- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Genetic Study in Colombia
Total 923 results
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BioMarin PharmaceuticalCompletedPhenylketonuria (PKU)United States
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CENTOGENE GmbH RostockWithdrawnHypophosphatemia | Photophobia | Renal Fanconi SyndromeGermany, India, Sri Lanka
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UCB PharmaCompletedUnverricht-Lundborg DiseaseUnited States, Canada, Finland, France, Israel, Russian Federation, Serbia, Tunisia
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Chris GossUniversity of Washington; University of Arkansas; Harvard University; Cystic Fibrosis...Completed
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BioMarin PharmaceuticalCompletedMorquio A Syndrome | MPS IVA | Mucopolysaccharidosis IV AUnited States, Canada, France, Taiwan, Argentina, Colombia, Spain, Turkey, Japan, Saudi Arabia, Netherlands, Denmark, Korea, Republic of, Brazil, United Kingdom, Germany, Norway, Portugal, Italy, Qatar
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Novartis PharmaceuticalsCompleted
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Ultragenyx Pharmaceutical IncNot yet recruitingAngelman SyndromeUnited States, Australia, Canada, Germany, United Kingdom, Israel, France, Spain
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Galderma R&DActive, not recruitingModerate-to-Severe Atopic DermatitisUnited States, Australia, Austria, Belgium, Bulgaria, Canada, Czechia, Estonia, France, Georgia, Germany, Hungary, Italy, Korea, Republic of, Latvia, Lithuania, Netherlands, New Zealand, Poland, Singapore, Spain, United Kingdom
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National Cancer Institute (NCI)TerminatedNeurofibromatosis Type 1 | Plexiform Neurofibroma | Spinal Cord NeurofibromaUnited States
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia BUnited States, Netherlands, Austria, Spain, Germany, Macedonia, The Former Yugoslav Republic of, Taiwan, United Kingdom, Italy, Malaysia, Thailand, France, Greece, Russian Federation, Turkey, Japan, South Africa, Romania
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Neurocrine BiosciencesHuntington Study GroupCompletedChorea, HuntingtonUnited States, Canada
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Andrea GropmanEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsRecruitingBrain Diseases, Metabolic, Inborn | Amino Acid Metabolism, Inborn Errors | Urea Cycle DisordersUnited States, Canada, Germany, Switzerland
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Vertex Pharmaceuticals IncorporatedCompletedCystic FibrosisUnited States, Canada
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Savient PharmaceuticalsCompleted
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SanofiRegeneron PharmaceuticalsCompletedHypercholesterolaemiaNetherlands, United States, Canada, Russian Federation, South Africa
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Regeneron PharmaceuticalsCompletedIntercritical GoutUnited States, Canada
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Johnson & Johnson Pharmaceutical Research & Development...CompletedMalabsorption Syndromes | Cystic Fibrosis | Steatorrhea | Exocrine Pancreatic InsufficiencyUnited States, Canada
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Medical College of WisconsinNational Cancer Institute (NCI); National Heart, Lung, and Blood Institute... and other collaboratorsActive, not recruitingSickle Cell DiseaseUnited States
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Ultragenyx Pharmaceutical IncActive, not recruitingOsteogenesis ImperfectaUnited States, Italy, Brazil, France, Canada, Germany, Netherlands, Poland
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SK Life Science, Inc.RecruitingSeizures | Lennox Gastaut SyndromeUnited States, Korea, Republic of, Taiwan, Colombia, Australia, Poland, Serbia, Mexico, Spain, Greece, Italy, Portugal, Germany, Argentina, Israel
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Merck Sharp & Dohme LLCCompletedPneumococcal InfectionsUnited States, Brazil, Colombia, Dominican Republic, Greece, Italy, Panama
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CENTOGENE GmbH RostockWithdrawnMuscle Weakness | Peripheral NeuropathyEgypt, Germany, India, Sri Lanka
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Astellas Pharma Global Development, Inc.Active, not recruitingStargardt's Macular DystrophyItaly, United States, Israel, United Kingdom, Germany, Spain, Hungary, France
