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Clinical Trials on Genetic Study in Colombia
Total 920 results
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ItalfarmacoCromsourceEnrolling by invitationDuchenne Muscular DystrophySpain, United States, Canada, Belgium, France, Israel, Italy, Netherlands, Serbia, Germany, United Kingdom
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National Institute of Allergy and Infectious Diseases...Rare Diseases Clinical Research Network; Primary Immune Deficiency Treatment...Enrolling by invitationGranulomatous Disease, ChronicUnited States, Canada
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Dermavant Sciences GmbHCompletedAtopic DermatitisUnited States, Canada
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LEO PharmaCompletedAtopic DermatitisUnited States, Germany, Belgium, Canada, Spain, United Kingdom, Poland, Netherlands
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Incyte CorporationCompletedAtopic DermatitisUnited States, Canada
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Nektar TherapeuticsRecruitingModerate to Severe Atopic DermatitisUnited States, Australia, Canada
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ItalfarmacoSyneos HealthCompletedDuchenne Muscular DystrophyUnited States, Italy, Spain, Canada, Belgium, France, Germany, Israel, Netherlands, Serbia, United Kingdom
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PfizerTerminatedDuchenne Muscular DystrophyUnited States, Australia, Canada, United Kingdom, Japan, Bulgaria, Italy, Poland
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University of UtahUniversity of British Columbia; Children's Hospital Medical Center, Cincinnati and other collaboratorsTerminatedNeurofibromatosis Type 1 (NF1)United States, Canada
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BayerCompletedHemophilia AUnited States, Japan, United Kingdom, Spain
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Eli Lilly and CompanyDermira, Inc.CompletedAtopic DermatitisUnited States
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AnaptysBio, Inc.RecruitingAtopic Dermatitis EczemaGeorgia, United States, Australia, Canada, Czechia, New Zealand, Poland
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Boston Children's HospitalUniversity of California, San Diego; Food and Drug Administration (FDA); Angelman... and other collaboratorsRecruiting
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Ionis Pharmaceuticals, Inc.CompletedHuntington's DiseaseCanada, United Kingdom, Germany
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Genzyme, a Sanofi CompanyCompletedGlycogen Storage Disease Type IIUnited States, France, Netherlands
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Baxalta now part of ShireCompleted
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Mendel TuchmanChildren's Hospital of Philadelphia; University of California, Los Angeles; Icahn... and other collaboratorsCompletedMethylmalonic Acidemia | Carbamoyl-Phosphate Synthase I Deficiency Disease | Propionic Acidemia, Type I and/or Type II | Ornithine Carbamoyltransferase DeficiencyUnited States
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National Heart, Lung, and Blood Institute (NHLBI)RecruitingCardiovascular Disease | Williams Syndrome | Supravalvular Aortic StenosisUnited States
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Sarepta Therapeutics, Inc.Active, not recruitingMuscular Dystrophy, DuchenneUnited States, Korea, Republic of, India, Slovenia, Turkey, United Kingdom, Germany, Switzerland, Spain, Czechia, France, Serbia, Taiwan, Netherlands, Mexico, Colombia, Denmark, New Zealand, Norway, Greece, Hungary, Ireland, Italy, Jo... and more
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Hoffmann-La RocheCompleted
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Dermavant Sciences GmbHCompletedAtopic DermatitisUnited States, Canada
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PTC TherapeuticsParexel; Dohmen Life Science ServicesApproved for marketingDuchenne Muscular DystrophyUnited States
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Bioverativ, a Sanofi companySwedish Orphan BiovitrumCompletedHemophilia BUnited States, Italy, Ireland, New Zealand, United Kingdom, Australia, Netherlands, Denmark, Poland, Sweden, France
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Seaside Therapeutics, Inc.CompletedFragile X SyndromeUnited States
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Seaside Therapeutics, Inc.TerminatedFragile X SyndromeUnited States
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CENTOGENE GmbH RostockWithdrawnFructose Metabolism, Inborn Errors | Glycogen Storage Disease Type II | Glycogen Storage Disease | Glycogen Storage Disease Type V | Glycogen Storage Disease Type I | Glycogen Storage Disease Type III | Glycogen Storage Disease Type VII | Glycogen Storage Disease Type IV | Glycogen Storage Disease Type... and other conditionsGermany, India, Sri Lanka
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BioMarin PharmaceuticalCompletedPhenylketonuriaUnited States
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Monica BhatiaActive, not recruitingSickle Cell Disease | Graft Versus Host DiseaseUnited States
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CENTOGENE GmbH RostockWithdrawnMetabolism, Inborn Errors | Mucopolysaccharidosis Type I | GargoylismGermany, India, Sri Lanka, Egypt
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Novartis PharmaceuticalsCompletedSickle Cell Disease (SCD)United States
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PharmaxisCompleted
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SanofiRecruitingDermatitis AtopicJapan, China, Spain, United States, Argentina, United Kingdom, Denmark, Sweden, Turkey
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National Institute of Allergy and Infectious Diseases...CompletedCongenital Heart Defects | Situs Inversus | Kartagener Syndrome | Ciliary Dyskinesia, PrimaryUnited States
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Arcutis Biotherapeutics, Inc.CompletedAtopic Dermatitis EczemaUnited States, Canada
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PfizerCompletedAtopic DermatitisUnited States, Canada, Australia, Germany, Hungary
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Regeneron PharmaceuticalsSanofiActive, not recruitingDermatitis, AtopicUnited States, Canada
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Regeneron PharmaceuticalsSanofiCompletedDermatitis, AtopicUnited States, France, Poland, United Kingdom, Germany, Hong Kong, Canada, Korea, Republic of, Italy, Lithuania, Sweden
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National Cancer Institute (NCI)Active, not recruitingNeurofibromatosis 1 | Neurofibroma, Plexiform | Neurofibromatosis Type 1 | NF1United States
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BioMarin PharmaceuticalCompletedSickle Cell DiseaseUnited States
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Montreal Heart InstituteCanadian Institutes of Health Research (CIHR)Enrolling by invitationCardiomyopathies | Hypertrophic Cardiomyopathy | Hypertrophic Obstructive Cardiomyopathy | Familial Hypertrophic CardiomyopathyCanada
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Children's Hospital Medical Center, CincinnatiRecruitingSickle Cell Anemia | Children, OnlyUnited States
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Genzyme, a Sanofi CompanyCompleted
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PfizerCompletedAtopic DermatitisGermany, United States, Canada, Denmark, Hungary, Australia, Latvia, Poland, Bulgaria, Japan
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Hoffmann-La RocheCompletedAtopic DermatitisUnited States, Korea, Republic of, Canada, United Kingdom, Germany, Australia, Poland, Finland, France, Spain, Switzerland, Czechia, Netherlands, Taiwan
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LEO PharmaRecruitingAtopic DermatitisUnited States, Canada, France, Germany, Japan, Poland, United Kingdom, Czechia, Spain, Romania, Hungary
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Swedish Orphan BiovitrumBioverativ Therapeutics Inc.CompletedHemophilia AIreland, United Kingdom, Germany, United States, Canada, Slovenia, Sweden
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CSL BehringActive, not recruitingHemophilia BUnited States, Belgium, Netherlands, Denmark, Germany, Ireland, Sweden, United Kingdom
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Annexon, Inc.CompletedHuntington DiseaseUnited States
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ShireCompletedHunter SyndromeUnited States, United Kingdom, Canada
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Sarepta Therapeutics, Inc.Completed