- ICH GCP
- US Clinical Trials Registry
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Clinical Trials on Hereditary Angioedema (HAE)
Total 2858 results
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Children's Oncology GroupNational Cancer Institute (NCI)RecruitingStage II Kidney Wilms Tumor | Stage III Kidney Wilms Tumor | Stage IV Kidney Wilms Tumor | Recurrent Kidney Wilms Tumor | Anaplastic Kidney Wilms TumorUnited States, Canada, Puerto Rico, Australia, New Zealand, Saudi Arabia
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National Cancer Institute (NCI)RecruitingNeurofibromatosis Type 1 | Low Grade Glioma | Visual Pathway GliomaUnited States, Canada, Puerto Rico
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Boston Children's HospitalEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsRecruitingIntellectual Disability | Tuberous Sclerosis | Autism DisorderUnited States
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bluebird bioCompletedCerebral Adrenoleukodystrophy (CALD)United States, France, Germany, Italy, Netherlands, United Kingdom
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S.L.A. Pharma AGActive, not recruitingFamilial Adenomatous PolyposisItaly
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Vanderbilt UniversityNational Institute of Neurological Disorders and Stroke (NINDS)CompletedNeurofibromatosis Type 1 | Reading DisabilitiesUnited States
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University Hospital, ToursCompletedTuberous Sclerosis Complex | LymphangioleiomyomatosisFrance
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Rapamycin Holdings, Inc. dba Emtora BiosciencesLumaBridgeActive, not recruitingFamilial Adenomatous PolyposisUnited States
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Talaris Therapeutics Inc.Duke UniversityNo longer availableMetachromatic LeukodystrophyUnited States
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Stanford UniversityNational Institute of Neurological Disorders and Stroke (NINDS); Hugo W. Moser... and other collaboratorsCompletedX-linked AdrenoleukodystrophyUnited States
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bluebird bioCompletedCerebral Adrenoleukodystrophy (CALD)United States, Germany, Argentina, Australia, France, United Kingdom
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University of Puerto RicoNational Institutes of Health (NIH)CompletedFamilial Adenomatous PolyposisPuerto Rico
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Vanderbilt-Ingram Cancer CenterNational Cancer Institute (NCI)TerminatedFamilial Adenomatous Polyposis | Deep Fibromatosis/Desmoid TumorUnited States
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Shenzhen Geno-Immune Medical InstituteUnknown
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NeuroVia, Inc.WithdrawnX-Linked AdrenoleukodystrophyAustralia, Argentina, United Kingdom, Colombia, Chile, France, Russian Federation, Ukraine
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Academisch Medisch Centrum - Universiteit van Amsterdam...Completed
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Xinhua Hospital, Shanghai Jiao Tong University...UnknownLymphoma | Acute Myeloid Leukemia | Neuroblastoma | Retinoblastoma | Hepatoblastoma | Acute Lymphoid LeukemiaChina
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Rabin Medical CenterUnknown
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NYU Langone HealthWithdrawnEpilepsy | Tuberous Sclerosis | Dravet Syndrome | Focal Seizures | Lennox-Gastaut SyndromeUnited States
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Nantes University HospitalUniversité de NantesUnknownChronic Inflammatory Demyelinating Polyneuropathy | Anti-MAG Neuropathy | Charcot-Marie-Tooth Disease, Type IAFrance
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Masonic Cancer Center, University of MinnesotaWithdrawnCerebral Adrenoleukodystrophy
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National Cancer Institute (NCI)CompletedFamilial Adenomatous PolyposisUnited States, Puerto Rico
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Washington University School of MedicineCompletedNeurofibromatosis Type 1 | Pediatric Brain TumorUnited States
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The Cleveland ClinicOhio State University Comprehensive Cancer CenterCompletedFamilial Adenomatous PolyposisUnited States
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University Hospital, ToulouseCompleted
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FDA Office of Orphan Products DevelopmentHugo W. Moser Research Institute at Kennedy Krieger, Inc.Completed
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The University of Texas Health Science Center,...Society for Pediatric DermatologyCompletedTuberous Sclerosis | Neurofibromatoses | Neurofibroma | AngiofibromaUnited States
