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Clinical Trials on Hemoglobinuria, Paroxysmal in United States
Total 196 results
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King's College Hospital NHS TrustCompletedParoxysmal Nocturnal HaemoglobinuriaUnited Kingdom
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Apellis Pharmaceuticals, Inc.RecruitingParoxysmal Nocturnal Hemoglobinuria (PNH) | Paroxysmal HemoglobinuriaMalaysia, United States, Czechia, France, Netherlands, Serbia, Spain, Thailand, United Kingdom
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National Heart, Lung, and Blood Institute (NHLBI)CompletedParoxysmal HemoglobinuriaUnited States
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National Heart, Lung, and Blood Institute (NHLBI)CompletedParoxysmal Hemoglobinuria, NocturnalUnited States
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Ra PharmaceuticalsCompletedParoxysmal Nocturnal Hemoglobinuria (PNH)United States
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Alexion PharmaceuticalsTerminatedParoxysmal Nocturnal Hemoglobinuria (PNH)United States, Czech Republic, Italy, Poland, United Kingdom
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Apellis Pharmaceuticals, Inc.CompletedParoxysmal Nocturnal Hemoglobinuria (PNH)United States
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Sidney Kimmel Comprehensive Cancer Center at Johns...CompletedAplastic Anemia | Paroxysmal Hemoglobinuria, NocturnalUnited States
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Alexion PharmaceuticalsAchillion, a wholly owned subsidiary of AlexionCompletedParoxysmal Nocturnal Hemoglobinuria (PNH)United Kingdom, New Zealand, Korea, Republic of, Italy
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Alnylam PharmaceuticalsCompletedParoxysmal Nocturnal Hemoglobinuria (PNH)Spain, United Kingdom
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Alexion PharmaceuticalsCompletedParoxysmal Hemoglobinuria, NocturnalUnited States, Australia, Belgium, Canada, Germany, Italy, Spain, Sweden, United Kingdom, France, Ireland, Netherlands
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AlexionCompletedParoxysmal Nocturnal Hemoglobinuria (PNH)United States, Korea, Republic of, Canada, France, Germany, Spain, United Kingdom, Japan, Australia, Italy, Netherlands
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Aplastic Anemia and MDS International FoundationNational Organization for Rare DisordersRecruiting
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AKARI TherapeuticsEnrolling by invitationParoxysmal Nocturnal Hemoglobinuria (PNH)United States
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AlexionActive, not recruitingParoxysmal Nocturnal Hemoglobinuria (PNH)United Kingdom, Italy, Canada, Korea, Republic of, New Zealand, Spain, Turkey
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Ra PharmaceuticalsCompletedParoxysmal Nocturnal Hemoglobinuria (PNH)United Kingdom, Australia, Canada, Denmark, Finland, Germany, Hungary, New Zealand
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Alexion Pharmaceuticals, Inc.Achillion, a wholly owned subsidiary of AlexionCompletedParoxysmal Nocturnal Hemoglobinuria (PNH)United Kingdom, United States, Italy
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AlexionCompletedParoxysmal Nocturnal Hemoglobinuria (PNH)Belgium, France, Italy, Japan, Spain, Taiwan, United Kingdom, United States, Canada, Czechia, Germany, Sweden, Singapore, Korea, Republic of, Russian Federation, Austria, Poland, Argentina, Australia, Brazil, Estonia, Malaysia, Mexico, Thaila... and more
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National Heart, Lung, and Blood Institute (NHLBI)Completed
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University of UtahNational Institutes of Health (NIH)CompletedHemoglobinuria, ParoxysmalUnited States
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Alexion PharmaceuticalsCompletedHemoglobinuria, ParoxysmalUnited States
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Ra Pharmaceuticals, Inc.TerminatedParoxysmal Nocturnal Hemoglobinuria (PNH)United States, Australia, Canada, Finland, Germany, Hungary, New Zealand, United Kingdom
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AlexionCompletedParoxysmal Nocturnal HemoglobinuriaFrance, United Kingdom, Norway, Russian Federation, Netherlands, United States
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BioCryst PharmaceuticalsTerminatedBCX9930 for Treatment of PNH in Subjects With Inadequate Response to C5 Inhibitor Therapy (REDEEM-1)Paroxysmal Nocturnal Hemoglobinuria (PNH)United Kingdom, Hungary, France, Italy, Spain
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Jonsson Comprehensive Cancer CenterCompleted
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BioCryst PharmaceuticalsCompletedParoxysmal Nocturnal HemoglobinuriaUnited Kingdom, Austria, South Africa
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Alexion PharmaceuticalsCompletedParoxysmal Nocturnal Hemoglobinuria | PNHAustralia, France, United Kingdom, Belgium, Germany, Netherlands, Ireland, United States, Switzerland, Italy
