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Clinical Trials on Genetic Diseases, Inborn in Denmark
Total 9308 results
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Henning BliddalCambridge Weight Plan Limited; Oak Foundation; The Danish Rheumatism AssociationCompleted
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Rigshospitalet, DenmarkCompleted
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Chiesi Farmaceutici S.p.A.CromsourceCompletedAlpha-MannosidosisFrance, Denmark, Austria, Germany, Italy
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Copenhagen University Hospital at HerlevUnknownDepression | Pathologic Processes | Heart Diseases | Cardiovascular Diseases | Congenital Abnormalities | Death | Death, Sudden | Arrhythmias, Cardiac | ADHD | Heart Arrest | Heart Defects, Congenital | Cardiovascular Abnormalities | Genetic Disease | Death, Sudden, Cardiac | Psychiatric Disorder | Genetic Syndrome | Long... and other conditionsDenmark
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University of Southern DenmarkRegion of Southern DenmarkCompletedMultiple Sclerosis | Drug Effect | Genetic Disease | Central Nervous System Lesion | Neurophysiologic Abnormality | Neurodegeneration | Neurologic Deficits | Peripheral Nervous System ProblemDenmark
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University of Southern DenmarkOdense University Hospital; Aarhus University HospitalCompleted
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University of AarhusAarhus University Hospital; University of East Anglia; Kolding SygehusCompleted
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Boston Scientific CorporationCompleted
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Telethon Kids InstituteRigshospitalet, Denmark; University of Haifa; Ariel UniversityUnknownRett SyndromeDenmark, Israel
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Rigshospitalet, DenmarkCompleted
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Studies&MeBispebjerg Hospital; Biotx.ai; Life&Brain; Stanford Health CareWithdrawnEczema | Atopic Dermatitis | DNAUnited States, Denmark
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Swedish Orphan BiovitrumCompletedEfficacy and Safety of Once Daily Dosing Compared to Twice Daily Dosing of Nitisinone in HT-1 (HT-1)Hereditary Tyrosinemia, Type IBelgium, Denmark, France, Germany, Sweden
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Torben HarsløfOdense University HospitalActive, not recruiting
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Aarhus University HospitalCompletedFuchs' Endothelial Corneal DystrophyDenmark
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Zymenex A/SEuropean CommissionCompletedA Placebo-Controlled Phase 3 Trial of Repeated Lamazym Treatment of Subjects With Alpha-MannosidosisAlpha-MannosidosisDenmark, United Kingdom, France, Germany, Poland
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Grete Andersen, MDAP Moeller Foundation; The Danish Rheumatism Association; Aase and Ejnar Danielsens... and other collaboratorsCompletedFacioscapulohumeral Muscle DystrophyDenmark
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Danish Study GroupDanish Heart FoundationCompletedHeart Failure | Dilated Cardiomyopathy | Reduced LVEFDenmark
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Odense University HospitalCompletedHealth Knowledge, Attitudes, Practice | Downs SyndromeDenmark
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Rigshospitalet, DenmarkCompleted
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Novo Nordisk A/SCompletedPrader-Willi Syndrome | Genetic DisorderGermany, Denmark, Switzerland
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JKastrupUniversity Medical Centre LjubljanaUnknownNon-ischemic Dilated CardiomyopathyDenmark
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Jacob ThyssenLEO PharmaCompletedAtopic Dermatitis | Atopic EczemaDenmark
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University of AarhusCompleted
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University Hospital, Gentofte, CopenhagenCompletedType 2 Diabetes | Atopic Dermatitis/EczemaDenmark
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Novo Nordisk A/SEnrolling by invitationHaemophilia ADenmark
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Rigshospitalet, DenmarkUnknownOculopharyngeal Muscular DystrophyDenmark
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Grete Andersen, MDCompletedHyperkalemic Periodic Paralysis | Myotonia Congenita | Paramyotonia Congenita | Dystrophia Myotonica Type 1 | Potassium-Aggravated MyotoniaDenmark
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University of AarhusUnknownPseudohypoparathyroidism | Idiopathic Hypoparathyroidism | Autosomal Dominant HypocalcaemiaDenmark
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Pharmacosmos A/SICON plcRecruitingBeta Thalassemia Major AnemiaDenmark
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University of AarhusUnknownGlycogen Storage Disease Type 2 | Dystrophia MyotonicaDenmark
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Bispebjerg HospitalCompletedEhlers-Danlos Syndrome, ClassicDenmark
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Rigshospitalet, DenmarkRecruitingLimb Girdle Muscular DystrophyDenmark
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Rigshospitalet, DenmarkCompletedBecker Muscular Dystrophy | Limb-Girdle Muscular Dystrophy Type 2IDenmark
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ShireCompletedFabry DiseaseFinland, Sweden, Germany, Belgium, Czechia, Denmark
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Grete Andersen, MDCompletedFSHD - Facioscapulohumeral Muscular DystrophyDenmark
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UNION therapeuticsCompletedAtopic DermatitisBulgaria, Denmark, Poland
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LEO PharmaCompletedAtopic DermatitisUnited Kingdom, Finland, Canada, Denmark
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Rigshospitalet, DenmarkCompletedNon-Dystrophic Myotonia | Myotonia CongenitaDenmark
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University of AarhusCompletedX-linked Hypophosphatemia | Hereditary HypophosphatemiaDenmark
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University of AarhusUnknownCystic Fibrosis | Gastrointestinal MotilityDenmark
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Karen Brorup Heje PedersenCompletedHealthy Subjects | Spinal and Bulbar Muscular AtrophyDenmark
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Blueskin ASRecruitingPsoriasis | Atopic Dermatitis | Vitiligo | Alopecia AreataDenmark
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Rigshospitalet, DenmarkCompletedLimb-girdle Muscular DystrophyDenmark
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Odense University HospitalCompletedThyroid Associated Ophthalmopathy | Graves´ DiseaseDenmark
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Rigshospitalet, DenmarkCompleted
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Rigshospitalet, DenmarkGilead SciencesCompleted
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Grete Andersen, MDCompletedFSHD - Facioscapulohumeral Muscular DystrophyDenmark
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CSL BehringCompletedHemophilia BGermany, Denmark, Netherlands
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AstraZenecaCompletedHomozygous Familial Hypercholesterolemia (HoFH)Malaysia, Canada, Taiwan, Belgium, Denmark, Israel