, CerebrotendinousTurkey
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University of TorontoUnknownCardiovascular Risk Factor | Cholesterol; LipidosisCanada
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Kuhnil Pharmaceutical Co., Ltd.UnknownHyperlipidemia, Familial CombinedKorea, Republic of
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Alexion Pharmaceuticals, Inc.Xcenda, LLCActive, not recruitingHypophosphatasiaUnited States