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Clinical Trials on GNE Myopathy
Total 1142 results
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Agyany Pharma LTDRecruiting
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Damascus UniversityUniversity Children's HospitalCompletedEsophageal Atresia | One Lung Ventilation OLV | Hydrocystoma | Pneumonectomy | Pleura; AbscessSyrian Arab Republic
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Shirish M GadgeelAstraZeneca; Henry Ford Health SystemWithdrawnLung Cancer | Non-small Cell Lung Cancer | PD-L1 Gene Mutation | KRAS Activating MutationUnited States
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Haukeland University HospitalTerminatedColorectal Cancer Metastatic | Colorectal Cancer Stage IV | TP53 Gene MutationNorway
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SpringWorks Therapeutics, Inc.AvailableDesmoid Tumor | NOTCH Gene Mutation Positive Tumors
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PfizerTerminatedDilated Cardiomyopathy | Lamin A/C Gene MutationUnited States, Spain, Canada, Belgium, Italy, Argentina, Mexico, Netherlands, Norway, United Kingdom
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Basilea PharmaceuticaCompletedIntrahepatic Cholangiocarcinoma | Combined Hepatocellular and CholangiocarcinomaCanada, United States, Spain, Belgium, Italy, Korea, Republic of, Germany, Switzerland, France, United Kingdom, Ireland
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Laurent ServaisSYSNAVRecruitingDuchenne Muscular Dystrophy | Myotonic Dystrophy 1 | Congenital Muscular Dystrophy | Centronuclear Myopathy | Charcot-Marie-Tooth | Fascioscapulohumeral Muscular DystrophyBelgium
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Ankara City Hospital BilkentRecruitingCoronary Arteriosclerosis | One-lung Ventilation | Heart Valvular DiseaseTurkey
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Peking University Third HospitalRecruitingCruciate Ligament Rupture | Meniscus Injury | Gene AbnormalityChina
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Cardiff OncologyCompletedMetastatic Colorectal Cancer | KRAS Gene MutationUnited States
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Cardiff OncologyNo longer availableMetastatic Colorectal Cancer | KRAS Gene Mutation
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Lawson Health Research InstituteUnknownLow Vision Aids | Low Vision, One Eye, Unspecified Eye | Low Vision BlindnessCanada
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Maastricht University Medical CenterRecruitingPost-Infarction Heart Rupture | Gene PolymorphismItaly
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Icahn School of Medicine at Mount SinaiMassachusetts General Hospital; National Institute of Neurological Disorders...RecruitingParkinson Disease | GBA Gene Mutation | LRRK2United States
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Peking University Cancer Hospital & InstituteNot yet recruitingColorectal Cancer | Radiofrequency Ablation | Liver Metastasis | KRAS Gene | Safe Margin
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Shanghai University of Traditional Chinese MedicineUnknownGene Mutation-Related Cancer | Traditional Chinese Medicine
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Hideho Okada, MD, PhDNational Cancer Institute (NCI); California Institute for Regenerative Medicine...RecruitingGlioblastoma | Recurrent Glioblastoma | EGFR Gene Mutation | MGMT-Unmethylated GlioblastomaUnited States
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Stony Brook UniversityRecruitingThe Primary Outcome is Preterm Delivery Before 28 Weeks Gestational Age Compared to Women With One vs Two Cerclages PlacedUnited States
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Betta Pharmaceuticals Co., Ltd.Active, not recruitingNon-Small Cell Lung Cancer | EGFR Gene MutationChina
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BayerCompletedLocally Advanced or Metastatic Infantile Fibrosarcoma Harboring an NTRK Gene Fusion | Infantile FibrosarcomaFrance
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University of Colorado, DenverCancer League of ColoradoWithdrawnMetastatic Breast Cancer | Triple Negative Breast Cancer | Locally Advanced Breast Cancer | Unresectable Breast Carcinoma | PD-L1 Gene MutationUnited States
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Beijing Tiantan HospitalBeijing Municipal Science & Technology CommissionCompletedTransient Ischemic Attack | Stroke, Acute | Single-gene DisordersChina
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Merrimack PharmaceuticalsTerminatedStomach Cancer | Gastroesophageal Junction Cancer | HER-2 Gene Amplification | Esophagus CancerUnited States
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Arog Pharmaceuticals, Inc.CompletedAcute Myeloid Leukemia With FLT3 Activating Mutations That Has Relapsed or Been Refractory After One or More Prior TherapiesUnited States
