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Clinical Trials on Genetic Mutations in Austria
Total 1149 results
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Academisch Medisch Centrum - Universiteit van Amsterdam...UnknownHemophiliaNetherlands, Austria, Australia, Belgium, Canada, Finland, Germany, Italy, Spain, United Kingdom
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Vyne Therapeutics Inc.CompletedAtopic DermatitisUnited States, Australia
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Archemix Corp.CompletedPurpura, Thrombotic Thrombocytopenic | Von Willebrand Disease Type-2bAustria
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Center for Eye Research AustraliaCompleted
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Santalis Pharmaceuticals, Inc.Derm Research, PLLC; ClinDatrix, Inc.; Texas Dermatology and Laser Specialists; Clinical Trials of Texas, Inc... and other collaboratorsCompletedEczema | Atopic DermatitisUnited States
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RBP4 Pty LtdBelite Bio, IncCompleted
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BayerTerminatedHemophilia A and BAustralia, United Kingdom, Taiwan, Japan, Korea, Republic of, Austria, Bulgaria, Hungary, Italy, France, New Zealand
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CSL LimitedCompletedPrimary Immune Deficiency (PID)Australia
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Orthopedic Hospital Vienna SpeisingCompleted
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Ribon Therapeutics, Inc.RecruitingAtopic DermatitisAustralia, New Zealand
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Otsuka Pharmaceutical Development & Commercialization...CompletedAtopic DermatitisPoland, United States, Australia
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The University of Western AustraliaNational Health and Medical Research Council, AustraliaUnknownFamilial Hypercholesterolaemia | HypertriglyceridaemiaAustralia
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Scioderm, Inc.Amicus TherapeuticsCompletedEpidermolysis BullosaItaly, Spain, Serbia, United States, Australia, Netherlands, Austria, Germany, Israel, Lithuania, France, United Kingdom, Poland
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Castle Creek Pharmaceuticals, LLCTerminatedEpidermolysis Bullosa SimplexUnited States, Israel, Australia, Austria, France, Germany, Netherlands, United Kingdom
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BayerActive, not recruitingHemophilia ASpain, Germany, Austria, Greece, Italy, Slovenia
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Calithera Biosciences, IncTerminatedNon-Small Cell Lung Cancer | Non-squamous Non-small-cell Lung Cancer | Non-Squamous Non-Small Cell Neoplasm of Lung | KEAP1 Gene Mutation | NRF2 Gene Mutation | NFE2L2 Gene MutationUnited States
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Medical University of GrazActive, not recruitingPrimary Immunodeficiency | Immune Thrombocytopenia | Autoimmune Hemolytic Anemia | Evans SyndromeAustria
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ASLAN PharmaceuticalsCompleted
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PfizerActive, not recruitingMuscular Dystrophy, DuchenneUnited States, Australia
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Anavex Life Sciences Corp.Completed
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BayerCompletedHemophilia AGermany, Spain, Austria, Italy, Slovenia, Greece, Netherlands
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DermBiont, Inc.Derm Research, PLLC; Northsoundderm; ClearDermatologyandAestheticsCenterTerminated
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Savara Inc.INC Research LimitedCompleted
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Novartis PharmaceuticalsCompletedAdvanced Solid Tumors With Alterations of FGFR1, 2 and or 3 | Squamous Lung Cancer With FGFR1 Amplification | Bladder Cancer With FGFR3 Mutation or Fusion | Advanced Solid Tumors With FGFR1 Amplication | Advanced Solid Tumors With FGFR2 Amplication | Advanced Solid Tumors With FGFR3 MutationFrance, Spain, Taiwan, Germany, Netherlands, Singapore, United States, Australia, Korea, Republic of, Thailand, Israel, Italy, Turkey, Austria
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Regeneron PharmaceuticalsSanofiCompletedAtopic DermatitisGermany, New Zealand, Australia
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Ultragenyx Pharmaceutical IncCompletedOrnithine Transcarbamylase DeficiencyUnited States
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Nacuity Pharmaceuticals, Inc.Recruiting
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Pixium Vision SACompletedRetinitis Pigmentosa | Choroideremia | Cone Rod DystrophyAustria, Spain, United Kingdom, France, Germany
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MyoKardia, Inc.CompletedDilated CardiomyopathyAustralia
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Amicus TherapeuticsCompletedFabry DiseaseFrance, Austria, United States, Belgium, Japan, United Kingdom, Denmark, Brazil, Australia, Italy
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Ionis Pharmaceuticals, Inc.Completed
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QED Therapeutics, Inc.Helsinn Healthcare SATerminatedFGFR2 Gene Mutation | Advanced CholangiocarcinomaKorea, Republic of, United States, Belgium, Spain, Taiwan, China, United Kingdom, France, Canada, Germany, Thailand, Italy, Portugal, Australia, Puerto Rico
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Arrowhead PharmaceuticalsActive, not recruitingAlpha 1-Antitrypsin DeficiencyAustria, Germany, United Kingdom
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Regeneron PharmaceuticalsCompletedHomozygous Familial HypercholesterolemiaUnited States, Australia, Austria, Netherlands, Taiwan, Ukraine
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Spark TherapeuticsChildren's Hospital of Philadelphia; University of Pittsburgh; St. James's Hospital... and other collaboratorsTerminated
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Chiesi Farmaceutici S.p.A.CromsourceCompletedAlpha-MannosidosisFrance, Denmark, Austria, Germany, Italy
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Ethicare GmbHUnknownHeart Failure | Dilated CardiomyopathyAustria, United Kingdom, Hungary, Netherlands, Serbia
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NestléCompletedPhenylketonuriaAustralia, Germany
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Orphatech Pharmaceuticals, GmbHWithdrawnMolybdenum Cofactor Deficiency Type AAustralia
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Reata, a wholly owned subsidiary of BiogenAbbVie; Friedreich's Ataxia Research AllianceActive, not recruitingFriedreich AtaxiaUnited States, Australia, Austria, Italy, United Kingdom
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Bond BiosciencesTerminatedHereditary HemochromatosisAustralia
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PfizerCompletedHemophilia BGermany, Austria
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Pierre Fabre MedicamentClinactCompletedMetastatic Colorectal Cancer | BRAF V600E Mutation PositiveFrance, United Kingdom, Spain, Belgium, Germany, Italy, Austria
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University College London HospitalsCompletedBreast Cancer | Hereditary Breast/Ovarian Cancer (brca1, brca2) | brca1 Mutation Carrier | brca2 Mutation CarrierAustralia, Israel, United Kingdom, Spain, Sweden, Portugal
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Ascendis Pharma Growth Disorders A/SEnrolling by invitationAchondroplasiaUnited States, Australia, Denmark, Ireland, Austria, Germany, New Zealand
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Baxalta now part of ShireCompletedAlpha 1-Antitrypsin DeficiencyNew Zealand, Australia
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CSL BehringRecruiting
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Murdoch Childrens Research InstituteCompletedFacio-Scapulo-Humeral Dystrophy | FSHD2 | FSHD1Australia
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BayerCompletedHemophilia ASwitzerland, France, Spain, Sweden, Austria, Italy, Belgium, Denmark, Greece, Netherlands
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Genzyme, a Sanofi CompanyTerminatedFabry Disease | Alpha Galactosidase A DeficiencyUnited States, Austria, United Kingdom