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Clinical Trials on Hereditary Angioedema in France
Total 392 results
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Assistance Publique - Hôpitaux de ParisUnknownBehçet's Disease, neuroBehcet, Anxiety, Depression, TirednessFrance
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Assistance Publique - Hôpitaux de ParisCompletedNephroblastoma With Vena Cava ThrombosisFrance
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Belite Bio, IncActive, not recruitingStargardt Disease 1United States, Australia, Belgium, China, France, Germany, Hong Kong, Netherlands, Switzerland, Taiwan, United Kingdom
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Novartis PharmaceuticalsCompletedHereditary Periodic FeversBelgium, Italy, Japan, Russian Federation, Turkey, Spain, Germany, United Kingdom, France, United States, Ireland, Israel, Canada, Hungary, Netherlands, Switzerland
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Nantes University HospitalTerminatedFamilial Adenomatous Polyposis | Inflammatory Bowel Disease (IBD)France
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Janssen Research & Development, LLCJanssen Research & Development, LLCActive, not recruitingX-Linked Retinitis PigmentosaBelgium, Canada, United States, Israel, United Kingdom, Spain, Denmark, France, Italy, Netherlands, Switzerland
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University Hospital, ToulouseNot yet recruitingFamilial Adenomatous PolyposisFrance
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Kubota Vision Inc.Food and Drug Administration (FDA)CompletedStargardt DiseaseUnited States, United Kingdom, Germany, Spain, Brazil, Canada, Denmark, France, Italy, Netherlands, South Africa
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Jaeb Center for Health ResearchFoundation Fighting BlindnessActive, not recruitingEye Diseases | Retinitis PigmentosaUnited States, Israel, Finland, Canada, France, Germany, Netherlands
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Centre Hospitalier National d'Ophtalmologie des...Institut National de la Santé Et de la Recherche Médicale, FranceUnknownUsher SyndromeFrance, Germany, Netherlands, Portugal
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Institut National de la Santé Et de la Recherche...RecruitingNeurofibromatosis Type 1 | Ichthyosis | Ectodermal Dysplasia | Albinism | Pemphigus | Mucous Membrane Pemphigoid | Inherited Epidermolysis Bullosa | Palmoplantar Keratoderma | Incontinentia PigmentiFrance
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Novartis PharmaceuticalsCompletedIron Overload | Hereditary HemochromatosisUnited States, Germany, Italy, Australia, Canada, France
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Janssen Research & Development, LLCJanssen Research & Development, LLCActive, not recruitingX-Linked Retinitis PigmentosaUnited States, Canada, Israel, United Kingdom, Spain, Denmark, France, Belgium, Italy, Netherlands, Switzerland
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Novartis PharmaceuticalsCompletedFamilial Cold Autoinflammatory SyndromeUnited States, France, Germany
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Pixium Vision SACompletedRetinitis Pigmentosa | Choroideremia | Cone Rod DystrophyAustria, Spain, United Kingdom, France, Germany
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NightstaRx Ltd, a Biogen CompanyCompletedX-Linked Retinitis PigmentosaUnited States, France, United Kingdom, Finland, Netherlands, Germany, Canada
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Ionis Pharmaceuticals, Inc.CompletedHereditary Transthyretin-Mediated Amyloid PolyneuropathyUnited States, Spain, Taiwan, Italy, Germany, Argentina, Australia, Brazil, Canada, Cyprus, France, Greece, New Zealand, Portugal, Sweden, Turkey
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Ultragenyx Pharmaceutical IncNewcastle UniversityCompletedHereditary Inclusion Body Myopathy | GNE Myopathy | Nonaka Disease | Quadriceps Sparing Myopathy (QSM) | Distal Myopathy With Rimmed Vacuoles (DMRV)United States, Bulgaria, Canada, France, United Kingdom
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Hospices Civils de LyonCompletedTelangiectasia, Hereditary Hemorrhagic | Rendu Osler DiseaseFrance
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Ionis Pharmaceuticals, Inc.RecruitingPelizaeus-Merzbacher DiseaseFrance, Australia, Germany, Netherlands
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Jaeb Center for Health ResearchDepartment of Health and Human Services; Food and Drug Administration (FDA); Conquering...RecruitingGyrate Atrophy | Gyrata of Choroid and Retina; Atrophy | Ornithine-δ-aminotransferase | OAT | Chorioretinal DegenerationUnited States, Canada, Finland, France, United Kingdom, Germany, Brazil
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Rhythm Pharmaceuticals, Inc.CompletedBardet Biedl Syndrome (BBS) | Alström Syndrome (AS)United States, United Kingdom, France, Canada, Puerto Rico, Spain
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University Hospital, ToulouseCompleted
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Astellas Pharma Global Development, Inc.Active, not recruitingStargardt's Macular DystrophyItaly, United States, Israel, United Kingdom, Germany, Spain, Hungary, France
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Alnylam PharmaceuticalsCompletedAcute Hepatic Porphyria | Acute Intermittent Porphyria | Porphyria, Acute Intermittent | Acute Porphyria | Hereditary Coproporphyria (HCP) | Variegate Porphyria (VP) | ALA Dehydratase Deficient Porphyria (ADP)United States, Spain, United Kingdom, Korea, Republic of, Australia, Bulgaria, Canada, Denmark, Finland, France, Germany, Italy, Japan, Mexico, Netherlands, Poland, Sweden, Taiwan
