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- US Clinical Trials Registry
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Clinical Trials on Genetics in South Africa
Total 1088 results
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The University of New South WalesRecruitingHealthy | Obstructive Sleep Apnea | Cystic Fibrosis | Hirschprung's DiseaseAustralia
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ModernaTX, Inc.RecruitingPhenylketonuriaUnited States, Australia
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PfizerCompletedHyperlipidemia | Hypercholesterolemia, FamilialUnited States, Canada, South Africa, Czech Republic, Italy, Finland, Netherlands, France
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PfizerTerminated
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Medical University of South CarolinaCompleted
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Regeneron PharmaceuticalsSanofiCompletedAtopic DermatitisGermany, New Zealand, Australia
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GlaxoSmithKlineRecruitingHematologic Diseases | Anaemia, Sickle CellUnited States
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Regeneron PharmaceuticalsCompletedHomozygous Familial HypercholesterolemiaUnited States, Netherlands, South Africa, Australia, Austria, Canada, Czechia, France, Greece, Italy, Japan, Ukraine
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Arcutis Biotherapeutics, Inc.CompletedAtopic Dermatitis (Eczema)United States
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Ardea Biosciences, Inc.Completed
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Regeneron PharmaceuticalsSanofiCompletedModerate-to-severe Atopic DermatitisUnited States
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PfizerCompletedDermatitis, AtopicUnited States, Hungary, Canada, Germany, Australia, Czechia, Poland, United Kingdom
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Bioverativ Therapeutics Inc.CompletedSevere Hemophilia BUnited States, Italy, Belgium, Australia, Brazil, Hong Kong, India, Ireland, Japan, South Africa, United Kingdom, Netherlands, Sweden, Canada, Poland, China, France, Germany
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International Rett Syndrome FoundationBaylor College of Medicine; Children's Hospital of Philadelphia; University of... and other collaboratorsRecruitingNervous System Diseases | Neurologic Manifestations | Neurobehavioral Manifestations | Genetic Diseases, X-Linked | Intellectual Disability | Neurodevelopmental Disorders | Neurologic Disorder | Rett Syndrome | Genetic Disease | Rett Syndrome, AtypicalUnited States
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Jnana TherapeuticsRecruitingPhenylketonuriaUnited States, Australia
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CSL LimitedCompleted
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Greenwood Genetic CenterShriners Hospitals for Children; BioMarin PharmaceuticalCompletedMPS IVA | Maroteaux Lamy Syndrome | MPS VI | Morquio Syndrome AUnited States
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National Center for Research Resources (NCRR)CompletedCongenital Adrenal HyperplasiaUnited States
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PfizerRecruitingHemophilia A | Hemophilia BDenmark, Taiwan, Canada, Turkey, Spain, China, United Kingdom, South Africa, Italy, Saudi Arabia, Israel, Korea, Republic of, Austria, Germany, Japan, Australia, India, Slovakia, France, United States, Brazil, Argentina
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Freeline TherapeuticsCompletedHemophilia B | Blood Coagulation Disorders, Inherited | Blood Coagulation Disorder | Haematologic DiseaseUnited States, United Kingdom, Australia, Netherlands, Austria, France, Ireland, Italy, Turkey, Canada, Germany, South Africa
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Genzyme, a Sanofi CompanyCompletedHemophilia A | Hemophilia BUnited States, Australia, China, Denmark, France, Israel, Japan, Korea, Republic of, Malaysia, Turkey, Ukraine, United Kingdom, Germany, India, South Africa, Spain, Taiwan, Hungary, Italy
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La Jolla Pharmaceutical CompanyTerminatedBeta-ThalassemiaAustralia, Thailand, United States, Greece, Italy, Lebanon, Turkey, United Kingdom
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Anavex Life Sciences Corp.Anavex Australia Pty Ltd.; Anavex Germany GmbHCompletedRett SyndromeCanada, Australia, United Kingdom
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PfizerCompletedAtopic DermatitisUnited States, Australia, Canada
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Scioderm, Inc.Amicus TherapeuticsTerminatedEpidermolysis BullosaPoland, Spain, Serbia, Netherlands, United States, Austria, Australia, Israel, Germany, France, United Kingdom, Lithuania
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ASLAN PharmaceuticalsCompletedAtopic DermatitisUnited States, Australia, Singapore, India, Canada, New Zealand, Dominican Republic, Poland
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Vanda PharmaceuticalsTerminatedAtopic DermatitisUnited States
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AmgenCompletedFamilial HypercholesterolemiaCanada, Italy, Norway, Belgium, United States, Turkey, Australia, Austria, South Africa, Poland, Switzerland, Spain, Portugal, Slovenia, Brazil, Russian Federation, Hungary, United Kingdom, Colombia, Czechia, Netherlands, Greece, Ma...