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Instituto Nacional de Cancerologia de MexicoRoche Pharma AGCompletedALK Gene Rearrangement Positive | Non-Squamous Non-Small Cell Neoplasm of LungMexico
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Poitiers University HospitalActive, not recruitingNon Small Cell Lung Cancer | Gene Mutation-Related Cancer | PD-L1 | PET/CTFrance
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Yonsei UniversityCompletedObese Patients, One Lung VentilationKorea, Republic of
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Shanghai General Hospital, Shanghai Jiao Tong University...Not yet recruitingTo Evaluate the Scaling Clinical Study of AAV2-RPE65 Gene Therapy Agent (LX101) in Patients With Congenital Amaurosis (LCA)
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University of North Carolina, Chapel HillMed-El CorporationRecruitingHearing Loss | Congenital Hearing Loss | Hearing Loss, Unilateral | Single Sided Deafness | Unilateral Deafness | Deafness One EarUnited States
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Hunan Province Tumor HospitalRecruitingLung Adenocarcinoma | ALK Gene Mutation | ImmunotherapyChina
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XuanwuH 2University of CologneRecruitingAlzheimer Disease | Subjective Cognitive Decline | Neuroimaging | GeneChina
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Medical University InnsbruckCompletedThoracic Surgery | Mechanical Ventilation | One-Lung VentilationAustria
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Laval UniversityCompletedVideo-assisted Thoracoscopic Surgery | One-lung Ventilation | Lung Isolation Device | Double Lumen Endotracheal Tube | Bronchial BlockerCanada
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Thammasat UniversityCompletedSeverity of OA Knee | Difference of Joint Space Width Between One-leg and Both-leg Standing RadiographThailand
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Latin American Cooperative Oncology GroupGlaxoSmithKlineCompletedBRMS1 | Performance Status Zero to Two for Beginning the Study | Patient With a Maximum of One Chemotherapy | Patient With Progression After TaxanesArgentina, Brazil, Peru
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The Catholic University of KoreaUnknownErectile Dysfunction | Myelopathy | Neurogenic Bladder | Sexual Arousal Disorder | Psychosexual DysfunctionsKorea, Republic of
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Number 2 Children's Hospital, Ho Chi Minh CityRecruitingChild Development | Epilepsy; Seizure | Gene Abnormality | Early Onset DisorderVietnam
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Shanghai Pulmonary Hospital, Shanghai, ChinaUnknownNonsmall Cell Lung Cancer | EGFR Gene Mutation
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Memorial Sloan Kettering Cancer CenterMerck Sharp & Dohme LLC; Genentech, Inc.RecruitingEsophageal Cancer | Gastric Adenocarcinoma | HER2 Gene MutationUnited States
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Yonsei UniversityRecruitingAssessment of Salbutamol Effect on Arterial Oxygenation in COPD Patients During One-lung VentilationChronic Obstructive Pulmonary Disease | One-lung VentilationKorea, Republic of
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Regeneron PharmaceuticalsRecruitingCongenital Hearing Loss Secondary to Biallelic Mutations of the Otoferlin Gene (OTOF)Spain, United Kingdom, United States
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Tianjin Medical University Cancer Institute and...RecruitingAdvanced Hepatocellular Carcinoma That Has Failed at Least One Prior Systemic TherapyChina
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Fundamenta Therapeutics, Ltd.The First Affiliated Hospital of Zhengzhou UniversityNot yet recruitingAllogeneic, CAR-T, Protein Sequestration, Non-gene Edited
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Institute of Hematology & Blood Diseases HospitalRecruiting
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Shengjing HospitalNot yet recruitingPostoperative Delirium | General Anesthesia | Circadian Rhythm Disorders | Exosomes | Clock GeneChina
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University College, LondonNIHR Rare Diseases Translational Research Collaboration; Barts Cardiovascular...RecruitingLamin A/C Gene Mutation | Dilated Cardiomyopathy, FamilialUnited Kingdom
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The Hospital for Sick ChildrenThe National Pancreas FoundationWithdrawnCystic Fibrosis | CFTR Gene Dysfunction
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Changhoon YooCompletedCholangiocarcinoma | Biliary Tract Cancer | HER-2 Gene Amplification | HER-2 Protein OverexpressionKorea, Republic of
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Beijing Tongren HospitalUnknownNeuromyelitis Optica | Glucocorticoid Resistance | GeneChina