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Clinical Trials on Hereditary Angioedema in France
Total 395 results
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Centre Hospitalier National d'Ophtalmologie des...Assistance Publique - Hôpitaux de ParisRecruiting
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University Hospital, ToulouseCompleted
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Hospices Civils de LyonCompletedNeurofibromatosis Type 1France
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Hospices Civils de LyonWithdrawnFacial AngiofibromasFrance
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Alnylam PharmaceuticalsRecruitingPolyneuropathy | Hereditary Transthyretin-mediated (hATTR) AmyloidosisNetherlands, Spain, United States, Germany, France, Italy, Portugal
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University Hospital, Strasbourg, FranceTerminated
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Columbia UniversityLudwig-Maximilians - University of Munich; Moorfields Eye Hospital NHS Foundation... and other collaboratorsRecruitingRetinitis Pigmentosa Associated With CNGB1 MutationsUnited States, France, Germany, United Kingdom
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Amsterdam UMC, location VUmcUniversity Hospital, Essen; Institut Curie; Ligue contre le cancer, FranceCompletedRetinoblastoma | Secondary Primary Malignancies After RetinoblastomaNetherlands, France, Germany
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University Hospital, Clermont-FerrandRecruitingBehçet Disease | Microbiota | Physiopathology | Oral MicrobiotaFrance
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Assistance Publique - Hôpitaux de ParisNovartisCompletedNeurofibromatoses | Neurofibromatosis Type 1 | Plexiform NeurofibromaFrance
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DeuterOncologyRecruitingAdult Solid Tumor | Lung Cancer | Advanced Solid Tumor | Non-small Cell Lung Cancer | Non-small Cell Carcinoma | Refractory Tumor | Hereditary Renal Papillary CancerFrance, Belgium, Netherlands
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ProQR TherapeuticsCompletedEye Diseases | Retinitis Pigmentosa | Eye Diseases, Hereditary | Vision Disorders | Retinal Disease | Eye Disorders Congenital | Usher Syndrome Type 2 | Deaf BlindUnited States, Canada, France
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Laboratoires GenévrierCompletedVitiligo | PiebaldismBelgium, France, Italy
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University Hospital, BordeauxCompletedTuberous Sclerosis | Renal AngiomyolipomasFrance
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Nantes University HospitalUniversité d'Angers (Angers, France); Association Neurofibromatoses et RecklinghaüsenCompletedNeurofibromatosis Type 1France
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Assistance Publique Hopitaux De MarseilleRecruitingCharcot-Marie-Tooth Disease Type 1AFrance
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BiogenCompletedChoroideremiaUnited States, Finland, France, Denmark, Netherlands, Germany, United Kingdom, Canada
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Swedish Orphan BiovitrumCompletedEfficacy and Safety of Once Daily Dosing Compared to Twice Daily Dosing of Nitisinone in HT-1 (HT-1)Hereditary Tyrosinemia, Type IBelgium, Denmark, France, Germany, Sweden
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Institut National de la Santé Et de la Recherche...Assistance Publique - Hôpitaux de Paris; European Leukodystrophy AssociationActive, not recruitingMetachromatic LeukodystrophyFrance
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Assistance Publique - Hôpitaux de ParisNot yet recruiting
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Centre Hospitalier National d'Ophtalmologie des...RecruitingHypertension | Retinal Degeneration | Diabetic Retinopathy | Macular Edema | Retinitis Pigmentosa | Macular Dystrophy | Maculopathy, Age Related | Occlusion Retinal VeinFrance
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Swedish Orphan BiovitrumCompletedHereditary Tyrosinemia, Type IGermany, United Kingdom, France
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University Hospital, BrestRecruiting
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University of LeicesterChildren's Cancer and Leukaemia Group; Gesellschaft fur Padiatrische Onkologie... and other collaboratorsUnknownKidney CancerUnited Kingdom, Germany, France, Netherlands
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Akcea TherapeuticsUnited BioSource, LLCRecruitingHereditary Transthyretin Amyloidosis With PolyneuropthyFrance, Greece, Italy, Spain, Germany, Portugal, United States, Canada
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University Hospital, ToursCompletedTuberous Sclerosis Complex | LymphangioleiomyomatosisFrance
