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Clinical Trials on Genetic Mutation in New Zealand
Total 2574 results
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Lenus Therapeutics, LLCTerminatedDystrophic Epidermolysis Bullosa | Junctional Epidermolysis BullosaUnited States
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Gilead SciencesCompletedCystic FibrosisUnited States, Canada, Australia, New Zealand
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Ultragenyx Pharmaceutical IncCompletedHereditary Inclusion Body Myopathy (HIBM)United States
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HanAll BioPharma Co., Ltd.CompletedMild to Moderate Atopic DermatitisUnited States
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National Center for Research Resources (NCRR)Icahn School of Medicine at Mount SinaiCompletedMetabolism, Inborn Errors | Leukodystrophy, Globoid Cell | Tay-Sachs Disease | Porphyria, ErythropoieticUnited States
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Wyeth is now a wholly owned subsidiary of PfizerCompleted
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RBP4 Pty LtdBelite Bio, IncCompleted
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Rockefeller UniversityNational Heart, Lung, and Blood Institute (NHLBI)RecruitingGlanzmann ThrombastheniaUnited States
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Columbia UniversityCompleted
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Deepa ManwaniRecruiting
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New York Medical CollegeUnknownSickle Cell Disease | AntibioticsUnited States
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BioMimetix JV, LLCCompletedPsoriasis | Atopic DermatitisUnited States
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Astellas Pharma IncCompleted
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Icahn School of Medicine at Mount SinaiNational Heart, Lung, and Blood Institute (NHLBI)Enrolling by invitationSickle Cell DiseaseUnited States
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Memorial Sloan Kettering Cancer CenterCompletedBeta Thalassemia Major | Congenital AnemiasUnited States
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Homology Medicines, IncWithdrawnMucopolysaccharidosis IIUnited States, Canada
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Arcutis Biotherapeutics, Inc.CompletedAtopic Dermatitis EczemaUnited States, Canada
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The University of QueenslandRecruitingPulmonary Fibrosis | Dyskeratosis Congenita | Telomere Shortening | Telomere DiseaseAustralia
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Swathi SethuramCompletedPhelan McDermid SyndromeUnited States
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Memorial Sloan Kettering Cancer CenterActive, not recruitingConfirmed Diagnosis of ß-thalassemia MajorUnited States
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Columbia UniversityActive, not recruitingSickle Cell Disease | Beta ThalassemiaUnited States
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Weill Medical College of Cornell UniversityWithdrawnVon Willebrand DiseaseUnited States
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Icahn School of Medicine at Mount SinaiTerminatedSickle Cell DiseaseUnited States
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Novartis PharmaceuticalsCompletedTransfusional HemosiderosisUnited States
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PfizerActive, not recruitingMuscular Dystrophy, DuchenneUnited States, Australia
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Rutgers, The State University of New JerseyNational Cancer Institute (NCI)CompletedMelanoma | Health Status Unknown | Dysplastic Nevus | No Evidence of DiseaseUnited States
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PfizerRecruiting
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Mylan Inc.DPT Laboratories, Ltd.CompletedAtopic DermatitisUnited States, Dominican Republic, Honduras
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Icahn School of Medicine at Mount SinaiRecruitingAutoimmune Diseases | Primary Immune Deficiency | Immunological DiseaseUnited States
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Columbia UniversityTerminatedSickle Cell Disease | Vaso-occlusive CrisisUnited States
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Icahn School of Medicine at Mount SinaiCompletedPolycystic Kidney DiseaseUnited States
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BayerCompleted
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RAPT Therapeutics, Inc.SuspendedAtopic DermatitisUnited States, Canada
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Scioderm, Inc.Amicus TherapeuticsTerminatedEpidermolysis BullosaPoland, Spain, Serbia, Netherlands, United States, Austria, Australia, Israel, Germany, France, United Kingdom, Lithuania
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ASLAN PharmaceuticalsRecruitingAtopic DermatitisUnited States, Canada
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New York Institute of TechnologyRecruitingPain, Chronic | Ehlers-Danlos SyndromeUnited States
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Ultragenyx Pharmaceutical IncMereo BioPharmaTerminatedOsteogenesis ImperfectaUnited States
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Academic and Community Cancer Research UnitedNational Cancer Institute (NCI)RecruitingBile Duct Adenocarcinoma | Fanconi Anemia Complementation Group Gene Mutation | Metastatic Bile Duct Carcinoma | PTEN Gene DeletionUnited States
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US Department of Veterans AffairsWithdrawn
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Elizabeth Berry-KravisNational Institute of Neurological Disorders and Stroke (NINDS); Novartis PharmaceuticalsCompleted
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Jiangsu Atom Bioscience and Pharmaceutical Co.,...Enrolling by invitationGoutUnited States, Georgia, Australia, Guatemala, Taiwan
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PTC TherapeuticsCompletedDuchenne Muscular DystrophyUnited States
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Baxalta now part of ShireCompletedHemophilia BRussian Federation, Ukraine, India, Poland, Romania, United Kingdom
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Calithera Biosciences, IncTerminatedNon-Small Cell Lung Cancer | Squamous Non-small-cell Lung Cancer | NFE2L2 Gene Mutation | Squamous Non-Small Cell Neoplasm of LungUnited States
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Anavex Life Sciences Corp.Completed
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Janssen Research & Development, LLCTerminatedDermatitis, AtopicUnited States, Germany, Canada, Poland, Japan
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State University of New York - Upstate Medical...Terminated
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University of RochesterCompletedFacioscapulohumeral Muscular DystrophyUnited States
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Ritter Pharmaceuticals, Inc.CompletedLactose IntoleranceUnited States