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Western Sydney Local Health DistrictWestmead Institute for Medical ResearchCompletedHypertension | Endothelial Dysfunction | Autosomal Dominant Polycystic KidneyAustralia
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Baylor College of MedicineUniversity of California, San Diego; University of Alabama at Birmingham; Boston... and other collaboratorsCompletedPrader-Willi Syndrome | Rett Syndrome | Angelman Syndrome | Sleep ProblemsUnited States
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Murdoch Childrens Research InstituteRoyal Children's HospitalCompletedPrimary Immunodeficiency | Invasive Pneumococcal Disease, Protection Against | Invasive Pneumococcal Disease, Recurrent Isolated, 1 | Invasive Pneumococcal Disease, Recurrent Isolated, 2Australia, New Zealand
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Kirby InstituteGilead Sciences; Melanoma Institute Australia; St Vincent's Hospital, Sydney; Royal... and other collaboratorsActive, not recruitingCOVID-19 | Cancer | Primary Immune Deficiency Disorder | HIV-1-infection | Immunosuppression DisordersAustralia
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Evelo Biosciences, Inc.CompletedPsoriasis | Asthma | Atopic DermatitisUnited Kingdom
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Arrowhead PharmaceuticalsCompletedHypertriglyceridemia | Familial ChylomicronemiaAustralia, Canada, New Zealand
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Otsuka Pharmaceutical Development & Commercialization...CompletedAtopic DermatitisPoland, United States, Australia
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Zynerba Pharmaceuticals, Inc.CompletedFragile X SyndromeUnited States, New Zealand, Australia
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Disc Medicine, IncEnrolling by invitationErythropoietic ProtoporphyriaUnited States, Australia
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Aerie PharmaceuticalsCompleted
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Jazz PharmaceuticalsGW PharmaceuticalsTerminatedRett Syndrome | RTTUnited States, Canada, Italy, Spain, United Kingdom, Australia
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Novartis PharmaceuticalsCompletedThalassemia, Non-transfusional-dependent Thalassemia (NTDT), Myeloplastic Dysplasia (MDS), Other AnemiaAustralia
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University of MiamiNational Institute of Neurological Disorders and Stroke (NINDS); St. Jude Children... and other collaboratorsEnrolling by invitationAmyotrophic Lateral Sclerosis | Primary Lateral Sclerosis | Frontotemporal Dementia | Progressive Muscular Atrophy | Hereditary Spastic Paraplegia | Multisystem ProteinopathyUnited States, South Africa, Germany
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Scioderm, Inc.Amicus TherapeuticsCompletedEpidermolysis BullosaItaly, Spain, Serbia, United States, Australia, Netherlands, Austria, Germany, Israel, Lithuania, France, United Kingdom, Poland
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University of California, San DiegoBaylor College of Medicine; Boston Children's Hospital; Rare Diseases Clinical... and other collaboratorsCompletedNervous System Diseases | Angelman SyndromeUnited States
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Ardea Biosciences, Inc.Completed
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Glycomine, Inc.Recruiting24-Week Study to Assess the PD, Safety, Tolerability, and PK of GLM101 in Participants With PMM2-CDGPmm2-CDGSpain, Australia, United States
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Aclaris Therapeutics, Inc.CompletedAtopic DermatitisUnited States
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia BUnited States, Netherlands, Austria, Spain, Germany, Macedonia, The Former Yugoslav Republic of, Taiwan, United Kingdom, Italy, Malaysia, Thailand, France, Greece, Turkey, Japan, South Africa, Romania
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The University of QueenslandRecruitingAutosomal Dominant Polycystic Kidney DiseaseAustralia
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Vertex Pharmaceuticals IncorporatedTerminatedCystic FibrosisUnited Kingdom, Canada, Australia
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PfizerCompletedAtopic DermatitisUnited States, Canada, Australia, Germany, Hungary