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Clinical Trials on Hemoglobin S Beta-0 Thalassemia
Total 289 results
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Thomas Jefferson UniversityGlaxoSmithKline; Drexel UniversityUnknownQuality of Life | Inflammation | Sickle Cell Disease | HEMOGLOBIN SS | Hemoglobin S Beta-0 ThalassemiaUnited States
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National Heart, Lung, and Blood Institute (NHLBI)Not yet recruitingSickle Cell Disease | Sickle Cell Disorders | Hb-SS Disease | Hemoglobin S | Disease Sickle Cell Anemia | Hemoglobin Beta Thalassemia DiseaseUnited States
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Emory UniversityPatient-Centered Outcomes Research InstituteCompletedSickle Cell Disease | Sickle Cell Anemia | Hemoglobin SC | Hemoglobin SS | Hemoglobin Beta ThalassemiaUnited States
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Nova Laboratories LimitedCompletedSickle Cell Disease | Sickle Cell Hemoglobin C | Sickle Cell-beta-thalassemia | Sickle-Cell; Hemoglobin Disease, ThalassemiaUnited Kingdom, Jamaica
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M.D. Anderson Cancer CenterWithdrawnSickle Cell Disease | Sickle Beta Thalassemia | Beta Thalassemia Major | Sickle Cell-SS Disease | Sickle Beta 0 Thalassemia | Sickle Beta Plus ThalassemiaUnited States
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Imara, Inc.Quintiles, Inc.CompletedSickle Cell Disease | Sickle Beta 0 Thalassemia | Sickle-Cell; Hb-SCUnited States
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IRCCS San RaffaeleTelethon Institute for Gene Therapy (OSR-TIGET)Active, not recruiting
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EdiGene (GuangZhou) Inc.Active, not recruitingTransfusion Dependent Beta-ThalassaemiaChina
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Institute of Hematology & Blood Diseases Hospital...EdiGene Inc.; The Affiliated Hospital Of Guizhou Medical University; Zunyi Medical...Active, not recruitingTransfusion Dependent Beta-ThalassaemiaChina
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EdiGene (GuangZhou) Inc.PLA 923 HospitalActive, not recruitingTransfusion Dependent Beta-ThalassaemiaChina
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Ann & Robert H Lurie Children's Hospital of ChicagoNational Heart, Lung, and Blood Institute (NHLBI)RecruitingSickle Cell Disease | Sickle B+ Thalassemia | Sickle Beta Zero Thalassemia | Sickle Cell Hemoglobin CUnited States
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Ann & Robert H Lurie Children's Hospital of ChicagoCompletedSickle Cell Disease | Sickle B+ Thalassemia | Sickle Beta Zero Thalassemia | Sickle Cell Hemoglobin CUnited States
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Tanta UniversityUnknownStudy of The Therapeutic Benefits of Al-hijamah in Children With Beta Thalassemia Major (Al-hijamah)AL-Hijama in Thalassmia MajorEgypt
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Ann & Robert H Lurie Children's Hospital of ChicagoNational Heart, Lung, and Blood Institute (NHLBI)Active, not recruitingSickle Cell Disease | Sickle B+ Thalassemia | Sickle Beta Zero Thalassemia | Sickle Cell Hemoglobin CUnited States
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Ann & Robert H Lurie Children's Hospital of ChicagoCompletedSickle Cell Disease | Sickle B+ Thalassemia | Sickle Beta Zero Thalassemia | Sickle Cell Hemoglobin CUnited States
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National Institute of Allergy and Infectious Diseases...TerminatedAnemia, Sickle Cell | Hemoglobinopathies | Thalassemia | Hemoglobin SC Disease | Thalassemia MajorUnited States
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CelgeneTerminatedBeta Thalassemia Intermedia | Beta Thalassemia MajorFrance, United Kingdom, Italy, Greece
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Centre Hospitalier Universitaire de Saint EtienneClaude Bernard University; Laboratoire de Physiologie de l'Exercice; Centre de...CompletedHemoglobin S Disease | Sickle Cell Hemoglobin C DiseaseFrance
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University of British ColumbiaCompletedSickle Cell Disease | Beta-Thalassemia | Sickle Cell Trait | Sickle Cell-Beta Thalassemia | Sickle Cell-SS DiseaseCanada, Nepal
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Editas Medicine, Inc.RecruitingHemoglobinopathies | Thalassemia Major | Thalassemia Intermedia | Transfusion Dependent Beta ThalassemiaUnited States, Canada
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Ionis Pharmaceuticals, Inc.TerminatedBeta Thalassemia IntermediaAustralia, Thailand, Greece, Lebanon, Turkey
