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Clinical Trials on Glycogen Storage Disease Type 4
Total 58527 results
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ISU Abxis Co., Ltd.Completed
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Amicus TherapeuticsTerminatedType 1 Gaucher DiseaseUnited States, United Kingdom
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Translational Research Center for Medical Innovation...TerminatedPrimary Triglyceride Deposit Cardiomyovasculopathy (TGCV) | Neutral Lipid Storage Disease With Myopathy (NLSD-M)Italy, Japan
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AlexionRecruitingWolman Disease | Cholesterol Ester Storage Disease | Lysosomal Acid Lipase Deficiency | Acid Cholesteryl Ester Hydrolase Deficiency, Type 2 | Acid Lipase Deficiency | LIPA Deficiency | LAL-DeficiencyFrance, Belgium, United States, Spain, Germany, Greece, Israel, Italy, Slovenia, United Kingdom, Brazil, Canada, Denmark, Australia, Croatia, Czechia, Ireland, Mexico, Netherlands, Poland, Portugal, Saudi Arabia
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He HuangLingyi Biotech Co., Ltd.Recruiting
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SanofiCompleted
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Shaare Zedek Medical CenterCompleted
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Lei LiRecruitingEpithelial Ovarian Cancer | Circulating Tumor DNA | CA125 | DNA Methylation | Non-invasive Diagnosis | Human Epididymis Protein 4 | Imaging Evaluation | Survival PrognosisChina
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Lei LiRecruitingEpithelial Ovarian Cancer | Circulating Tumor DNA | CA125 | DNA Methylation | Non-invasive Diagnosis | Human Epididymis Protein 4 | Imaging Evaluation | Survival Prognosis | ROMA IndexChina
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University Hospital, RouenUniversity Hospital, CaenRecruitingLysosomal Storage Diseases | Neonatal ScreeningFrance
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Lysosomal and Rare Disorders Research and Treatment...UnknownGaucher Disease Type 1United States
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Yonsei UniversityUnknownSymptomatic Peripheral Artery Disease With Femoropopliteal Lesions | Moderate or Severe Claudication (Rutherford Category 2 or 3) | Critical Limb Ischemia (Rutherford Category 4 or 5)Korea, Republic of
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Institute for Clinical Effectiveness, JapanCompletedCoronary Disease | Diabetes Mellitus | Dipeptidyl-Peptidase 4 Inhibitors | LDL Cholesterol | Glycosylated HemoglobinJapan
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Mustafa Kemal UniversityMersin UniversityNot yet recruitingShoulder Pain | Laparoscopic Cholecystectomy | Pulmonary Function Test | Breathing Exercise | Surgical Nursing | 4-7-8 Breathing Technique
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Massachusetts General HospitalRecruiting
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Assistance Publique Hopitaux De MarseilleNot yet recruitingChronic Kidney Disease (Stages 4 and 5)France
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Mayo ClinicCelgene CorporationCompletedIgG4-related Disease | Retroperitoneal Fibrosis | Autoimmune Pancreatitis | IgG4-related Sclerosing Cholangitis | Immunoglobulin G Subclass 4 Related DiseaseUnited States
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Maastricht University Medical CenterCompletedNeutral Lipid Storage DiseaseNetherlands
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Alexion PharmaceuticalsCompletedLysosomal Acid Lipase Deficiency | Cholesterol Ester Storage Disease(CESD) | LAL-DeficiencyFrance, United States, United Kingdom, Czechia
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National Institute of Neurological Disorders and...CompletedLysosomal Storage DiseaseUnited States, France, Israel, Netherlands
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Passage Bio, Inc.Active, not recruitingGM1 Gangliosidosis | GM1 Gangliosidosis, Type I | GM1 Gangliosidosis, Type 2 | Beta-Galactosidase-1 (GLB1) DeficiencyUnited States, Canada, United Kingdom, Turkey, Brazil
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Northern Care Alliance NHS Foundation TrustBrighter ABCompletedDiabetes type1 | Diabetes type2United Kingdom
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Lawson Health Research InstituteSequana Medical N.V.RecruitingHemodialysis | Peritoneal Dialysis | End Stage Renal Disease on Dialysis | Nonosmotic Sodium StorageCanada
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Idorsia Pharmaceuticals Ltd.CompletedGM2 Gangliosidosis | GM1 Gangliosidosis | Tay-Sachs Disease | Sandhoff Disease | Gaucher Disease, Type 2 | AB Variant Gangliosidosis GM2United States, Spain, Germany, Italy, Belgium, Brazil, France, Portugal, Switzerland, United Kingdom
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Alexion PharmaceuticalsCompletedLysosomal Acid Lipase Deficiency | LAL-Deficiency | Cholesterol Ester Storage Disease (CESD)France, United Kingdom, United States, Canada, Czechia
