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- US Clinical Trials Registry
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Clinical Trials on Genetic Diseases, X-Linked in Switzerland
Total 339 results
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Eli Lilly and CompanyIncyte CorporationCompletedAtopic DermatitisBelgium, Netherlands, Japan, Spain, Switzerland, United Kingdom, Germany, France, Austria, Russian Federation, Poland, Italy, Brazil, Finland
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Novo Nordisk A/SEnrolling by invitationHaemophilia AAustria, Spain, Bulgaria, Croatia, Estonia, Hungary, Italy, Lithuania, Portugal, Greece, Germany, Czechia, Slovenia, Switzerland, Slovakia
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University of UlmUniversity of Pisa; IRCCS Azienda Ospedaliero-Universitaria di Bologna; Medical... and other collaboratorsRecruitingLipodystrophy Acquired | Lipodystrophy CongenitalAustria, France, Germany, Hungary, Italy, Portugal, Spain, Netherlands, Russian Federation, Slovenia, Switzerland, Turkey, United Kingdom
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Novartis PharmaceuticalsCompletedTreatment of Early Pulmonary Infections With P. Aeruginosa in Cystic Fibrosis PatientsEgypt, Greece, Hungary, Russian Federation, Canada, Germany, France, Italy, Switzerland, Romania
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Novartis PharmaceuticalsCompletedCystic FibrosisSpain, Germany, Switzerland, United Kingdom, Ireland
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CSL BehringCompletedHemophilia AAustria, Belgium, France, Germany, Italy, Spain, Switzerland
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CENTOGENE GmbH RostockTerminatedDeafness | Immunodeficiency | Mental Retardation | Gingival Hypertrophy | Skeletal Abnormalities | Facial DysmorphismGermany, Switzerland
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BayerActive, not recruitingHemophilia ACanada, Japan, Spain, United States, Germany, Sweden, Belgium, Brazil, Greece, Italy, Netherlands, Taiwan, Denmark, Kuwait, Saudi Arabia, United Arab Emirates, Norway, Colombia, Switzerland, Slovenia
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AbbVieRecruitingAtopic DermatitisAustralia, Austria, Canada, Spain, Switzerland, Taiwan, United Arab Emirates, Poland, Czechia, Greece, Russian Federation, Italy, Israel, Argentina, Hungary, Mexico
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Kaleido BiosciencesTerminatedUrea Cycle DisorderBelgium, United States, Spain, United Kingdom, Germany, Switzerland, Turkey
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AmgenRecruitingOsteogenesis ImperfectaUnited States, United Kingdom, Hungary, Germany, Switzerland, Spain, Japan, France, Belgium, Poland, Australia, Austria, Slovakia, Turkey, Canada
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Eli Lilly and CompanyIncyte CorporationCompletedAtopic DermatitisSpain, Korea, Republic of, France, Taiwan, India, Australia, Germany, Japan, Italy, Switzerland, Israel, Argentina, Austria, Czechia, Hungary, Mexico, Poland, Russian Federation, Denmark
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Vertex Pharmaceuticals IncorporatedCompletedCystic FibrosisCanada, France, Germany, United Kingdom, Israel, Australia, Spain, Netherlands, Denmark, Switzerland
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Glanzmann's DiseaseSpain, Bulgaria, Pakistan, Belgium, Germany, France, United Kingdom, Italy, Hungary, Netherlands, United States, Algeria, Austria, Sweden, Switzerland
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Vertex Pharmaceuticals IncorporatedCompletedCystic FibrosisCanada, France, United Kingdom, Israel, Australia, Spain, Germany, Netherlands, Denmark, Switzerland
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AmgenActive, not recruitingAtopic DermatitisBelgium, Spain, China, Germany, United States, Austria, France, Hungary, Switzerland, Canada, United Kingdom, Bulgaria, Australia, Netherlands, Malaysia, Singapore, Slovenia, Italy, Japan, Argentina, Greece, Turkey, Poland, Puerto Rico, Romani... and more
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AbbVieActive, not recruitingAtopic DermatitisUnited States, Argentina, Australia, Bosnia and Herzegovina, Bulgaria, Canada, China, Colombia, Croatia, Denmark, Estonia, Finland, France, Germany, Italy, Japan, Malaysia, New Zealand, Puerto Rico, Romania, Russian Federation, Sw... and more