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Roswell Park Cancer InstituteCompletedLymphoma | Brain and Central Nervous System Tumors | Neuroblastoma | RetinoblastomaUnited States
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Skane University HospitalCompletedDiabetes Complications | Carpal Tunnel Syndrome | Peripheral Neuropathy | Entrapment NeuropathiesSweden
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Far Eastern Memorial HospitalNational Taiwan University Hospital; Fu Jen Catholic UniversityUnknownAdrenoleukodystrophyTaiwan
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National Institute of Allergy and Infectious Diseases...CompletedChronic Granulomatous Disease | Leukocyte Disorder | Job's Syndrome | Chediak Higashi SyndromeUnited States
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Radboud University Medical CenterDutch Cancer SocietyUnknownAdenomatous Polyposis ColiNetherlands
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National Institute of Neurological Disorders and...CompletedMuscle Rigidity | Spasm | Stiff Man SyndromeUnited States
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National Center for Research Resources (NCRR)Icahn School of Medicine at Mount SinaiCompletedMetabolism, Inborn Errors | Leukodystrophy, Globoid Cell | Tay-Sachs Disease | Porphyria, ErythropoieticUnited States
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Fairview University Medical CenterUnknownHemophagocytic Lymphohistiocytosis | Graft Versus Host Disease | Chediak-Higashi Syndrome | Virus-Associated Hemophagocytic Syndrome | X-Linked Lymphoproliferative Syndrome | Familial Erythrophagocytic LymphohistiocytosisUnited States
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bluebird bioCenter for International Blood and Marrow Transplant ResearchRecruitingCerebral Adrenoleukodystrophy (CALD)United States
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University Hospital, AntwerpKom Op Tegen Kanker; Stichting tegen KankerRecruitingEsophageal Cancer | Ovarian Cancer | Pancreas Cancer | Liver CancerBelgium
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National Tuberous Sclerosis AssociationRecruitingTuberous Sclerosis | LymphangioleiomyomatosisUnited States, Canada
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Brigham and Women's HospitalMassachusetts General HospitalRecruitingTuberous Sclerosis Complex | LymphangioleiomyomatosisUnited States
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Medical University of BialystokUniversity of BialystokRecruitingOptic Neuritis | Ischemic Optic Neuropathy | Traumatic Optic Neuropathy | Toxic Optic Neuropathy | Compressive Optic Neuropathy | Hereditary Optic NeuropathiesPoland
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Poxel SANot yet recruiting
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Zarife SahenkRecruitingCharcot-Marie-Tooth Disease | Peripheral Neuropathy | Chronic Inflammatory Demyelinating PolyneuropathyUnited States
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Academisch Medisch Centrum - Universiteit van Amsterdam...IRCCS Azienda Ospedaliero-Universitaria di Bologna; Hospital Clinic of Barcelona and other collaboratorsRecruitingFamilial Adenomatous PolyposisNetherlands
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George ZogopoulosRecruitingPancreatic Cancer | Bile Duct Cancer | Pancreas Cancer | Gallbladder Cancer | Pancreas Neoplasm | Familial Pancreatic Cancer | Duodenal Cancer | Hereditary Cancer | Pancreas Cyst | Ampullary Cancer | Pancreatic Precancerous ConditionCanada
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Masonic Cancer Center, University of MinnesotaRecruitingCerebral Adrenoleukodystrophy | Adrenoleukodystrophy | ALD (Adrenoleukodystrophy)United States
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National Cancer Institute (NCI)CompletedNeurofibromatosis | MPNSTUnited States
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National Cancer Institute (NCI)CompletedLeukemia | Solid Tumor | Sickle Cell Disease | NeurofibromatosisUnited States
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Cellaion SATerminatedUrea Cycle Disorder | Crigler-Najjar Syndrome | Acute on Chronic Liver FailureBelgium, Spain, France, Bulgaria, Poland
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SpringWorks Therapeutics, Inc.AvailableNeurofibromatosis Type 1-Associated Plexiform Neurofibromas | Histiocytic Neoplasm | Other MAP-K Pathway Driven Diseases
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Sarcoma Alliance for Research through CollaborationUnited States Department of Defense; AstraZenecaCompletedNeurofibromatosis 1 | Malignant Peripheral Nerve Sheath TumorsUnited States