- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Genetic Alteration in Australia
Total 960 results
-
Intellia TherapeuticsActive, not recruitingHereditary AngioedemaFrance, New Zealand, Germany, United Kingdom, Netherlands, Australia
-
Galapagos NVCompletedCystic FibrosisUnited Kingdom, Australia, Ireland, Germany, Czech Republic
-
Novo Nordisk A/SCompletedKidney Diseases | Urologic Diseases | Genetic Disease | Primary Hyperoxaluria Type 1 (PH1) | Primary Hyperoxaluria Type 2 (PH2)Poland, United States, United Kingdom, New Zealand, Australia, Canada, France, Germany, Israel, Italy, Japan, Lebanon, Netherlands, Romania, Spain
-
Evelo Biosciences, Inc.TerminatedAtopic DermatitisUnited States, Australia, Bulgaria, Canada, Germany, Poland
-
Novo Nordisk A/SActive, not recruitingHaemophilia A With Inhibitors | Haemophilia B With InhibitorsSpain, Korea, Republic of, India, Australia, United Kingdom, Russian Federation, Poland, Ukraine, Thailand, Mexico, United States, Turkey, Japan, South Africa, Serbia, France, Croatia, Denmark, Algeria, Bulgaria, Malaysia, Portugal, Slovaki... and more
-
Ultragenyx Pharmaceutical IncTerminatedGlucose Transporter Type 1 Deficiency SyndromeUnited States, Spain, Denmark, United Kingdom, Australia
-
Neovii BiotechCompletedBronchiectasis | Idiopathic Pulmonary Fibrosis | Cystic Fibrosis | Chronic Obstructive Pulmonary | Pulmonary Vascular DiseaseUnited States, Australia, Austria, Canada
-
CSL BehringTerminatedHemophilia ARussian Federation, Germany, Italy, Austria, Greece
-
Baxalta now part of ShireCompletedPrimary Immunodeficiency Diseases (PID)Germany, Austria, Hungary, Sweden, United Kingdom
-
AbbVieActive, not recruitingAtopic DermatitisUnited States, Argentina, Australia, Bosnia and Herzegovina, Bulgaria, Canada, China, Colombia, Croatia, Denmark, Estonia, Finland, France, Germany, Italy, Japan, Malaysia, New Zealand, Puerto Rico, Romania, Russian Federation, Sw... and more
-
Idorsia Pharmaceuticals Ltd.Active, not recruitingFabry DiseaseUnited States, United Kingdom, Norway, Germany, Australia, Canada, Spain, Switzerland, Austria, Belgium, France, Netherlands, Poland
-
PTC TherapeuticsCompletedNervous System Diseases | Genetic Diseases, Inborn | Genetic Diseases, X-Linked | Musculoskeletal Diseases | Muscular Diseases | Neuromuscular Diseases | Muscular Dystrophies | Muscular Disorders, Atrophic | Muscular Dystrophy, DuchenneUnited States, Spain, Korea, Republic of, Belgium, France, Canada, Australia, United Kingdom, Israel, Italy, Brazil, Chile, Czechia, Sweden, Switzerland, Turkey, Germany, Poland
-
PfizerCompletedAtopic DermatitisChina, United States, Turkey, Australia, Canada, Israel
-
PfizerCompletedSkin Diseases | Immune System Diseases | Hypersensitivity | Hypersensitivity, Immediate | Genetic Diseases, Inborn | Skin Diseases, Genetic | Dermatitis | Eczema | Skin Diseases, Eczematous | Dermatitis, AtopicSpain, Taiwan, United States, Australia, Poland, Germany, Hungary, Bulgaria, Czechia, Japan, Korea, Republic of, Latvia, Canada, United Kingdom, Mexico, Chile, Slovakia, Italy
-
Wave Life Sciences Ltd.TerminatedHuntington DiseaseDenmark, Australia, Canada, France, United Kingdom, Germany, Poland
-
Monash UniversityChildren's Hospital of Philadelphia; McGill University; University of Florida; University... and other collaboratorsActive, not recruitingFriedreich AtaxiaUnited States, Canada, Australia, Brazil, Germany
-
Vertex Pharmaceuticals IncorporatedCompletedCystic FibrosisSpain, Belgium, Australia, Canada, Czechia
-
AbbVieActive, not recruitingAtopic DermatitisAustralia, Belgium, Bulgaria, Canada, China, Germany, Hungary, Italy, Korea, Republic of, Netherlands, New Zealand, Poland, Portugal, Slovakia, Spain, Taiwan, United Kingdom, Japan
-
ReCode TherapeuticsRecruitingPrimary Ciliary DyskinesiaUnited Kingdom, United States, Australia, New Zealand
-
Spark TherapeuticsActive, not recruitingHemophilia AUnited States, Canada, Australia
-
Mitsubishi Tanabe Pharma America Inc.Active, not recruitingEPP | XLPUnited States, Germany, Japan, Spain, Italy, Sweden, Australia, Canada, Norway, United Kingdom
-
ReveraGen BioPharma, Inc.University of Pittsburgh; Newcastle University; European Union; Cooperative International...CompletedDuchenne Muscular DystrophyUnited States, Belgium, Canada, United Kingdom, Spain, Netherlands, Sweden, Czechia, Australia, Greece, Israel
-
