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Clinical Trials on Hereditary Angioedema Attack in France
Total 430 results
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Swedish Orphan BiovitrumCompletedEfficacy and Safety of Once Daily Dosing Compared to Twice Daily Dosing of Nitisinone in HT-1 (HT-1)Hereditary Tyrosinemia, Type IBelgium, Denmark, France, Germany, Sweden
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Swedish Orphan BiovitrumCompletedHereditary Tyrosinemia, Type IGermany, United Kingdom, France
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Centre Hospitalier National d'Ophtalmologie des...RecruitingHypertension | Retinal Degeneration | Diabetic Retinopathy | Macular Edema | Retinitis Pigmentosa | Macular Dystrophy | Maculopathy, Age Related | Occlusion Retinal VeinFrance
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University Hospital, BrestRecruiting
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University of LeicesterChildren's Cancer and Leukaemia Group; Gesellschaft fur Padiatrische Onkologie... and other collaboratorsUnknownKidney CancerUnited Kingdom, Germany, France, Netherlands
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Assistance Publique - Hôpitaux de ParisAxcan PharmaUnknownAdenomatous Polyposis Coli, FamilialFrance
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University Hospital, ToursCompletedTuberous Sclerosis Complex | LymphangioleiomyomatosisFrance
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Nantes University HospitalUniversité de NantesUnknownChronic Inflammatory Demyelinating Polyneuropathy | Anti-MAG Neuropathy | Charcot-Marie-Tooth Disease, Type IAFrance
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Assistance Publique - Hôpitaux de ParisEuropean Leukodystrophy AssociationCompletedLate Infantile Metachromatic LeukodystrophyFrance
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University Hospital, AngersRecruitingCharcot-Marie-Tooth Disease Type 2AFrance
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Akcea TherapeuticsUnited BioSource, LLCRecruitingHereditary Transthyretin Amyloidosis With PolyneuropthyFrance, Greece, Italy, Spain, Germany, Portugal, United States, Canada
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University Hospital, Clermont-FerrandCompletedCharcot-Marie-Tooth Type 1A NeuropathyFrance
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Hoffmann-La RocheActive, not recruitingHemophilia A | Mild Hereditary Factor VIII Deficiency Disease Without Inhibitor | Moderate Hereditary Factor VIII Deficiency Disease Without InhibitorUnited States, Netherlands, Belgium, France, Germany, South Africa, Spain, Canada, United Kingdom, Poland
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University Hospital, Clermont-FerrandActive, not recruitingCharcot-Marie-Tooth Type 1A NeuropathyFrance
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Novartis PharmaceuticalsTerminatedHereditary HemochromatosisBelgium, France, Russian Federation, Romania, Slovakia, Spain, Switzerland
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Hospices Civils de LyonRecruitingFamilial Mediterranean Fever | MEFV Gene MutationFrance
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University Hospital, Clermont-FerrandCompletedCIDP (Chronic Inflammatory Demyelinating Polyradiculoneuropathy) | CMT (Charcot Marie Tooth Disease)France
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Minoryx Therapeutics, S.L.RecruitingX-linked AdrenoleukodystrophyFrance
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University Hospital, BrestCompletedPost Traumatic Stress Disorder | Neurofibromatosis 1 | Diagnoses DiseaseFrance
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Ionis Pharmaceuticals, Inc.RecruitingPelizaeus-Merzbacher DiseaseFrance, Netherlands, United States, Germany
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University of BirminghamActive, not recruitingWolfram SyndromeFrance, United Kingdom, Poland, Spain
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Ultragenyx Pharmaceutical IncTerminatedHereditary Inclusion Body Myopathy | GNE Myopathy | Distal Myopathy With Rimmed Vacuoles | Distal Myopathy, Nonaka Type | Quadriceps Sparing MyopathyUnited States, Canada, United Kingdom, Israel, Italy, Bulgaria, France
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Alnylam PharmaceuticalsCompletedAmyloid Neuropathies | Amyloid Neuropathies, Familial | TTR-mediated Amyloidosis | Amyloidosis, Hereditary | Amyloidosis, Hereditary, Transthyretin-Related | Familial Amyloid PolyneuropathiesUnited States, Canada, Argentina, Australia, Bulgaria, Cyprus, Italy, Japan, Malaysia, Mexico, Netherlands, Portugal, Spain, Sweden, Germany, France, Brazil, Turkey, Korea, Republic of, Taiwan, United Kingdom
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ShireCompletedMetachromatic Leukodystrophy (MLD)Australia, Denmark, Japan, France, Germany
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Belite Bio, IncActive, not recruitingStargardt Disease 1United States, Australia, Belgium, China, France, Germany, Hong Kong, Netherlands, Switzerland, Taiwan, United Kingdom
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Clementia Pharmaceuticals Inc.TerminatedExostoses, Multiple HereditaryUnited States, Spain, Canada, Japan, Italy, Portugal, United Kingdom, Turkey, Australia, Belgium, France, Netherlands