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BioMarin PharmaceuticalRecruitingHypochondroplasiaUnited States, Spain, Canada, France, Japan, Australia, Italy, Argentina, Brazil, Germany, United Kingdom
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BioMarin PharmaceuticalCompletedPhenylketonuria | HyperphenylalaninaemiaUnited States
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Vaccinex Inc.Huntington Study GroupCompletedHuntington's DiseaseUnited States, Canada
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University of Washington, the Collaborative Health...Cystic Fibrosis FoundationCompletedCystic FibrosisSpain, United States, Australia, Italy, France, Canada, Belgium, Denmark, Netherlands
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BioMarin PharmaceuticalCompletedPhenylketonuriaUnited States, Canada
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Vertex Pharmaceuticals IncorporatedCompletedCystic FibrosisUnited States, Canada
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GlycoMimetics IncorporatedCompletedSickle Cell Disease | Vaso-occlusive Crisis | Pain CrisisUnited States, Canada
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Medical College of WisconsinNational Heart, Lung, and Blood Institute (NHLBI); Dana-Farber Cancer Institute and other collaboratorsCompletedSickle Cell DiseaseUnited States
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PfizerPfizerAvailableSickle Cell DiseaseUnited States, Brazil
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Cyclerion TherapeuticsCompletedSickle Cell DiseaseUnited States, United Kingdom, Lebanon
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Genzyme, a Sanofi CompanyCompletedPompe Disease (Late-onset) | Glycogen Storage Disease Type II (GSD-II) | Acid Maltase Deficiency Disease | Glycogenosis 2United States, France, Netherlands
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Ray HershbergerNational Heart, Lung, and Blood Institute (NHLBI); National Human Genome Research...Active, not recruiting
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Eli Lilly and CompanyCompleted
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Sage TherapeuticsCompletedHuntington DiseaseUnited States
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University College, LondonCHDI Foundation, Inc.RecruitingHuntington's DiseaseUnited States, United Kingdom, France, Canada, Germany, Italy, Spain, New Zealand, Poland
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Boehringer IngelheimTerminatedCystic FibrosisUnited States, Spain, Belgium, Germany, Canada, United Kingdom, Sweden, France
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BayerAmerican Thrombosis and Hemostasis NetworkTerminated
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BioMarin PharmaceuticalActive, not recruitingLate-Infantile Neuronal Ceroid Lipofuscinosis Type 2United States
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University of Alabama at BirminghamNational Cancer Institute (NCI); Children's Hospital of Philadelphia; Washington... and other collaboratorsCompletedNeurofibromatosis Type 1United States
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Ultragenyx Pharmaceutical IncActive, not recruitingAngelman SyndromeUnited States, United Kingdom, Canada, Australia, France, Germany, Spain, Israel
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PfizerCompletedHyperlipidemia | Hypercholesterolemia, FamilialUnited States, Canada, South Africa, Czech Republic, Italy, Finland, Netherlands, France
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Emmaus Medical, Inc.CompletedSickle Cell Anemia | Sickle ß0-ThalassemiaUnited States
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HealthCore-NERINational Heart, Lung, and Blood Institute (NHLBI)CompletedSickle Cell DiseaseUnited States
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National Institute of Allergy and Infectious Diseases...National Center for Advancing Translational Sciences (NCATS); Primary Immune...Enrolling by invitationADA-SCID | Omenn Syndrome | SCID | Reticular Dysgenesis | XSCID | Leaky SCIDUnited States, Canada
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Mereo BioPharmaSyneos HealthCompletedEmphysema | Alpha 1-Antitrypsin Deficiency | COPDUnited Kingdom, Belgium, United States, Denmark, Canada, Sweden, Poland, Spain
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Hoffmann-La RocheCompletedHuntington DiseaseUnited States, Canada, Netherlands, Germany, Spain, United Kingdom, Austria, Italy
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Calithera Biosciences, IncCompletedCystic FibrosisUnited States, Canada