- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Hereditary Autoinflammatory Diseases in France
Total 34947 results
-
Centre Hospitalier de CayenneUnknown
-
Centre Hospitalier de CayenneRecruitingHuman Immunodeficiency VirusFrench Guiana
-
Alnylam PharmaceuticalsCompletedAcute Hepatic Porphyria | Acute Intermittent Porphyria | Porphyria, Acute Intermittent | Acute Porphyria | Hereditary Coproporphyria (HCP) | Variegate Porphyria (VP) | ALA Dehydratase Deficient Porphyria (ADP)United States, Spain, United Kingdom, Korea, Republic of, Australia, Bulgaria, Canada, Denmark, Finland, France, Germany, Italy, Japan, Mexico, Netherlands, Poland, Sweden, Taiwan
-
Centre Hospitalier de CayenneEuropean Regional Development FundRecruitingChildren | Dengue Fever | AdultsFrance
-
Alnylam PharmaceuticalsCompletedAmyloid Neuropathies | Amyloid Neuropathies, Familial | Amyloidosis, Hereditary | Transthyretin (TTR) Mediated Familial Amyloidotic Cardiomyopathy (FAC) | Amyloidosis, Hereditary, Transthyretin-Related | Familial Transthyretin Cardiac AmyloidosisUnited States, France, Italy, Spain, Canada, Germany, Belgium, Sweden, United Kingdom
-
Ionis Pharmaceuticals, Inc.RecruitingHereditary Transthyretin-Mediated Amyloid PolyneuropathyUnited States, Italy, Portugal, Spain, Taiwan, Sweden, Canada, Brazil, France, New Zealand, Argentina, Cyprus, Australia, Turkey
-
Centre Hospitalier de Cayenneuniversite de guyaneCompleted
-
Centre Hospitalier de CayenneCompleted
-
Centre Hospitalier de CayenneCompleted
-
Centre Hospitalier de CayenneCompleted
-
Centre Hospitalier de CayenneCompleted
-
Centre Hospitalier de CayenneRecruitingHIV SeropositivityFrench Guiana
-
Centre Hospitalier de CayenneUnknown
-
Hoffmann-La RocheRecruitingThyroid Eye DiseaseKorea, Republic of, United Kingdom, United States, Canada, China, Israel, France, Spain
-
ShireTakeda Development Center Americas, Inc.Active, not recruitingMetachromatic Leukodystrophy (MLD)Denmark, Germany, Japan, Australia, France, Brazil, Czechia
-
Institut CurieRecruiting
-
MedDay Pharmaceuticals SACompletedAdrenoleukodystrophy | Adrenomyeloneuropathy | AMNFrance, Germany, Spain
-
NightstaRx Ltd, a Biogen CompanyEnrolling by invitationChoroideremia | X-Linked Retinitis PigmentosaUnited States, United Kingdom, Netherlands, Germany, France, Brazil, Canada, Denmark, Finland
-
La Jolla Pharmaceutical CompanyPRA Health SciencesCompletedHereditary HemochromatosisUnited States, Australia, France, United Kingdom
-
Assistance Publique - Hôpitaux de ParisRecruitingAdrenoleukodystrophy | Adrenomyeloneuropathy | Metachromatic Leukodystrophy | Adult-Onset Leukoencephalopathy With Axonal Spheroids and Pigmented GliaFrance
-
Centre Oscar LambretRecruiting
-
Forge Biologics, IncRecruitingKrabbe DiseaseUnited States
-
Institut CurieFondation Rothschild ParisRecruiting
-
University Hospital, BordeauxRecruitingIntellectual Disability | Cystic Fibrosis | Neurodegeneration With Brain Iron Accumulation (NBIA) | Congenital Heart Defect | Albinism | Rubinstein-Taybi Syndrome | Periventricular Nodular HeterotopiaFrance
-
AmgenActive, not recruitingThyroid Eye DiseaseUnited States, Spain, Germany, Italy, France, United Kingdom
-
Minoryx Therapeutics, S.L.Active, not recruitingCerebral AdrenoleukodystrophySpain, Germany, France, Argentina
-
Jaeb Center for Health ResearchFoundation Fighting BlindnessRecruitingRetinitis Pigmentosa | Inherited Retinal DegenerationUnited States, United Kingdom, France, Finland, Israel, Netherlands, Switzerland, Australia, Canada, Brazil, Mexico
-
