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Clinical Trials on Genetic Predisposition to Disease in Colombia
Total 984 results
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Monica BhatiaCompletedSickle Cell Disease | Graft Versus Host DiseaseUnited States
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Novartis PharmaceuticalsRecruitingAcute Kidney Injury Due to SepsisUnited States, Canada, Turkey, United Kingdom, Thailand
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PfizerTerminatedHemophilia AUnited States, New Zealand
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AbbVieCompletedAtopic DermatitisUnited States, Australia, Canada, Finland, Germany, Japan, Netherlands, Spain
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Uta Lichter-KoneckiMedical College of Wisconsin; Children's National Research InstituteCompletedUrea Cycle Disorders | Organic AcidemiasUnited States
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Genzyme, a Sanofi CompanyCompleted
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PfizerTerminatedDuchenne Muscular DystrophyUnited States, Canada, United Kingdom, Japan, Italy
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University of British ColumbiaCanadian Cystic Fibrosis FoundationCompleted
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Ionis Pharmaceuticals, Inc.CompletedHuntington's DiseaseCanada, United Kingdom, Germany
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Hoffmann-La RocheCompleted
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Mendel TuchmanChildren's Hospital of Philadelphia; University of California, Los Angeles; Icahn... and other collaboratorsCompletedMethylmalonic Acidemia | Carbamoyl-Phosphate Synthase I Deficiency Disease | Propionic Acidemia, Type I and/or Type II | Ornithine Carbamoyltransferase DeficiencyUnited States
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Regeneron PharmaceuticalsSanofiActive, not recruitingAtopic DermatitisUnited States, Canada, Czechia, Germany, Hungary, Poland, United Kingdom
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National Institute of Allergy and Infectious Diseases...Rare Diseases Clinical Research Network; Primary Immune Deficiency Treatment...CompletedWiskott-Aldrich SyndromeUnited States, Canada
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Eli Lilly and CompanyDaiichi Sankyo, Inc.CompletedSickle Cell DiseaseUnited States
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PTC TherapeuticsCompletedNervous System Diseases | Genetic Diseases, Inborn | Genetic Diseases, X-Linked | Musculoskeletal Diseases | Muscular Diseases | Neuromuscular Diseases | Muscular Dystrophies | Muscular Disorders, Atrophic | Muscular Dystrophy, DuchenneUnited States, Spain, Korea, Republic of, Belgium, France, Canada, Australia, United Kingdom, Israel, Italy, Brazil, Chile, Czechia, Sweden, Switzerland, Turkey, Germany, Poland
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LEO PharmaCompletedAtopic DermatitisUnited States, Canada
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Children's National Research InstituteNational Center for Advancing Translational Sciences (NCATS)RecruitingHypoxic-Ischemic Encephalopathy | Urea Cycle Disorder | Organic Acidemia | Fatty Acid Oxidation Disorder | Maple Syrup Urine Disease | Glutaric Acidemia IUnited States
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Francis D. PaganiUniversity of Pennsylvania; Northwestern University; Georgetown University; Montefiore... and other collaboratorsTerminatedHeart Failure | Dilated CardiomyopathyUnited States
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Ultragenyx Pharmaceutical IncCompletedMucopolysaccharidosis | Sly Syndrome | Mucopolysaccharidosis VII | MPS VIISpain, United States, Portugal
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Children's National Research InstituteEmory University; University of Texas Southwestern Medical Center; Arizona State...Completed
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Hoffmann-La RocheCompleted
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Novartis PharmaceuticalsCompletedSickle Cell Disease (SCD)United States
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Genzyme, a Sanofi CompanyBioMarin/Genzyme LLCCompletedMucopolysaccharidosis I | Hurler-Scheie Syndrome | Hurlers SyndromeUnited States, Canada, Germany
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Allievex CorporationCompletedMucopolysaccharidosis Type IIIB | MPS III BUnited States, Taiwan, Spain, Colombia, Germany, United Kingdom, Turkey
