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Clinical Trials on Hereditary Diseases
Total 378202 results
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Medical University of ViennaUnknownRetina Disorder | Macula; Degeneration, Congenital or Hereditary
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Intellia TherapeuticsNot yet recruitingHereditary AngioedemaFrance, New Zealand, United Kingdom
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Ionis Pharmaceuticals, Inc.RecruitingHereditary AngioedemaUnited States, Puerto Rico, Belgium, Bulgaria, Canada, France, Germany, Israel, Italy, Netherlands, Poland, Spain, Turkey, United Kingdom
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BioMarin PharmaceuticalRecruitingHereditary Angioedema | HAEUnited States, Spain, Australia
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Pharming Technologies B.V.CompletedHereditary AngioedemaIsrael, Italy, United States, Czechia, Germany, Hungary, Poland, Romania, Slovakia, North Macedonia
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Astria Therapeutics, Inc.Completed
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Ionis Pharmaceuticals, Inc.CompletedHereditary AngioedemaUnited States, France, Netherlands, Spain, United Kingdom, Belgium, Bulgaria, Canada, Denmark, Germany, Israel, Italy, Poland, Turkey
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CSL BehringCompletedHereditary AngioedemaUnited States, Germany, Japan, Hungary, Canada, Netherlands, Israel
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TakedaCompletedHereditary AngioedemaBelgium, Bulgaria, Estonia, Spain, Hungary, Israel, Germany, Czechia, Portugal, Greece, Lithuania, Poland, Latvia, Croatia, Slovakia, Austria, Canada, Ireland, North Macedonia, Romania, Serbia, Slovenia
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TakedaCompletedHereditary AngioedemaJapan
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CSL BehringCompletedHereditary AngioedemaCanada, Australia, Germany, United States, Israel
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ShireCompletedHereditary AngioedemaUnited States, Canada, Germany, Hungary, Spain
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TakedaCompletedHereditary AngioedemaJapan
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CENTOGENE GmbH RostockTerminated
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KalVista Pharmaceuticals, Ltd.CompletedHereditary AngioedemaUnited Kingdom
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AO GENERIUMWithdrawnHereditary AngioedemaRussian Federation
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ShireCompletedHereditary AngioedemaUnited States
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ShireCompletedHereditary AngioedemaUnited States
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ShireCompletedHereditary AngioedemaUnited States, Australia, Israel, Canada, Hungary, Romania, Russian Federation, South Africa, Ukraine
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ShireCompletedHereditary AngioedemaItaly
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ShireCompletedHereditary AngioedemaUnited States
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AO GENERIUMCompletedHereditary AngioedemaRussian Federation
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BioCryst PharmaceuticalsTerminatedHereditary Angioedema | HAEFrance, Belgium
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BioCryst PharmaceuticalsCompletedHereditary AngioedemaGermany, United Kingdom
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BioCryst PharmaceuticalsCompletedHereditary AngioedemaUnited Kingdom
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NYU Langone HealthNational Eye Institute (NEI)Active, not recruitingFuch's Dystrophy | Corneal Disorders | Prior SurgeryUnited States
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Nanoscope Therapeutics Inc.CompletedEye Diseases | Retinal Degeneration | Retinal Diseases | Retinitis Pigmentosa | Retinitis | Eye Diseases, Hereditary | Retinal DystrophiesUnited States, Puerto Rico
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Case Western Reserve UniversityNational Eye Institute (NEI); Jaeb Center for Health ResearchRecruitingFuchs' Endothelial Dystrophy | Corneal Endothelial DecompensationUnited States
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Wageningen UniversityDutch Cancer Society; Wereld Kanker Onderzoek Fonds; Funding: Biobanking and...RecruitingNeoplasms | Colorectal Neoplasms | Lynch Syndrome | Hereditary Nonpolyposis Colorectal CancerNetherlands
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Kowa Research Institute, Inc.CompletedFuchs' Endothelial Corneal DystrophyUnited States, Australia, Germany, Spain, Denmark
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Cornea Research Foundation of AmericaCompletedCorneal Edema | Fuchs' DystrophyUnited States
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Alcon ResearchEnrolling by invitationCorneal Edema | Bullous Keratopathy | Corneal Dystrophy | Entropion | Corneal ErosionUnited States
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Cornea Associates of TexasCompletedKeratoconus | Corneal Ectasia | Pellucid Marginal Corneal Degeneration | Corneal DegenerationUnited States
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Aerie PharmaceuticalsCompleted
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Oregon Health and Science UniversityNational Eye Institute (NEI)Recruiting
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Mayo ClinicCompletedCorneal Edema | Fuchs DystrophyUnited States
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Spaulding Rehabilitation HospitalMassachusetts General HospitalWithdrawnHereditary Spastic Paraplegia
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University Hospital, Strasbourg, FranceTerminated
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Stealth BioTherapeutics Inc.CompletedFuchs' Corneal Endothelial Dystrophy (FCED)United States
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KalVista Pharmaceuticals, Ltd.RecruitingHereditary AngioedemaUnited States, Bulgaria, France, Greece, Israel, Netherlands, Spain, United Kingdom, Australia, Germany, South Africa, Slovakia, Austria, New Zealand, Romania, Canada, Japan
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KalVista Pharmaceuticals, Ltd.RecruitingHereditary AngioedemaUnited States, Bulgaria, France, Greece, Hungary, Israel, Italy, Netherlands, New Zealand, North Macedonia, Poland, Spain, United Kingdom, Australia, Germany, South Africa, Austria, Portugal, Slovakia, Romania, Canada, Saudi Arabia, Japa...
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Pharming Technologies B.V.US Hereditary Angioedema AssociationCompleted
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BioCryst PharmaceuticalsActive, not recruitingHereditary Angioedema | PediatricSpain, Austria, Canada, France, Germany, Israel, Italy, Poland, Romania, United Kingdom
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Ionis Pharmaceuticals, Inc.Active, not recruitingHereditary AngioedemaNetherlands, United States
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KalVista Pharmaceuticals, Ltd.CompletedHereditary AngioedemaUnited States, Australia, Bulgaria, Canada, France, Germany, Greece, Hungary, Israel, Italy, Japan, Netherlands, New Zealand, North Macedonia, Poland, Portugal, Puerto Rico, Romania, Slovakia, Spain, United Kingdom
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TakedaCompletedAngioedemas, HereditaryArgentina
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BioCryst PharmaceuticalsCompletedHereditary Angioedema | HAEUnited States, Austria, Canada, Czechia, France, Germany, Hungary, North Macedonia, Romania, Spain, United Kingdom
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ShireCompletedHereditary AngioedemaUnited States
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ShireJerini AGCompletedHereditary AngioedemaSpain, Argentina, Austria, Denmark, France, Germany, Israel, Italy, Switzerland, United Kingdom
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BioCryst PharmaceuticalsCompletedHereditary AngioedemaUnited Kingdom