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NightstaRx Ltd, a Biogen CompanyCompletedChoroideremiaFinland, United States, Canada, Denmark, Netherlands, Germany, United Kingdom, Brazil, France
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SanofiTerminatedRetinitis Pigmentosa | Usher SyndromeUnited States, France
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MedDay Pharmaceuticals SACompletedCharcot-Marie-Tooth Disease | Peripheral Neuropathy | Chronic Inflammatory Demyelinating Polyneuropathy | Charcot-Marie-Tooth Disease Type 1A | Charcot-Marie-Tooth Disease, Type 1B | Anti-MAG NeuropathyFrance
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Centre Hospitalier Universitaire de NiceUnknownNeurofibromatosis 2 | Dermatology/Skin - OtherFrance
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Assistance Publique - Hôpitaux de ParisCompleted
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Fondation Ophtalmologique Adolphe de RothschildRecruitingTuberous Sclerosis | Focal Cortical Dysplasia | Hemimegalencephaly | Refractory Focal Epilepsy | Mild Malformation of Cortical Development With Oligodendroglial Hyperplasia in Epilepsy (MOGHE)France
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SanofiActive, not recruitingUsher's SyndromeUnited States, France
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Assistance Publique - Hôpitaux de ParisCompletedNephroblastoma With Vena Cava ThrombosisFrance
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Assistance Publique - Hôpitaux de ParisUnknownBehçet's Disease, neuroBehcet, Anxiety, Depression, TirednessFrance
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Novartis PharmaceuticalsCompletedHereditary Periodic FeversBelgium, Italy, Japan, Russian Federation, Turkey, Spain, Germany, United Kingdom, France, United States, Ireland, Israel, Canada, Hungary, Netherlands, Switzerland
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Nantes University HospitalTerminatedFamilial Adenomatous Polyposis | Inflammatory Bowel Disease (IBD)France
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Jaeb Center for Health ResearchFoundation Fighting BlindnessActive, not recruitingEye Diseases | Retinitis PigmentosaUnited States, Israel, Finland, Canada, France, Germany, Netherlands
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AstraZenecaCompletedIschemic Attack, Transient | Stroke, Acute | Cerebral Stroke | Cerebrovascular StrokeUnited States, Australia, Brazil, Bulgaria, Czech Republic, France, Korea, Republic of, Mexico, Poland, Russian Federation, South Africa, Spain, United Kingdom, Philippines, China, Germany, Hungary, Hong Kong, Argentina, Austria, Cana... and more
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University Hospital, ToulouseNot yet recruitingFamilial Adenomatous PolyposisFrance
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Janssen Research & Development, LLCJanssen Research & Development, LLCActive, not recruitingX-Linked Retinitis PigmentosaBelgium, Canada, United States, Israel, United Kingdom, Denmark, France, Italy, Netherlands, Switzerland, Spain
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Novartis PharmaceuticalsCompletedIron Overload | Hereditary HemochromatosisUnited States, Germany, Italy, Australia, Canada, France
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Kubota Vision Inc.Food and Drug Administration (FDA)CompletedStargardt DiseaseUnited States, United Kingdom, Germany, Spain, Brazil, Canada, Denmark, France, Italy, Netherlands, South Africa
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Janssen Research & Development, LLCJanssen Research & Development, LLCActive, not recruitingX-Linked Retinitis PigmentosaUnited States, Canada, Israel, United Kingdom, Denmark, France, Belgium, Italy, Netherlands, Switzerland, Spain
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Centre Hospitalier National d'Ophtalmologie des...Institut National de la Santé Et de la Recherche Médicale, FranceUnknownUsher SyndromeFrance, Germany, Netherlands, Portugal
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Institut National de la Santé Et de la Recherche...RecruitingNeurofibromatosis Type 1 | Ichthyosis | Ectodermal Dysplasia | Albinism | Pemphigus | Mucous Membrane Pemphigoid | Inherited Epidermolysis Bullosa | Palmoplantar Keratoderma | Incontinentia PigmentiFrance
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Jaeb Center for Health ResearchDepartment of Health and Human Services; Food and Drug Administration (FDA); Conquering...RecruitingGyrate Atrophy | Gyrata of Choroid and Retina; Atrophy | Ornithine-δ-aminotransferase | OAT | Chorioretinal DegenerationUnited States, Finland, France, United Kingdom, Germany, Brazil, Canada
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Ionis Pharmaceuticals, Inc.RecruitingPelizaeus-Merzbacher DiseaseFrance, Australia, Germany, Netherlands
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Novartis PharmaceuticalsCompletedFamilial Cold Autoinflammatory SyndromeUnited States, France, Germany
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Pixium Vision SACompletedRetinitis Pigmentosa | Choroideremia | Cone Rod DystrophyAustria, Spain, United Kingdom, France, Germany