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Eisai Inc.TerminatedUnresectable Stage III Melanoma | Wild Type BRAF Stage IV MelanomaUnited States
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University of MinnesotaNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... and other collaboratorsRecruitingGaucher Disease Type 1United States
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Chung-Hsing WangSanofiNot yet recruiting
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LYSOGENECompletedMucopolysaccharidosis Type III A | Sanfilippo Disease Type AFrance
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LYSOGENECompletedMucopolysaccharidosis Type III A | Sanfilippo Disease Type AFrance
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Eline C. B. EskesRecruiting
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Corporal Michael J. Crescenz VA Medical CenterCompletedIdiopathic Pulmonary Fibrosis | COPD | Congestive Heart Failure | Malignancy | Severe or Very Severe Airflow Obstruction and/or Receiving or Eligible to Receive Long-term Oxygen Therapy | Other Interstitial Lung Disease Without Curative Therapy | NYHA Class IV or NYHA Class III Plus 1 Hospitalization... and other conditionsUnited States
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University Hospital Center of MartiniqueClinique Antilles-Guyane; Fondation de FranceCompleted1- Women | 2- HIV Infection | 3- Followed in West Indies and French Guiana for His Infection | 4- Acceptance of the Use of Nadis® Medical FilesMartinique
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Lyell Immunopharma, Inc.RecruitingAdvanced Breast Cancer | NSCLC | Non Small Cell Lung Cancer | Triple Negative Breast Cancer | Non-small Cell Lung Cancer | Advanced Lung Carcinoma | Non Small Cell Lung Cancer Metastatic | NSCLC Stage IV | Recurrent Breast Cancer | TNBC - Triple-Negative Breast Cancer | Relapsed Cancer | NSCLC, Recurrent | Recurrent... and other conditionsUnited States
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Charite University, Berlin, GermanyCompletedDehiscent Type of Alveolar Bone Defect | One Stage Bone Augmentation
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Novartis PharmaceuticalsWithdrawnPatients With Migraine Equal of /More Than 3 and Equal of/ Less Than 12 Migraine Attacks/4 Weeks for Each of the Last 6 Months Preceding the Screening
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University of MinnesotaRecruitingInflammation | Oxidative Stress | Gaucher Disease Type IUnited States
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SanofiRecruitingAcid Sphingomyelinase Deficiency (ASMD)France
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SanofiCompletedSphingomyelin LipidosisItaly, Czechia, Belgium, France, Portugal, Turkey, United States, Argentina, Brazil, Chile, Germany, Romania, Spain
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National Institute of Neurological Disorders and...Completed
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National Taiwan University HospitalRecruiting
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Istanbul UniversityBiruni UniversityNot yet recruitingLipid Storage DiseaseTurkey
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Theodor Bilharz Research InstituteUnknownGenotype 4 Chronic Hepatitis C InfectionEgypt
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Astellas Pharma IncCompletedNon-Small Cell Lung Cancer (NSCLC) With Nonprogression Following 4 Cycles of Platinum-based ChemotherapyUnited Kingdom, United States, Brazil, Canada, Germany, Korea, Republic of, Poland, Romania, Russian Federation
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CinnagenCompletedMucopolysaccharidosis Type 1Iran, Islamic Republic of
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Nationwide Children's HospitalSanfilippo Children's Research Foundation; The Sanfilippo Research Foundation; The Children's Medical Research FoundationCompletedMucopolysaccharidosis Type IIIA | Mucopolysaccharidosis Type IIIBUnited States
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QIAGEN Gaithersburg, IncCompletedRespiratory Syncytial Virus Infections | Influenza A | Rhinovirus | Influenza B | QIAGEN ResPlex II Advanced Panel | Infection Due to Human Parainfluenza Virus 1 | Parainfluenza Type 2 | Parainfluenza Type 3 | Parainfluenza Type 4 | Human Metapneumovirus A/B | Coxsackie Virus/Echovirus | Adenovirus Types B/C/E | Coronavirus Subtypes 229E and other conditionsUnited States
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Jonsson Comprehensive Cancer CenterNational Cancer Institute (NCI); Genzyme, a Sanofi CompanyWithdrawnStage IIB Melanoma | Stage IIC Melanoma | Stage IB Melanoma | Stage IIA MelanomaUnited States
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Genzyme, a Sanofi CompanyCompletedSphingomyelin LipidosisUnited States, Argentina, Australia, Belgium, Brazil, Bulgaria, Chile, France, Germany, Italy, Japan, Netherlands, Portugal, Spain, Tunisia, Turkey, United Kingdom
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Genzyme, a Sanofi CompanyCompletedSphingomyelin LipidosisUnited States, Belgium, Brazil, France, Germany, Italy, United Kingdom