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Alexion PharmaceuticalsCompletedParoxysmal Nocturnal HemoglobinuriaUnited Kingdom
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Novartis PharmaceuticalsCompletedParoxysmal Nocturnal Hemoglobinuria (PNH)Italy, Japan, Taiwan, Germany, France, United Kingdom, Spain, Korea, Republic of, Czechia, Brazil, Netherlands, United States
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Memorial Sloan Kettering Cancer CenterNational Cancer Institute (NCI)CompletedLeukemia | Lymphoblastic Lymphoma | Myelodysplastic Syndrome | Paroxysmal Nocturnal Hemoglobinuria (PNH) | Allogeneic Stem Cell Transplant | Non-HodgkinsUnited States
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Regeneron PharmaceuticalsCompletedParoxysmal Nocturnal Hemoglobinuria (PNH)Hong Kong, Hungary, Korea, Republic of, Malaysia, United Kingdom
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Novartis PharmaceuticalsCompletedParoxysmal Nocturnal Hemoglobinuria (PNH)China, Germany, Singapore, Korea, Republic of, Italy, United Kingdom, Malaysia, France
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Regeneron PharmaceuticalsTerminatedParoxysmal Nocturnal HemoglobinuriaUnited States
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BioCryst PharmaceuticalsActive, not recruitingParoxysmal Nocturnal Hemoglobinuria | PNHUnited Kingdom, Austria, South Africa
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Apellis Pharmaceuticals, Inc.CompletedParoxysmal Nocturnal HemoglobinuriaUnited States, France, Russian Federation, Korea, Republic of, Canada, Germany, Australia, Japan, Spain, Belgium, United Kingdom
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Alexion Pharmaceuticals, Inc.RecruitingParoxysmal Nocturnal HemoglobinuriaUnited States
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National Heart, Lung, and Blood Institute (NHLBI)RecruitingParoxysmal Nocturnal Hemoglobinuria (PNH) | Severe Aplastic Anemia (SAA) | Hypo-Plastic Myelodysplastic Syndrome (MDS)United States
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SanofiCompletedParoxysmal Nocturnal HemoglobinuriaUnited States
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Alexion PharmaceuticalsCompletedParoxysmal Nocturnal Hemoglobinuria | PNHKorea, Republic of, Canada, France, Germany, Spain, Taiwan, United Kingdom
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David Rizzieri, MDCompletedSickle Cell Anemia | Pure Red Cell Aplasia | Paroxysmal Nocturnal Hemoglobinuria (PNH) | Severe Aplastic AnemiaUnited States
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Oregon Health and Science UniversityCompletedMicrovascular and Cardiac Dysfunction in Paroxysmal Nocturnal Hemoglobinuria and Sickle Cell DiseaseSickle Cell Disease | Paroxysmal Nocturnal Hemoglobinuria | Rheologic DiseaseUnited States
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Regeneron PharmaceuticalsCompletedParoxysmal Nocturnal HemoglobinuriaUnited Kingdom
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Alexion Pharmaceuticals, Inc.Active, not recruitingParoxysmal Nocturnal HemoglobinuriaFrance, Italy, Spain, United States, Thailand, Korea, Republic of, United Kingdom, Israel, Czechia, Greece, Poland, Brazil, Japan, Canada, Malaysia
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Omeros CorporationRecruitingParoxysmal Nocturnal HemoglobinuriaSwitzerland, Germany, Ukraine, United Kingdom
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Omeros CorporationRecruitingParoxysmal Nocturnal HemoglobinuriaGermany, Greece, Switzerland, United Kingdom
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Novartis PharmaceuticalsRecruitingParoxysmal Nocturnal HemoglobinuriaFrance, Spain, Italy, Turkey, Germany, United States, Korea, Republic of, United Kingdom
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Alexion Pharmaceuticals, Inc.CompletedParoxysmal Nocturnal HemoglobinuriaItaly, Spain, Belgium, France, Turkey, Austria, Brazil, Netherlands, Australia, Finland, Russian Federation, Sweden, Canada, United States
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Regeneron PharmaceuticalsRecruitingParoxysmal Nocturnal HemoglobinuriaMexico, Korea, Republic of, Turkey, Italy, United Kingdom, Thailand, Poland, Singapore, Spain, Taiwan, Canada, Japan, United States, Malaysia, Greece, Romania, Hungary
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Hoffmann-La RocheChugai PharmaceuticalRecruitingParoxysmal Nocturnal HemoglobinuriaUnited States, Korea, Republic of, Spain, Germany, Italy, Sweden, Netherlands, Japan, Belgium, Greece, Colombia, Saudi Arabia, Turkey, Poland, Ireland, Brazil, Canada, Czechia, Estonia, France, Hong Kong, Singapore, Taiwan, United Kingdom and more
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BioCryst PharmaceuticalsActive, not recruitingParoxysmal Nocturnal HemoglobinuriaUnited Kingdom, Hungary, France, Spain, Malaysia, South Africa, Korea, Republic of