Ultragenyx Pharmaceutical IncCompletedHereditary Inclusion Body Myopathy | GNE Myopathy | Distal Myopathy With Rimmed Vacuoles | Distal Myopathy, Nonaka TypeUnited States, Canada, United Kingdom, Israel, Italy, Bulgaria, France
-
Sergiusz JozwiakMedical University of Vienna; Charite University, Berlin, Germany; Institut National... and other collaboratorsUnknownEpilepsy | Tuberous Sclerosis Complex | TSCPoland, Austria, Belgium, Czech Republic, France, Germany, Italy, Netherlands
-
Ultragenyx Pharmaceutical IncTerminatedHereditary Inclusion Body Myopathy | GNE Myopathy | Inclusion Body Myopathy 2 | Distal Myopathy With Rimmed Vacuoles | Distal Myopathy, Nonaka Type | Quadriceps Sparing MyopathyCanada, United States, Bulgaria
-
ProQR TherapeuticsTerminatedRetinitis Pigmentosa | Usher Syndrome Type 2United States, Canada, France
-
Medacta International SAActive, not recruitingArthrosis | Congenital Hip Dysplasia | Traumatic Arthritis | Rheumatoid Polyarthritis | Avascular Necrosis of the Femoral HeadFrance
-
Alnylam PharmaceuticalsRecruitingAcute Hepatic PorphyriaBelgium, France, Germany, United Kingdom, United States, Italy, Switzerland, Sweden
-
Centre Hospitalier Universitaire de Pointe-a-PitreRecruitingAtypical ParkinsonismMartinique, French Guiana
-
National Cancer Institute (NCI)Active, not recruitingLynch Syndrome | Stage III Colon Cancer AJCC v8 | Colon Adenocarcinoma | DNA Repair DisorderUnited States, Puerto Rico, Germany
-
Enyo PharmaRecruitingAlport SyndromeGermany, Spain, United States, France
-
Promethera TherapeuticsCompletedUrea Cycle Disorders | Crigler Najjar SyndromeIsrael, United Kingdom, Belgium, France, Italy
-
Stallergenes GreerCompletedPrimary DiseaseFrance, Italy, Spain
-
Centre Hospitalier de CayenneBichat HospitalCompletedMental Health | Sexual HealthFrance, French Guiana
-
AstraZenecaRecruitingAdv Solid Malig - H&N SCC, ATM Pro / Def NSCLC, Gastric, Breast and Ovarian CancerSpain, United States, Belgium, United Kingdom, France, Hungary, Canada, Korea, Republic of, Australia
-
Viridian Therapeutics, Inc.Active, not recruitingThyroid Eye DiseaseUnited States, Spain, United Kingdom, Canada, Germany, Italy, Netherlands, Australia, France, Turkey
-
Assistance Publique - Hôpitaux de ParisNot yet recruitingHemophilia A | Hemophilia B | Cystic Fibrosis | Sickle Cell Disease | Muscular Dystrophy, Duchenne | Fragile X Syndrome | Huntington Disease | Myotonic Dystrophy | Autosomal Recessive Polycystic Kidney Disease | Neurofibromatosis-Noonan Syndrome | Muscular Dystrophy, Becker | Invasive PreNatal Diagnosis in a... and other conditionsFrance
-
University Hospital, AngersUnknownAcute Lymphoblastic Leukemia | Nephroblastoma | Hepatic Veno-Occlusive DiseaseFrance
-
Genzyme, a Sanofi CompanyCompletedAlport Syndrome Patients With eGFR Between 45-90 ml/Min/1.73 m2France, Germany, Australia, United States, United Kingdom, Canada
-
University Hospital Center of MartiniqueRecruitingEpilepsy | Status EpilepticusFrance
-
bluebird bioCompletedCerebral Adrenoleukodystrophy (CALD)United States, France, Germany, Italy, Netherlands, United Kingdom
-
LYSOGENETerminatedGM1 GangliosidosisUnited Kingdom, United States, France
-
Gynecologic Oncology GroupNational Cancer Institute (NCI)CompletedOsteoporosis | Ovarian Carcinoma | Hereditary Breast and Ovarian Cancer SyndromeUnited States
-
Alnylam PharmaceuticalsCompletedAcute Hepatic PorphyriaUnited States, Belgium, Bulgaria, France, Italy, Mexico, Spain, Taiwan, United Kingdom, Netherlands, Korea, Republic of, Switzerland, Czechia, Poland, Finland, Australia, Germany, Israel, Norway, South Africa
-
NeuroVia, Inc.WithdrawnX-Linked AdrenoleukodystrophyAustralia, Argentina, United Kingdom, Colombia, Chile, France, Russian Federation, Ukraine