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Ionis Pharmaceuticals, Inc.RecruitingHereditary Transthyretin-Mediated Amyloid PolyneuropathyUnited States, Italy, Portugal, Spain, Taiwan, Sweden, Canada, Brazil, France, New Zealand, Argentina, Cyprus, Australia, Turkey
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Alnylam PharmaceuticalsCompletedAmyloid Neuropathies | Amyloid Neuropathies, Familial | Amyloidosis, Hereditary | Transthyretin (TTR) Mediated Familial Amyloidotic Cardiomyopathy (FAC) | Amyloidosis, Hereditary, Transthyretin-Related | Familial Transthyretin Cardiac AmyloidosisUnited States, France, Italy, Spain, Canada, Germany, Belgium, Sweden, United Kingdom
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Institut CurieRecruiting
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MedDay Pharmaceuticals SACompletedAdrenoleukodystrophy | Adrenomyeloneuropathy | AMNFrance, Germany, Spain
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La Jolla Pharmaceutical CompanyPRA Health SciencesCompletedHereditary HemochromatosisUnited States, Australia, France, United Kingdom
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Institut CurieFondation Rothschild ParisRecruiting
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NightstaRx Ltd, a Biogen CompanyEnrolling by invitationChoroideremia | X-Linked Retinitis PigmentosaUnited States, United Kingdom, Netherlands, Germany, France, Brazil, Canada, Denmark, Finland
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ShireTakeda Development Center Americas, Inc.Active, not recruitingMetachromatic Leukodystrophy (MLD)Denmark, Germany, Japan, Australia, France, Brazil, Czechia
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Assistance Publique - Hôpitaux de ParisRecruitingAdrenoleukodystrophy | Adrenomyeloneuropathy | Metachromatic Leukodystrophy | Adult-Onset Leukoencephalopathy With Axonal Spheroids and Pigmented GliaFrance
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Centre Oscar LambretRecruiting
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Assistance Publique - Hôpitaux de ParisCompletedVasculitis | Behcet's DiseaseFrance
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Assistance Publique - Hôpitaux de ParisNational Research Agency, FranceCompletedRheumatoid Arthritis | Uveitis | Vasculitis | Type 1 Diabetes | Crohn's Disease | Myositis | Healthy Volunteer | Ankylosing Spondylitis | FMF | Systemic Lupus Erythematosus/Antiphospholipid Syndrome | Cryopyrin-Associated Periodic Syndromes /TNF-receptor Associated Periodic Syndrome | Ulcerative Rectocolitis | Unclassified...France
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Ultragenyx Pharmaceutical IncCompletedHereditary Inclusion Body Myopathy | GNE Myopathy | Distal Myopathy With Rimmed Vacuoles | Distal Myopathy, Nonaka TypeUnited States, Canada, United Kingdom, Israel, Italy, Bulgaria, France
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Sergiusz JozwiakMedical University of Vienna; Charite University, Berlin, Germany; Institut National... and other collaboratorsUnknownEpilepsy | Tuberous Sclerosis Complex | TSCPoland, Austria, Belgium, Czech Republic, France, Germany, Italy, Netherlands
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Forge Biologics, IncRecruitingKrabbe DiseaseUnited States
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ProQR TherapeuticsTerminatedRetinitis Pigmentosa | Usher Syndrome Type 2United States, Canada, France
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Ultragenyx Pharmaceutical IncTerminatedHereditary Inclusion Body Myopathy | GNE Myopathy | Inclusion Body Myopathy 2 | Distal Myopathy With Rimmed Vacuoles | Distal Myopathy, Nonaka Type | Quadriceps Sparing MyopathyCanada, United States, Bulgaria
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University Hospital, BordeauxRecruitingIntellectual Disability | Cystic Fibrosis | Neurodegeneration With Brain Iron Accumulation (NBIA) | Congenital Heart Defect | Albinism | Rubinstein-Taybi Syndrome | Periventricular Nodular HeterotopiaFrance
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Assistance Publique - Hôpitaux de ParisIltoo PharmaCompletedRheumatoid Arthritis | Systemic Lupus Erythematosus | Psoriasis | Systemic Sclerosis | Crohn's Disease | Ulcerative Colitis | Idiopathic Thrombocytopenic Purpura | Autoimmune Hepatitis | Wegener's Granulomatosis | Ankylosing Spondylitis | Behcet's Disease | Takayasu's Disease | Sclerosing Cholangitis | Gougerot-sj...France
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Forge Biologics, IncActive, not recruiting
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Hoffmann-La RocheRecruitingThyroid Eye DiseaseKorea, Republic of, United Kingdom, United States, Canada, China, Israel, France, Spain
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Minoryx Therapeutics, S.L.Active, not recruitingCerebral AdrenoleukodystrophySpain, Germany, France, Argentina
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National Cancer Institute (NCI)Active, not recruitingLynch Syndrome | Stage III Colon Cancer AJCC v8 | Colon Adenocarcinoma | DNA Repair DisorderUnited States, Puerto Rico, Germany
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Alnylam PharmaceuticalsRecruitingAcute Hepatic PorphyriaBelgium, France, Germany, United Kingdom, United States, Italy, Switzerland, Sweden
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NovartisCompletedMuckle Wells SyndromeUnited States, Spain, United Kingdom, France, Germany, India