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- US Clinical Trials Registry
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Clinical Trials on Genetic Disorders
Total 152761 results
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Sahlgrenska University Hospital, SwedenNot yet recruitingFibrosis, Liver | Steatosis | Elastography | Diagnosis | Child Obesity | Metabolic Disease | Shear Wave Elastography | Shear Wave Dispersion | Attenuation Imaging | Metabolic and Genetic Disorder Affecting the Liver | Inflammation; Liver
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University of Central FloridaNational Institute on Deafness and Other Communication Disorders (NIDCD); University...CompletedDown Syndrome | Speech Sound Disorder | Speech Disorders in Children | Speech Intelligibility | Speech and Language DisorderUnited States
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CSL BehringRecruiting
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CSL BehringRecruiting
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Institute of Hematology & Blood Diseases HospitalEast China University of Science and TechnologyActive, not recruiting
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Skane University HospitalIndiana Hemophilia &Thrombosis Center, Inc.; Bioverativ Therapeutics Inc.; Swedish...Active, not recruitingFactor IX DeficiencyUnited States
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Baxalta now part of ShireCompletedHemophilia BColombia, Bulgaria, Chile, Poland, Romania, Argentina, Brazil, Czechia, Russian Federation, Ukraine
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Spark TherapeuticsChildren's Hospital of Philadelphia; Royal Prince Alfred Hospital, Sydney,... and other collaboratorsCompleted
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Bio Products LaboratoryCompletedHaemophilia BUnited Kingdom, Poland
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Bio Products LaboratoryCompletedHaemophilia BPoland, Romania, Russian Federation
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PfizerCompleted
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Hacettepe UniversitySuleyman Demirel UniversityCompletedDuchenne Muscular Dystrophy | Ambulation Difficulty | Posture Disorders in Children | Ambulation Disorder, NeurologicTurkey
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Firalis SARecruiting
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Swedish Orphan BiovitrumCompletedHaemophilia A | Haemophilia BGermany
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Bioverativ, a Sanofi companySwedish Orphan BiovitrumCompletedHemophilia BUnited States, Italy, Ireland, New Zealand, United Kingdom, Australia, Netherlands, Denmark, Poland, Sweden, France
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Baxalta now part of ShireCompletedRecombinant Factor VIIa BI (rFVIIa BI) Treatment of Acute Bleeding Episodes Per an On-demand RegimenHemophilia A | Hemophilia BJapan, Russian Federation, Spain, United States, Poland, Romania, Serbia, Taiwan, Ukraine
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BayerCompletedHemophilia A; Hemophilia BIsrael
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Novo Nordisk A/SCompletedHaemophilia A | Haemophilia BUnited States
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Centre Hospitalier Universitaire de Saint EtiennePfizer; Ecole Normale Supérieure des Mines de Saint-EtienneCompletedHaemophilia A | Haemophilia BFrance
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National Institute of Allergy and Infectious Diseases...CompletedGenetic Diseases, X-Linked | Lymphoproliferative Disease | X-Linked Lymphoproliferative DiseaseUnited States
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National Cancer Institute (NCI)CompletedDyskeratosis Congenita | Telomere Biology DisordersUnited States
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Clinical Hospital Center RijekaKarolinska Institutet; University Medical Centre Ljubljana; Croatian Science...Enrolling by invitationParkinson Disease | Genetic Disease | Microbiota | Neuro-Degenerative Disease | Neuroinflammatory ResponseCroatia
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Eloxx Pharmaceuticals, Inc.SGS Life Sciences, a division of SGS Belgium NVCompleted
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General Genetics CorporationSyntactxUnknownGenetics of Drug MetabolismUnited States, Puerto Rico
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Regina Elena Cancer InstituteRecruiting
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Lithuanian University of Health SciencesRecruitingInflammation | Cognitive Dysfunction | Genetic Predisposition to Disease | Endotoxemia | Major Depressive Disorder | Blood Brain Barrier DefectLithuania