AmgenAstraZenecaTerminatedAtopic DermatitisUnited Kingdom, Spain, Australia, Hungary, Switzerland, United States, Germany, Korea, Republic of, Canada, Czechia, Poland, Japan, Estonia, Latvia, Ukraine
-
Incyte CorporationRecruitingAtopic DermatitisGermany, Poland, United States, Spain, United Kingdom, Italy, Belgium, Canada, Netherlands, Australia, Bulgaria, France, Switzerland, Hungary, Korea, Republic of
-
La Jolla Pharmaceutical CompanyPRA Health SciencesCompletedHereditary HemochromatosisUnited States, Australia, France, United Kingdom
-
Evelo Biosciences, Inc.CompletedAtopic DermatitisUnited States, Australia, Bulgaria, Canada, Germany, Poland
-
MedImmune LLCCompletedAtopic DermatitisUnited States, Germany, Canada, Australia, Poland, Japan
-
Almirall, S.A.CompletedEczema | Dermatitis, AtopicAustria, Belgium, France, Germany, Netherlands, Poland, Spain, United Kingdom
-
PTC TherapeuticsTerminatedNervous System Diseases | Genetic Diseases, Inborn | Genetic Diseases, X-Linked | Musculoskeletal Diseases | Muscular Diseases | Neuromuscular Diseases | Muscular Dystrophies | Muscular Disorders, Atrophic | Muscular Dystrophy, DuchenneUnited States, Spain, Korea, Republic of, Belgium, France, Canada, Australia, United Kingdom, Israel, Italy, Germany, Brazil, Bulgaria, Chile, Czechia, Poland, Sweden, Switzerland, Turkey
-
AstraZenecaIqvia Pty LtdTerminatedAtopic DermatitisUnited States, France, Korea, Republic of, Spain, Czechia, Bulgaria, Australia, Poland
-
ShireCompletedHunter SyndromeSpain, United States, Canada, United Kingdom, France, Australia, Mexico
-
Zynerba Pharmaceuticals, Inc.CompletedFragile X SyndromeUnited States, New Zealand, Australia
-
Jazz PharmaceuticalsGW PharmaceuticalsTerminatedRett Syndrome | RTTUnited States, Canada, Italy, Spain, United Kingdom, Australia
-
Synchron Medical, Inc.WithdrawnParalysis | Amyotrophic Lateral Sclerosis | Muscular Dystrophies | Neurologic Disorder | Spinal Muscular Atrophy | Spinal Cord Injury | Stroke, Lacunar | Upper Limb Injury | Paralysis; Stroke | Stroke, BrainstemAustralia
-
Regeneron PharmaceuticalsSanofiCompletedAtopic DermatitisUnited States, Italy, United Kingdom, Spain, Japan, Canada, Netherlands, New Zealand, Hungary, Czechia, Poland, Australia, Romania, Korea, Republic of
-
Wave Life Sciences Ltd.TerminatedHuntington's DiseaseDenmark, Canada, Australia, United Kingdom, France, Germany, Poland
-
LEO PharmaCompletedAtopic DermatitisUnited States, Canada, Czechia, Germany, Poland, Spain, Australia, Japan
-
Boehringer IngelheimRecruitingNetherton SyndromeBelgium, United Kingdom, Australia, Germany, China, Malaysia, United States, Japan, France, Israel, Bulgaria, Italy, Switzerland, Netherlands, Portugal
-
Mitsubishi Tanabe Pharma America Inc.CompletedEPP | XLPSpain, United States, Germany, Norway, Italy, Australia, Canada, Japan, Sweden, United Kingdom
-
Dyne TherapeuticsRecruitingDuchenne Muscular Dystrophy (DMD)United States, Belgium, Canada, United Kingdom, Australia, Spain, Italy
-
PfizerTerminatedAchondroplasiaUnited States, Australia, Belgium, Denmark, Italy, Portugal, Spain
-
SanofiActive, not recruitingDermatitis AtopicAustralia, United States, Argentina, Brazil, Canada, Colombia, France, Mexico, Netherlands
-
Novo Nordisk A/SEnrolling by invitationHaemophilia BCanada, United Kingdom, Czechia, Germany, Greece, Austria, Belgium, Croatia, Denmark, Finland, Norway, Portugal
-
ProtalixChiesi Farmaceutici S.p.A.CompletedFabry DiseaseUnited States, Serbia, Spain, United Kingdom, Australia, Paraguay
-
Prana Biotechnology LimitedCompletedHuntington DiseaseUnited States, Australia
-
NS Pharma, Inc.Nippon Shinyaku Co., Ltd.CompletedDuchenne Muscular DystrophyKorea, Republic of, Chile, Taiwan, China, United States, United Kingdom, Netherlands, Spain, Australia, Norway, Russian Federation, Greece, Italy, Turkey, Mexico, Canada, Hong Kong, New Zealand, Ukraine
-
PfizerTerminatedDuchenne Muscular DystrophyUnited States, Australia, Canada, United Kingdom, Japan, Bulgaria, Italy, Poland
-
BioMarin PharmaceuticalNo longer availableDuchenne Muscular DystrophyUnited States, Germany, United Kingdom, Japan, Netherlands, France, Spain, Korea, Republic of, Italy, Belgium, Taiwan, Argentina, Australia, Bulgaria, Czechia, Israel, Norway, Poland, Russian Federation, Turkey
-
CSL BehringCompletedVon Willebrand DiseasePoland, Germany, Austria, Greece, United Kingdom
-
Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia BSpain, United Kingdom, Australia, Taiwan, France, Malaysia, United States, Austria, Canada, Israel, Japan, Thailand, Algeria, Argentina