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Bambino Gesù Hospital and Research InstituteRadboud University Medical Center; University of Exeter; Consorzio per Valutazioni...RecruitingCystic Fibrosis | AspergillosisIreland, Spain, Netherlands, France, United Kingdom, Czechia, Germany, Greece, Italy, Portugal, Switzerland
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Baxalta now part of ShireCompletedHemophilia AUnited States, Spain, Netherlands, United Kingdom, Bulgaria, Lithuania, Russian Federation, Switzerland, Ukraine
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Novartis PharmaceuticalsCompletedHereditary Periodic FeversBelgium, Italy, Japan, Russian Federation, Turkey, Spain, Germany, United Kingdom, France, United States, Ireland, Israel, Canada, Hungary, Netherlands, Switzerland
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BiositeCompletedStroke | Stroke Mimic(Conditions Presenting With Stroke-like Conditions)United States, Canada, Germany, Switzerland, United Kingdom
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AbbVieActive, not recruitingAtopic DermatitisUnited States, Australia, Belgium, Bulgaria, Canada, China, Denmark, France, Germany, Hungary, Italy, Korea, Republic of, Mexico, Netherlands, Poland, Portugal, Puerto Rico, Romania, Slovakia, South Africa, Spain, Sweden, Switzerland, Taiwa... and more
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Alnylam PharmaceuticalsCompletedPrimary Hyperoxaluria Type 1 (PH1)United States, France, United Kingdom, Switzerland, Netherlands, Israel, Germany, United Arab Emirates
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Genzyme, a Sanofi CompanyCompletedThyroid CancerItaly, Spain, Romania, Netherlands, Canada, United States, Switzerland, Australia
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AmgenRecruitingAtopic DermatitisUnited States, Japan, Korea, Republic of, Australia, Taiwan, Spain, Switzerland, Germany, Austria, Denmark, China, Netherlands, Hungary, Czechia, Poland, Brazil, France, Greece, Portugal, Italy, Finland, Argentina, Bulgaria, Slovenia, E... and more
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Novo Nordisk A/SCompletedChronic Kidney Disease | Turner Syndrome | Noonan Syndrome | Chronic Renal Insufficiency | Growth Hormone Disorder | Growth Hormone Deficiency in Children | Adult Growth Hormone Deficiency | Genetic Disorder | Foetal Growth Problem | Small for Gestational AgeIsrael, Saudi Arabia, Spain, Argentina, Russian Federation, Germany, Netherlands, Italy, Belgium, United Kingdom, Slovenia, Ireland, Sweden, Denmark, Hungary, Finland, Norway, France, Czechia, Lithuania, Luxembourg, Serbia, Switzerland
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Idorsia Pharmaceuticals Ltd.CompletedGM2 Gangliosidosis | GM1 Gangliosidosis | Tay-Sachs Disease | Sandhoff Disease | Gaucher Disease, Type 2 | AB Variant Gangliosidosis GM2United States, Spain, Germany, Italy, Belgium, Brazil, France, Portugal, Switzerland, United Kingdom
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia AUnited States, Germany, Switzerland, United Kingdom, Italy, Japan, Turkey
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ShireTakeda Development Center Americas, Inc.Active, not recruitingHereditary Angioedema (HAE)Germany, Switzerland, Spain, Israel, Italy, Austria, Portugal, Kuwait
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Swedish Orphan BiovitrumActive, not recruitingHemophilia ASpain, Germany, Czechia, Italy, Estonia, Finland, Greece, Netherlands, Saudi Arabia, Slovenia, Sweden, Switzerland, United Kingdom
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Novo Nordisk A/SCompletedHealthy Volunteers | Haemophilia A With or Without InhibitorsUnited States, Germany, Spain, Austria, Bulgaria, Italy, Japan, South Africa, Switzerland, Turkey, United Kingdom, Poland
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IntraBio IncActive, not recruitingNiemann-Pick Disease, Type CUnited States, Australia, United Kingdom, Germany, Slovakia, Netherlands, Czechia, Switzerland
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KemPharm Denmark A/SCompletedNiemann-Pick Disease, Type CSpain, France, United Kingdom, Switzerland, Denmark, Poland, Italy, Germany