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Nantes University HospitalUniversité de NantesUnknownChronic Inflammatory Demyelinating Polyneuropathy | Anti-MAG Neuropathy | Charcot-Marie-Tooth Disease, Type IAFrance
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Assistance Publique - Hôpitaux de ParisAxcan PharmaUnknownAdenomatous Polyposis Coli, FamilialFrance
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University Hospital, AngersRecruitingCharcot-Marie-Tooth Disease Type 2AFrance
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Assistance Publique - Hôpitaux de ParisEuropean Leukodystrophy AssociationCompletedLate Infantile Metachromatic LeukodystrophyFrance
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Novartis PharmaceuticalsTerminatedHereditary HemochromatosisBelgium, France, Russian Federation, Romania, Slovakia, Spain, Switzerland
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University Hospital, Clermont-FerrandCompletedCharcot-Marie-Tooth Type 1A NeuropathyFrance
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University Hospital, Clermont-FerrandActive, not recruitingCharcot-Marie-Tooth Type 1A NeuropathyFrance
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Hoffmann-La RocheActive, not recruitingHemophilia A | Mild Hereditary Factor VIII Deficiency Disease Without Inhibitor | Moderate Hereditary Factor VIII Deficiency Disease Without InhibitorUnited States, Netherlands, Belgium, France, Germany, South Africa, Spain, Canada, United Kingdom, Poland
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Hospices Civils de LyonRecruitingFamilial Mediterranean Fever | MEFV Gene MutationFrance
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University Hospital, Clermont-FerrandCompletedCIDP (Chronic Inflammatory Demyelinating Polyradiculoneuropathy) | CMT (Charcot Marie Tooth Disease)France
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Minoryx Therapeutics, S.L.RecruitingX-linked AdrenoleukodystrophyFrance
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University Hospital, BrestCompletedPost Traumatic Stress Disorder | Neurofibromatosis 1 | Diagnoses DiseaseFrance
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Ionis Pharmaceuticals, Inc.RecruitingPelizaeus-Merzbacher DiseaseFrance, Netherlands, United States, Germany
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University of BirminghamActive, not recruitingWolfram SyndromeFrance, United Kingdom, Poland, Spain
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Alnylam PharmaceuticalsCompletedAmyloid Neuropathies | Amyloid Neuropathies, Familial | TTR-mediated Amyloidosis | Amyloidosis, Hereditary | Amyloidosis, Hereditary, Transthyretin-Related | Familial Amyloid PolyneuropathiesUnited States, Canada, Argentina, Australia, Bulgaria, Cyprus, Italy, Japan, Malaysia, Mexico, Netherlands, Portugal, Spain, Sweden, Germany, France, Brazil, Turkey, Korea, Republic of, Taiwan, United Kingdom
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Ultragenyx Pharmaceutical IncTerminatedHereditary Inclusion Body Myopathy | GNE Myopathy | Distal Myopathy With Rimmed Vacuoles | Distal Myopathy, Nonaka Type | Quadriceps Sparing MyopathyUnited States, Canada, United Kingdom, Israel, Italy, Bulgaria, France
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ShireCompletedMetachromatic Leukodystrophy (MLD)Australia, Denmark, Japan, France, Germany
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Belite Bio, IncActive, not recruitingStargardt Disease 1United States, Australia, Belgium, China, France, Germany, Hong Kong, Netherlands, Switzerland, Taiwan, United Kingdom
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Clementia Pharmaceuticals Inc.TerminatedExostoses, Multiple HereditaryUnited States, Spain, Canada, Japan, Italy, Portugal, United Kingdom, Turkey, Australia, Belgium, France, Netherlands
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NightstaRx Ltd, a Biogen CompanyCompletedChoroideremiaFinland, United States, Canada, Denmark, Netherlands, Germany, United Kingdom, Brazil, France
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SanofiTerminatedRetinitis Pigmentosa | Usher SyndromeUnited States, France
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SanofiActive, not recruitingUsher's SyndromeUnited States, France
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MedDay Pharmaceuticals SACompletedCharcot-Marie-Tooth Disease | Peripheral Neuropathy | Chronic Inflammatory Demyelinating Polyneuropathy | Charcot-Marie-Tooth Disease Type 1A | Charcot-Marie-Tooth Disease, Type 1B | Anti-MAG NeuropathyFrance
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Centre Hospitalier Universitaire de NiceUnknownNeurofibromatosis 2 | Dermatology/Skin - OtherFrance