Clinical Trials on Genetic Diseases, Inborn in Canada
Total 24977 results
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York UniversityNorth York General HospitalCompleted
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Vertex Pharmaceuticals IncorporatedRecruitingCystic FibrosisUnited Kingdom, Canada
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PfizerCompletedHyperlipidemia | Hypercholesterolemia, FamilialAustralia, Canada, United States, France, South Africa, Sweden, Norway, Denmark, Iceland
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University Health Network, TorontoRecruitingHypermobile EDS (hEDS) | Hypermobility SyndromeCanada
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PTC TherapeuticsRecruitingPhenylketonuriaUnited States, Germany, Spain, Australia, Brazil, United Kingdom, Denmark, Mexico, Portugal, Turkey, Canada, Georgia, Italy, Netherlands, Japan
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Anavex Life Sciences Corp.Anavex Australia Pty Ltd.; Anavex Germany GmbHCompletedRett SyndromeCanada, Australia, United Kingdom
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University of ManitobaUnknownCystic Fibrosis | Cystic Fibrosis Liver Disease | Pancreatic Insufficiency Due to Cystic Fibrosis of PancreasCanada
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Cooperative International Neuromuscular Research...CompletedMuscular Dystrophy, DuchenneUnited States, Canada, Argentina, Australia, Israel, Italy
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BioMarin PharmaceuticalTerminatedMorquio A Syndrome | MPS IVA | Mucopolysaccharidosis IVAUnited States, United Kingdom, Canada, Germany
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Vertex Pharmaceuticals IncorporatedRecruitingMyotonic Dystrophy Type 1 (DM1)Canada
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Ardea Biosciences, Inc.CompletedGoutPoland, United States, Spain, Canada, Ukraine, United Kingdom
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Unity Health TorontoCompletedCystic Fibrosis | Burkholderia Cepacia InfectionCanada
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Immunovant Sciences GmbHCompletedGraves' OphthalmopathyCanada
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Ionis Pharmaceuticals, Inc.RecruitingAlexander DiseaseUnited States, United Kingdom, Australia, Canada, Israel, Italy, Japan, Netherlands
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University of CalgaryCanadian Institutes of Health Research (CIHR)Recruiting
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HealthCore-NERINational Heart, Lung, and Blood Institute (NHLBI)Completed
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Arcutis Biotherapeutics, Inc.CompletedAtopic DermatitisUnited States, Canada
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Arrowhead PharmaceuticalsActive, not recruitingFamilial ChylomicronemiaKorea, Republic of, Canada, Australia, Singapore, Belgium, Spain, Japan, United States, Austria, Germany, Ireland, Oman, Poland, Israel, New Zealand, Argentina, France, Croatia, Mexico, Serbia, Turkey
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Amicus TherapeuticsTerminatedLate-onset Pompe DiseaseUnited States, Canada, Australia, Belgium
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Amicus TherapeuticsRecruitingPompe Disease (Late-onset)United States, Taiwan, Japan, Australia, Canada
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University Health Network, TorontoRecruitingThalassemia MajorCanada
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The Hospital for Sick ChildrenProvincial Health Services AuthorityCompletedPrimary Ciliary DyskinesiaCanada
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University of AlbertaCompleted
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The Hospital for Sick ChildrenUnity Health TorontoActive, not recruiting
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Idorsia Pharmaceuticals Ltd.CompletedFabry DiseaseUnited States, Spain, Belgium, Australia, Austria, Canada, Germany, Ireland, Italy, Netherlands, Norway, Poland, Switzerland, United Kingdom
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Prolong PharmaceuticalsCompletedAnemia, Sickle CellColombia, Panama, Dominican Republic, Honduras
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CSL BehringCompletedPrimary ImmunodeficiencyUnited States, Canada
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Spark TherapeuticsCompletedHematologic Diseases | Hemophilia A | Blood Coagulation Disorders, Inherited | Coagulation Protein Disorders | Hemorrhagic Disorders | Genetic Diseases, Inborn | Genetic Diseases, X-Linked | Blood Coagulation Disorder | Factor VIII DeficiencyUnited States, Australia, Thailand, Canada
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Genzyme, a Sanofi CompanyCompletedFabry DiseaseUnited States, United Kingdom, Canada, Hungary, Poland, Czech Republic
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PTC TherapeuticsCompletedPhenylketonuriaSpain, United States, Australia, Germany, United Kingdom, Brazil, Denmark, Canada, France, Georgia, Italy, Mexico, Netherlands, Portugal, Turkey
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Santhera PharmaceuticalsAvailableDuchenne Muscular DystrophyUnited States, Canada, Israel
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University of BahrainCompletedSelf-Efficacy | Self-CareBahrain
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Bioblast Pharma Ltd.CompletedOculopharyngeal Muscular DystrophyUnited States, Israel, Canada
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University Health Network, TorontoCompletedThalassemia Major | Chronic Blood Transfusion Related Iron OverloadCanada
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Montreal Heart InstituteEnrolling by invitationAtrial Fibrillation | Genetic PredispositionCanada
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The Medicines CompanyCompletedElevated Cholesterol | Heterozygous Familial HypercholesterolemiaUnited States, Canada, Czechia, Denmark, Netherlands, South Africa, Spain, Sweden
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University of British ColumbiaTerminated
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Ionis Pharmaceuticals, Inc.Active, not recruitingFamilial Chylomicronemia SyndromeSpain, United Kingdom, France, Canada, United States, Italy, Netherlands, Norway, Portugal, Slovakia, Sweden
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Opsidio, LLCInnovaderm Research Inc.Active, not recruitingAtopic DermatitisCanada, United States
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MedImmune LLCAmgenCompletedAtopic DermatitisUnited States, Germany, New Zealand, Hungary, Australia, Canada
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SanofiRegeneron PharmaceuticalsRecruitingModerate to Severe Atopic DermatitisCanada
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Institut de Recherches Cliniques de MontrealUniversity Hospital, Strasbourg, France; Centre hospitalier de l'Université... and other collaboratorsRecruitingCystic FibrosisCanada, France
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Vertex Pharmaceuticals IncorporatedCRISPR TherapeuticsRecruitingHematologic Diseases | Genetic Diseases, Inborn | Hemoglobinopathies | Thalassemia | Beta-ThalassemiaUnited States, Germany, Italy, United Kingdom, Canada
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HealthCore-NERINational Heart, Lung, and Blood Institute (NHLBI); Pediatric Heart NetworkCompletedCardiomyopathy, DilatedUnited States, Canada
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Regeneron PharmaceuticalsCompletedHomozygous Familial HypercholesterolemiaUnited States, Netherlands, South Africa, Australia, Austria, Canada, Czechia, France, Greece, Italy, Japan, Ukraine
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ReveraGen BioPharma, Inc.University of Pittsburgh; Cooperative International Neuromuscular Research...CompletedDuchenne Muscular DystrophyUnited States, Canada, United Kingdom, Sweden, Australia, Israel
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Universidad de GranadaUnknown
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University of British ColumbiaHuntington Study Group; Huntington Society of CanadaCompletedHuntington DiseaseCanada
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HealthCore-NERINational Heart, Lung, and Blood Institute (NHLBI)CompletedThalassemiaUnited States, Canada
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Merck Sharp & Dohme LLCActive, not recruitingHypercholesterolemia | Familial HypercholesterolemiaUnited States, Australia, Brazil, Canada, Chile, Colombia, Czechia, Finland, Hong Kong, Hungary, Israel, Netherlands, New Zealand, Norway, Singapore, Spain, Taiwan