- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Genetic Diseases, Inborn in China
Total 31698 results
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Sun Yat-sen UniversityUnknownGraves' OphthalmopathyChina
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Jie ShenZhujiang Hospital; The Fifth Affiliated Hospital of Southern Medical University and other collaboratorsUnknownThyroid Associated OphthalmopathyChina
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First Affiliated Hospital of Guangxi Medical UniversityGenmedicn Biopharma Ltd.RecruitingTransfusion-dependent α-ThalassemiaChina
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Sun Yat-sen UniversityRecruitingThalassemia Major | Transfusion-dependent AnemiaChina
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Nanjing Medical UniversityRecruitingMyocardial Fibrosis | Cardiac RehabilitationChina
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Institute of Hematology & Blood Diseases Hospital...Sinocelltech Ltd.RecruitingHemophilia A With InhibitorChina
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Institute of Hematology & Blood Diseases HospitalRecruiting
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Beijing Children's HospitalUnknownHemophilia A With InhibitorChina
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Eisai Co., Ltd.Completed
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Aier Eye Hospital, GuangzhouCompletedMacular Degeneration | Low Vision | Stargardt DiseaseChina
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Bioray LaboratoriesXiangya Hospital of Central South University; The 923rd Hospital of Joint Logistics...Recruiting
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Huashan HospitalEnrolling by invitation
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Kanglin Biotechnology (Hangzhou) Co., Ltd.Not yet recruitingTransfusion-dependent Beta-ThalassemiaChina
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BGI-researchShenzhen Children's HospitalNot yet recruiting
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EdiGene (GuangZhou) Inc.PLA 923 HospitalActive, not recruitingTransfusion Dependent Beta-ThalassaemiaChina
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Sun Yat-sen UniversityRecruitingThyroid Associated OphthalmopathyChina
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Sun Yat-sen UniversityUnknown
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Andrea DoriaBeijing Children's Hospital, Baxalta US Inc.Completed
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Capital Medical UniversityWangjing Hospital, China Academy of Chinese Medical Sciences; Bejing Fengtai...RecruitingCerebral Amyloid Angiopathy | Intracerebral Hemorrhage LobarChina
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CorrectSequence Therapeutics Co., LtdRecruitingBeta-Thalassemia MajorChina
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Peking Union Medical College HospitalRecruiting
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Sun Yat-sen UniversityCompletedImmune System Diseases | Autoimmune Diseases | Eye Diseases | Endocrine System Diseases | Thyroid Diseases | Eye Diseases, Hereditary | Graves Ophthalmopathy | Graves Disease | HyperthyroidismChina
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Zhang Lei, MDHenan Cancer Hospital; Qilu Hospital of Shandong University; Tianjin First Central... and other collaboratorsCompletedAcquired Hemophilia AChina
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Institute of Hematology & Blood Diseases HospitalRecruiting
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Hangzhou Zede Pharma-Tech Co., Ltd.RecruitingIron Overload | ThalassemiaChina
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Hangzhou Zede Pharma-Tech Co., Ltd.Completed
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Shanghai Children's Medical CenterUnknownSevere Combined ImmunodeficiencyChina
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Innovent Biologics (Suzhou) Co. Ltd.RecruitingThyroid Eye Disease, TEDChina
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Alexion Pharmaceuticals, Inc.RecruitingHypophosphatasiaItaly, Spain, Israel, Korea, Republic of, Belgium, Germany, United States, China, France, Taiwan, Austria, Japan, India, Australia, Argentina, Poland, Turkey, Brazil, Canada, Thailand, United Kingdom, Slovakia, Czechia
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Sun Yat-sen UniversityRecruiting
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Sun Yat-sen UniversityRecruiting
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Sun Yat-sen UniversityWithdrawn
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Second Affiliated Hospital of Nanchang UniversityEnrolling by invitationPrimary Aldosteronism Due to Adrenal Hyperplasia (Bilateral)China
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GeneScience Pharmaceuticals Co., Ltd.The First Affiliated Hospital with Nanjing Medical University; First Affiliated... and other collaboratorsUnknown
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Sun Yat-Sen Memorial Hospital of Sun Yat-Sen UniversityNot yet recruitingAcute Leukemia | Thalassemia MajorChina
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Peking Union Medical College HospitalUnknownAcquired Hemophilia AChina
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Children's Hospital of Fudan UniversityCompletedSevere Combined Immunodeficiency | Neonatal ScreeningChina
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Xinhua Hospital, Shanghai Jiao Tong University...UnknownIntellectual Disability | Rare Diseases | Multiple Congenital AnomalyChina
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Sun Yat-Sen Memorial Hospital of Sun Yat-Sen UniversityRecruitingThyroid Eye DiseaseChina
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Ascendis Pharma A/SActive, not recruiting
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Novartis PharmaceuticalsTerminatedGouty ArthritisChina, Poland, Singapore, Argentina
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Shanghai High Myopia Study GroupEye & ENT Hospital of Fudan UniversityRecruiting
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PfizerCompletedAtopic DermatitisChina, Japan, Korea, Republic of
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Zeria PharmaceuticalCompletedPrimary Hypophosphatemic RicketsJapan
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Second Affiliated Hospital, School of Medicine,...The First Affiliated Hospital with Nanjing Medical University; The First People... and other collaboratorsRecruitingAsthma | Rhinitis, Allergic | Dermatitis, Atopic | UrticariaChina
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Yiqi DuUnknown
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Evidence Based Cataract Study GroupEye & ENT Hospital of Fudan UniversityRecruitingVisual Outcome | Congenital Cataract | Traumatic Cataract | Pediatric Cataract | Genetic AnticipationChina
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Institute of Hematology & Blood Diseases HospitalRecruitingGene Therapy | Transfusion-dependent Beta-ThalassemiaChina
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Dalian UniversityCompleted
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Changhai HospitalUnknownDiagnoses Disease | Urothelial Carcinoma | Chromosomal Abnormality | Urine MarkingChina