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BioCryst PharmaceuticalsCompletedHereditary Angioedema (HAE)Canada, United Kingdom, Germany, Spain, Australia, Hungary, Italy, Austria, North Macedonia, Denmark, Switzerland
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Ascendis Pharma A/SCompletedAchondroplasiaUnited States, Australia, Austria, Germany, China, Canada, Denmark, France, Ireland, Italy, New Zealand, Portugal, Spain, Switzerland, United Kingdom
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University Hospital, GenevaCompletedAfibrinogenemia, CongenitalFrance, Turkey, Switzerland, Netherlands, Spain, India, Poland, Canada, United States, Algeria, Egypt, Germany, Italy, Japan, Kuwait, Lebanon, Morocco, Pakistan, Serbia, Slovakia, Tunisia
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BioCryst PharmaceuticalsCompletedHereditary Angioedema (HAE)Austria, Denmark, France, Germany, Hungary, Israel, Italy, North Macedonia, Poland, Romania, Switzerland, United Kingdom
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Jaeb Center for Health ResearchFoundation Fighting BlindnessRecruitingRetinitis Pigmentosa | Inherited Retinal DegenerationUnited States, United Kingdom, France, Finland, Israel, Netherlands, Switzerland, Australia, Canada, Brazil, Mexico
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Vertex Pharmaceuticals IncorporatedEnrolling by invitationCystic FibrosisUnited States, Australia, Germany, Sweden, Switzerland, France, Netherlands, United Kingdom
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Vertex Pharmaceuticals IncorporatedActive, not recruitingCystic FibrosisUnited States, Australia, Germany, Sweden, Switzerland, France, Netherlands, United Kingdom
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Pfizer's Upjohn has merged with Mylan to form Viatris...CompletedFamilial HypercholesterolemiaUnited States, Spain, Turkey, Canada, Belgium, Germany, Greece, Hungary, Italy, Norway, Poland, Puerto Rico, Russian Federation, Slovakia, Switzerland
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University Medical Center GoettingenCompletedMyocardial Infarction | Coronary Artery Disease | Dilated Cardiomyopathy | Implantable Defibrillator UserHungary, Poland, Belgium, Bulgaria, Croatia, Czechia, Denmark, Finland, Germany, Greece, Netherlands, Slovakia, Spain, Sweden, Switzerland, United Kingdom
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PfizerTerminatedAchondroplasiaUnited States, Canada, China, Japan, Australia, Germany, France, United Kingdom, Denmark, Belgium, Italy, Portugal, Spain, Switzerland
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ZevraDenmarkActive, not recruitingNiemann-Pick Disease, Type CUnited States, Spain, United Kingdom, Denmark, France, Germany, Italy, Poland, Switzerland
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AmgenCompletedHyperlipidemiaCanada, France, Netherlands, United Kingdom, New Zealand, South Africa, Spain, United States, Australia, Germany, Sweden, Hong Kong, Switzerland, Norway
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CSL BehringCompletedCongenital Hemophilia AUnited States, Austria, Germany, Malaysia, Netherlands, Philippines, Ukraine, Romania, Spain, Australia, France, Georgia, Italy, Lebanon, Poland, Portugal, Switzerland, Thailand, Turkey
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Johns Hopkins UniversityMayo Clinic; Medical University of Graz; Radboud University Medical Center; University... and other collaboratorsRecruitingRetinitis PigmentosaUnited States, Austria, Mexico, Netherlands, United Kingdom, Germany, Canada, Switzerland
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Alnylam PharmaceuticalsRecruitingPrimary Hyperoxaluria Type 1France, Spain, United States, Israel, Belgium, Switzerland, Germany, United Kingdom, Italy, Canada
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Bioverativ, a Sanofi companyCompletedHemophilia ATurkey, Australia, Canada, France, Germany, Hungary, Ireland, Italy, Netherlands, Spain, Sweden, Switzerland, Taiwan, United Kingdom, United States
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Agios Pharmaceuticals, Inc.Active, not recruitingPediatric Pyruvate Kinase Deficiency | Pediatric Hemolytic AnemiaUnited States, Spain, Denmark, Turkey, Netherlands, Czechia, United Kingdom, Germany, Canada, Switzerland