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- US Clinical Trials Registry
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Clinical Trials on Glycogen Storage Disorders
Total 150853 results
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IRCCS Eugenio MedeaUniversity of Pisa; University of MessinaCompleted
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Rigshospitalet, DenmarkCompleted
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Rigshospitalet, DenmarkCompleted
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Ultragenyx Pharmaceutical IncTerminatedGlycogen Storage Disease Type IIIUnited States, Spain, Italy
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Genzyme, a Sanofi CompanyTerminatedGlycogenosis 2 | Glycogen Storage Disease Type II (GSD II) | Acid Maltase Deficiency | Pompe Disease (Infantile-Onset)United States, Taiwan, Germany
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Genzyme, a Sanofi CompanyCompletedGlycogenesis 2 Acid Maltase Deficiency | Pompe Disease (Late-Onset) | Glycogen Storage Disease Type II (GSD II)United States, Netherlands, United Kingdom, Germany
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Genzyme, a Sanofi CompanyCompletedGlycogenesis 2 Acid Maltase Deficiency | Pompe Disease (Late-Onset) | Glycogen Storage Disease Type II (GSD II)France
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Genzyme, a Sanofi CompanyCompletedGlycogen Storage Disease Type II (GSD-II) | Pompe Disease (Late-Onset) | Glycogenesis Type II | Acid Maltase Deficiency (AMD)United States, France, Canada, Netherlands, Australia
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Children's Healthcare of AtlantaTerminatedCongenital Disorders
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Rigshospitalet, DenmarkCompletedGlycogen Storage Disease Type IIIDenmark
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Genzyme, a Sanofi CompanyRecruitingPompe Disease (Late-onset) | Glycogen Storage Disease Type II (GSD-II) | Glycogenesis 2 Acid Maltase DeficiencyCroatia, United States, Italy, Belgium, Czechia
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Genzyme, a Sanofi CompanyCompletedPompe Disease (Late-onset) | Glycogen Storage Disease Type II (GSD-II) | Acid Maltase Deficiency Disease | Glycogenosis 2United States, France, Netherlands
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National Institute of Arthritis and Musculoskeletal...CompletedMyositis | Dermatomyositis | Polymyositis | Glycogen Storage Disease Type II | Glycogen Storage Disease Type VIIUnited States
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Genzyme, a Sanofi CompanyCompletedPompe Disease (Late-onset) | Glycogen Storage Disease Type II (GSD-II) | Acid Maltase Deficiency Disease | Glycogenosis 2Netherlands
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Genzyme, a Sanofi CompanyCompletedPompe Disease (Late-onset) | Glycogen Storage Disease Type II (GSD-II) | Acid Maltase Deficiency Disease | Glycogenosis 2France
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University College, LondonCompleted
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Cliniques universitaires Saint-Luc- Université...UnknownGlucose 6 Phosphatase Deficiency | Glycogen Storage Disease Type IBelgium
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SanofiRecruitingGlycogen Storage Disease Type IIBelgium, United States, Italy, Spain, Taiwan, United Kingdom, Netherlands, France, Germany
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Genzyme, a Sanofi CompanyActive, not recruitingGlycogen Storage Disease Type IIFrance
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Genzyme, a Sanofi CompanyCompletedGlycogen Storage Disease Type IIChina
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Duke UniversityNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS)CompletedGlycogen Storage Disease Type IIUnited States
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Columbia UniversityWithdrawnGlycogen Storage Disease Type IIUnited States
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University of FloridaAmicus TherapeuticsCompletedLysosomal Storage Diseases | Glycogen Storage Disease Type II | Pompe DiseaseUnited States
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Children's Memorial Health Institute, PolandDepartment of Internal Medicine, Hypertension and Vascular Diseases, The...Not yet recruitingGlucose 6 Phosphatase DeficiencyPoland
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Taipei Veterans General Hospital, TaiwanNot yet recruitingGlycogen Storage Disease Type II
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Hong Kong Children's HospitalRecruitingGlycogen Storage Disease Type IBHong Kong
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Duke UniversityRecruitingAdult Polyglucosan Body Disease | Glycogen Storage Disease Type IV | GSD4 | GSD IV | APBDUnited States
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SanofiRecruitingGlycogen Storage Disease Type IIBelgium, United States, China, Germany, Italy, Netherlands, Spain, Taiwan, United Kingdom
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Taipei Veterans General Hospital, TaiwanUnknownGlycogen Storage Disease Type IITaiwan
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Amicus TherapeuticsRecruitingPompe DiseaseUnited States, Germany
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Duke UniversitySanofiRecruiting
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Duke UniversityGenzyme, a Sanofi CompanyRecruitingPompe DiseaseUnited States
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Genzyme, a Sanofi CompanyCompleted
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Valerion Therapeutics, LLCTerminatedPompe DiseaseUnited States, United Kingdom
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University of FloridaNational Heart, Lung, and Blood Institute (NHLBI)CompletedPompe DiseaseUnited States
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BioMarin PharmaceuticalCompletedPompe DiseaseUnited States, United Kingdom, France, Australia, Germany
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BioMarin PharmaceuticalTerminatedPompe DiseaseUnited States, United Kingdom, Australia, France, Germany, New Zealand
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University of FloridaCompletedPompe DiseaseUnited States
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Centre Hospitalier de CayenneCompleted
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National Taiwan University HospitalUnknown
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Genzyme, a Sanofi CompanyTerminatedPompe DiseaseUnited States
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Genzyme, a Sanofi CompanyCompletedGlycogen Storage Disease Type II | Pompe DiseaseUnited States
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Genzyme, a Sanofi CompanyCompletedGlycogen Storage Disease Type IIUnited States, Taiwan, Israel, United Kingdom, France
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University Children's Hospital, ZurichSanofiCompleted
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Genzyme, a Sanofi CompanyCompletedGlycogen Storage Disease Type II | Acid Maltase Deficiency Disease | Glycogenosis 2 | Pompe DiseaseUnited States, Israel, France, United Kingdom
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Serhat Gumrukcu, MD PhDFrida Therapeutics LLCRecruiting
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Genzyme, a Sanofi CompanyActive, not recruiting
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Amicus TherapeuticsAvailable
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Duke UniversityCompleted