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Clinical Trials on Genetic Diseases, Inborn in Brazil
Total 8414 results
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Hospital de Clinicas de Porto AlegreConselho Nacional de Desenvolvimento Científico e Tecnológico; Fundação Médica...CompletedGlycogen Storage Disease Type IBrazil
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University of Campinas, BrazilCompletedHypoalphalipoproteinemiaBrazil
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Libbs Farmacêutica LTDACompletedArterial Hypertension | Blood Glucose, High | Cholesterol; LipidosisBrazil
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Applied Biology, Inc.Jupiter Wellness, Inc.Withdrawn
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University of Sao Paulo General HospitalPfizerRecruiting
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Amicus TherapeuticsCompletedFabry DiseaseAustralia, Brazil
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ArmaGen, IncCompletedMucopolysaccharidosis IBrazil
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Azidus BrasilWithdrawn
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TakedaCompletedMucopolysaccharidosis (MPS)Brazil
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Johnson & Johnson Consumer Inc. (J&JCI)Completed
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Cosmetique Active InternationalCompleted
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Hospital de Clinicas de Porto AlegreFundação de Amparo à Pesquisa do Estado do Rio Grande do Sul, BrazilSuspendedCBS DeficiencyBrazil
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National Institute of Cardiology, Laranjeiras,...CompletedEndothelial Dysfunction | HyperhomocysteinemiaBrazil
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Libbs Farmacêutica LTDACompletedAtopic DermatitisBrazil
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ArmaGen, IncCompletedMucopolysaccharidosis IBrazil
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Galderma Brasil Ltda.Recruiting
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University of Sao Paulo General HospitalFUNADERSP (Foundation for Research Support of the State of São Paulo)CompletedAtopic DermatitisBrazil
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JCR Pharmaceuticals Co., Ltd.Completed
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University of Sao Paulo General HospitalRecruitingMicrobial Colonization | Amyloidosis, Hereditary, Transthyretin-RelatedBrazil
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University of Sao PauloMerck Sharp & Dohme LLCUnknownHeterozigous Familial HypercholesterolemiaBrazil
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JCR Pharmaceuticals Co., Ltd.Active, not recruitingMucopolysaccharidosis IIBrazil
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Genzyme, a Sanofi CompanyBioMarin/Genzyme LLCCompletedMucopolysaccharidosis IBrazil, Russian Federation
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Galderma Brasil Ltda.Completed
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Faculdades Metropolitanas UnidasUniversity of Sao PauloCompleted
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Casa Espirita Terra de IsmaelUniversity of Sao PauloCompletedAtopic DermatitisBrazil
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Monica Levy AndersenCompletedOther Diseases or ConditionsBrazil
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University of Sao PauloCompletedDuchenne Muscular DystrophyBrazil
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PATHFundação de Medicina Tropical Dr. Heitor Vieira DouradoCompleted
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Horizon Pharma USA, Inc.Completed
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University of Sao PauloCompletedDuchenne Muscular DystrophyBrazil
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Hospital do CoracaoUniversity of Sao Paulo; National Institute of Cardiology, Laranjeiras, BrazilActive, not recruitingFamilial HypercholesterolemiaBrazil
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Universidade Estadual de LondrinaCompletedCardiovascular Disease | Hemodialysis | Chronic Renal Failure | Uremia | HyperhomocysteinemiaBrazil
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AVROBIOTerminatedFabry DiseaseAustralia, Brazil
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University of Sao Paulo General HospitalBiosense Webster, Inc.RecruitingBrugada SyndromeBrazil
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REGENXBIO Inc.Enrolling by invitation
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LYSOGENECompletedMucopolysaccharidosis IIIAGermany, Brazil, United Kingdom, France, Netherlands
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Ministry of Health, BrazilTerminated
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Ministry of Health, BrazilFinanciadora de Estudos e ProjetosCompleted
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Instituto de Cardiologia do Rio Grande do SulFundação de Amparo à Pesquisa do Estado do Rio Grande do Sul, Brazil; Conselho...CompletedDilated CardiomyopathyBrazil
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JCR Pharmaceuticals Co., Ltd.CompletedMucopolysaccharidosis IUnited States, Brazil, Japan
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University of Sao PauloCompletedRetinitis PigmentosaBrazil
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JCR Pharmaceuticals Co., Ltd.Active, not recruitingMucopolysaccharidosis IUnited States, Brazil, Japan
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Fundação de Medicina Tropical Dr. Heitor Vieira...Oswaldo Cruz Foundation; Conselho Nacional de Desenvolvimento Científico e...Active, not recruitingVivax Malaria | G6PD DeficiencyBrazil
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University of Sao PauloCompletedRetinitis PigmentosaBrazil
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Federal University of São PauloCompletedAge Related Macular Degeneration | Exudative Age-related Macular Degeneration | Stargardt's DiseaseBrazil
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University of Sao PauloConselho Nacional de Desenvolvimento Científico e TecnológicoUnknown
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ShireCovance; PRA Health Sciences; PharmaNetCompletedMucopolysaccharidosis II | Hunter Syndrome | MPS IIBrazil, Poland, Taiwan
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University of Sao PauloCompleted
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REGENXBIO Inc.CompletedMucopolysaccharidosis IIBrazil, United States, United Kingdom
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Eurofarma Laboratorios S.A.Completed