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Baylor College of MedicineUniversity of California, San Diego; University of Alabama at Birmingham; Boston... and other collaboratorsCompletedPrader-Willi Syndrome | Rett Syndrome | Angelman Syndrome | Sleep ProblemsUnited States
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Liggins InstituteRecruiting
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Children's Mercy Hospital Kansas CityCompletedGenetic Disease | Diseases/DiagnosesUnited States
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Yale UniversityCompletedSkin Diseases | Immune System Diseases | Hypersensitivity | Hypersensitivity, Immediate | Skin Diseases, Genetic | Dermatitis | Eczema | Skin Diseases, Eczematous | Dermatitis, Atopic | Genetic Disease, InbornUnited States
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University of AlbertaSt. Justine's HospitalRecruitingNeurobehavioral Manifestations | Genetic Diseases, X-Linked | Mental Retardation, X-Linked | Intellectual Disability | Fragile X Syndrome | Sex Chromosome Disorders | Fragile X Mental Retardation Syndrome | Trinucleotide Repeat Expansion | Fra(X) Syndrome | FXSCanada
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Affiliated Hospital of Guangdong Medical UniversityNot yet recruitingHemophilia B Without Inhibitor
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PfizerRecruitingHemophilia A | Hemophilia BDenmark, Taiwan, Canada, Turkey, Spain, China, United Kingdom, South Africa, Italy, Saudi Arabia, Israel, Korea, Republic of, Austria, Germany, Japan, Australia, India, Slovakia, France, United States, Brazil, Argentina
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ApcinteX LtdCentessa Pharmaceuticals plcRecruitingHemophilia A | Hemophilia BSpain, Taiwan, United Kingdom, Italy, Germany, United States, South Africa, Australia, Poland, Armenia, France, India, Canada, Brazil, Turkey, Egypt
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Goethe UniversitySociety for Thrombosis and Haemostasis Research (Germany)RecruitingHemophilia A | Hemophilia B | Children | Drug Specific AntibodiesGermany
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PfizerCompleted
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Bioverativ Therapeutics Inc.Swedish Orphan BiovitrumCompletedHemophilia BUnited States, United Kingdom, South Africa, Netherlands, Ireland, Australia
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Novo Nordisk A/SCompletedChronic Kidney Disease | Turner Syndrome | Chronic Renal Insufficiency | Growth Hormone Disorder | Growth Hormone Deficiency in Children | Genetic Disorder | Delivery Systems | Foetal Growth Problem | Small for Gestational AgeFrance
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Novo Nordisk A/SCompletedChronic Kidney Disease | Turner Syndrome | Chronic Renal Insufficiency | Growth Hormone Disorder | Growth Hormone Deficiency in Children | Genetic Disorder | Delivery Systems | Foetal Growth Problem | Small for Gestational AgeFrance
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Icahn School of Medicine at Mount SinaiNational Institute of Neurological Disorders and Stroke (NINDS)Enrolling by invitationAutism Spectrum Disorder (ASD) | Phelan-McDermid SyndromeUnited States
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Zhejiang UniversityNot yet recruitingHemophilia B Without Inhibitor
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Hasan Kalyoncu UniversityNot yet recruitingHemophilia B | Hemophilia | Hemophilia A, SevereTurkey
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ApcinteX LtdCentessa Pharmaceuticals plcRecruitingHemophilia B | Hemophilia B With InhibitorUnited States, Spain, Australia, Taiwan, France, United Kingdom, Italy, Turkey, Armenia, India, Germany
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PfizerActive, not recruitingHemophilia BGermany, United Kingdom, Canada, Australia, Taiwan, Japan, France, Turkey, Korea, Republic of, United States, Brazil, Greece, Saudi Arabia, Sweden
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PfizerActive, not recruitingHemophilia A | Hemophilia BUnited States, Spain, Canada, China, Korea, Republic of, Hong Kong, Serbia, Taiwan, Turkey, France, Oman, Saudi Arabia, Japan, India, South Africa, Mexico, Croatia, Italy, Bulgaria, Russian Federation
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Novo Nordisk A/SEnrolling by invitationHaemophilia A | Haemophilia BJapan
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Assistance Publique - Hôpitaux de ParisUnknown
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Swedish Orphan BiovitrumCompletedHaemophilia A | Haemophilia BFrance, Germany, Italy, Spain, Sweden, Belgium, United Kingdom
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University Hospital, BordeauxNot yet recruitingNervous System Diseases | Genetic Disease