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Agios Pharmaceuticals, Inc.Active, not recruitingTransfusion-dependent Alpha-Thalassemia | Transfusion-dependent Beta-ThalassemiaSpain, Taiwan, Thailand, United States, France, Canada, Malaysia, Germany, Netherlands, Bulgaria, United Kingdom, Turkey, Italy, Greece, United Arab Emirates, Brazil, Denmark, Lebanon, Saudi Arabia
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Children's Hospital of PhiladelphiaNot yet recruiting
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Bristol-Myers SquibbRecruiting
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Assiut UniversityRecruiting
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CelgeneAcceleron Pharma, Inc., a wholly-owned subsidiary of Merck & Co., Inc., Rahway...RecruitingBeta-ThalassemiaUnited States, Turkey, Italy, Thailand, Germany, Greece, China, India, Lebanon
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Vertex Pharmaceuticals IncorporatedCRISPR TherapeuticsActive, not recruitingHematologic Diseases | Genetic Diseases, Inborn | Hemoglobinopathies | Thalassemia | Beta-ThalassemiaUnited States, United Kingdom, Canada, Germany, Italy
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CorrectSequence Therapeutics Co., LtdFirst Affiliated Hospital of Guangxi Medical UniversityEnrolling by invitation
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Rare Partners srl Impresa SocialeUniversità degli Studi di FerraraCompletedBeta-ThalassemiaItaly
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Acceleron Pharma Inc. (a wholly owned subsidiary...Completed
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University Hospital of PatrasCompleted
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IRCCS San RaffaeleOrchard Therapeutics; Fondazione TelethonUnknown
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Hoffmann-La RocheCompletedBeta-ThalassemiaItaly, Lebanon, Thailand
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Prolong PharmaceuticalsCompleted
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Shenzhen Geno-Immune Medical InstituteUnknown
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University of WashingtonNational Heart, Lung, and Blood Institute (NHLBI); George Papanicolaou HospitalCompletedBeta-ThalassemiaGreece
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University of RegensburgRecruitingSickle Cell Disease | Sickle Cell Anemia | Sickle Cell Disorders | HbS Disease | Hemoglobin S Disease | Sickling Disorder Due to Hemoglobin SGermany, Austria
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Agios Pharmaceuticals, Inc.Active, not recruitingNon-Transfusion-dependent Alpha-Thalassemia | Non-Transfusion-dependent Beta-ThalassemiaSpain, Taiwan, Thailand, United Kingdom, Malaysia, United States, Netherlands, Bulgaria, Turkey, Italy, Canada, Brazil, France, United Arab Emirates, Denmark, Greece, Lebanon, Saudi Arabia
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Aga Khan UniversityCompletedBeta Thalassemia Major
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China Medical University HospitalCompleted
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Vifor (International) Inc.Labcorp Corporation of America Holdings, IncCompletedBeta-Thalassemia | Non-transfusion-dependent ThalassemiaGreece, Israel, Italy, Lebanon, Thailand
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Lantu BiopharmaNot yet recruitingBeta-Thalassemia
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bluebird bioCenter for International Blood and Marrow Transplant ResearchRecruitingBeta-ThalassemiaUnited States
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Children's Hospital of Fudan UniversityCorrectSequence Therapeutics Co., LtdRecruiting
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Assiut UniversityNot yet recruiting
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Vertex Pharmaceuticals IncorporatedCRISPR TherapeuticsRecruitingHematologic Diseases | Genetic Diseases, Inborn | Hemoglobinopathies | Thalassemia | Beta-ThalassemiaUnited States, Germany, Italy, United Kingdom, Canada
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CorrectSequence Therapeutics Co., LtdFirst Affiliated Hospital of Guangxi Medical UniversityActive, not recruiting
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bluebird bioCompletedBeta-ThalassemiaUnited States, Germany, United Kingdom, France, Greece, Italy
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bluebird bioCompletedBeta-ThalassemiaFrance, United Kingdom, United States, Thailand, Italy, Germany