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Medical College of WisconsinNational Cancer Institute (NCI); National Heart, Lung, and Blood Institute... and other collaboratorsCompletedChronic Granulomatous Disease | Hemophagocytic Lymphohistiocytosis | Leukocyte Adhesion Deficiency | Chronic Active Epstein-Barr Virus Infection | HIGM-1 | IPEXUnited States, Canada
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DS BiopharmaTerminatedAtopic DermatitisUnited States, Austria, Germany, Latvia, Poland
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Incyte CorporationRecruitingModerate to Severe AsthmaKorea, Republic of, United States, Spain, Poland, Japan, Canada, Germany, Belgium, Argentina
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CENTOGENE GmbH RostockWithdrawnMetabolic Disorders | Tyrosinosis | Hepatorenal Tyrosinemia | Fumarylacetoacetase Deficiency | Fah DeficiencyGermany, Sri Lanka, India
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SanofiActive, not recruitingDermatitis AtopicAustralia, United States, Argentina, Brazil, Canada, Colombia, France, Mexico, Netherlands
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AmgenCompletedDermatitis, Atopic DermatitisCanada, United States, Japan
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Boston Children's HospitalUniversity of California, San Diego; Food and Drug Administration (FDA); Angelman... and other collaboratorsRecruiting
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PTC TherapeuticsTerminatedNervous System Diseases | Genetic Diseases, Inborn | Genetic Diseases, X-Linked | Musculoskeletal Diseases | Muscular Diseases | Neuromuscular Diseases | Muscular Dystrophies | Muscular Disorders, Atrophic | Muscular Dystrophy, DuchenneUnited States, Spain, Korea, Republic of, Belgium, France, Canada, Australia, United Kingdom, Israel, Italy, Germany, Brazil, Bulgaria, Chile, Czechia, Poland, Sweden, Switzerland, Turkey
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Georgetown UniversityVirginia Commonwealth University; Basser Center for BRCA; Nueva Vida, Inc.; Capital... and other collaboratorsCompletedHereditary Breast and Ovarian Cancer SyndromeUnited States
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Annexon, Inc.CompletedHuntington DiseaseUnited States
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Regeneron PharmaceuticalsSanofiCompletedDermatitis, AtopicUnited States, Germany, Poland, United Kingdom
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PfizerCompletedHemophilia AUnited States, Argentina, Austria, Colombia, Croatia, Jordan, Mexico, New Zealand, Oman, Peru, Poland, Romania, Turkey
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Dermavant Sciences, Inc.CompletedAtopic DermatitisUnited States, Canada
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Cooperative International Neuromuscular Research...United States Department of Defense; National Institutes of Health (NIH); U.S... and other collaboratorsUnknownDuchenne Muscular DystrophyUnited States, Canada, Australia, India, Israel, Argentina, Italy, Sweden
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TakedaRecruitingAngioedema | Hereditary Angioedema (HAE)Canada
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National Institute of Allergy and Infectious Diseases...CompletedCongenital Heart Defects | Situs Inversus | Kartagener Syndrome | Ciliary Dyskinesia, PrimaryUnited States
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Allievex CorporationActive, not recruitingMucopolysaccharidosis Type IIIB | MPS III BGermany, United States, Turkey, United Kingdom, Colombia, Spain, Taiwan
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MedImmune LLCCompletedAtopic DermatitisUnited States, Germany, Canada, Australia, Poland, Japan
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Georgetown UniversityVirginia Commonwealth University; Cornell UniversityCompletedHereditary Breast and Ovarian CancerUnited States
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Georgetown UniversityCompletedHereditary Breast and Ovarian CancerUnited States
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Novo Nordisk A/SCompletedHaemophilia A | Haemophilia BUnited States
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AstraZenecaCompletedChronic Obstructive Pulmonary Disease | COPD | Moderate to Very Severe COPDUnited States, Canada
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BioMarin PharmaceuticalCompletedSickle Cell DiseaseUnited States
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Allakos Inc.TerminatedAtopic DermatitisUnited States, Germany
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The Hospital for Sick ChildrenCanadian Cystic Fibrosis FoundationCompletedCystic Fibrosis Pulmonary ExacerbationCanada
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Georgetown UniversityNational Cancer Institute (NCI); Virginia Commonwealth UniversityEnrolling by invitation