- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Heterozygous Familial
Total 1176 results
-
Central South UniversityCompletedHomozygous Familial HypercholesterolemiaChina
-
CymaBay Therapeutics, Inc.CompletedHomozygous Familial HypercholesterolemiaCanada, France, Netherlands, Norway
-
Merck Sharp & Dohme LLCTerminatedHyperlipoproteinemia Type II | Homozygous Familial Hypercholesterolemia
-
First Affiliated Hospital Xi'an Jiaotong UniversityRecruitingHomozygous Familial HypercholesterolemiaChina
-
Beijing Suncadia Pharmaceuticals Co., LtdNot yet recruitingHomozygous Familial Hypercholesterolemia
-
Arrowhead PharmaceuticalsActive, not recruitingHomozygous Familial HypercholesterolemiaAustralia, Canada, United States, South Africa
-
AkesoAD Pharmaceuticals Co., Ltd.CompletedHomozygous Familial HypercholesterolemiaChina
-
Akcea TherapeuticsIonis Pharmaceuticals, Inc.TerminatedFamilial Partial LipodystrophyUnited States, Netherlands, Belgium, Brazil, Canada, Germany, Russian Federation
-
Regeneron PharmaceuticalsSanofiCompletedHomozygous Familial HypercholesterolemiaUnited States, South Africa, Canada, Greece, Japan, Ukraine, Austria, Czechia, France, Germany, Italy, Taiwan, Turkey
-
Regeneron PharmaceuticalsCompletedHomozygous Familial HypercholesterolemiaUnited States, Netherlands, Australia, Austria, Canada, France, Greece, Italy, Japan, South Africa, Ukraine
-
Aegerion Pharmaceuticals, Inc.WithdrawnHomozygous Familial Hypercholesterolemia
-
University Hospital, Basel, SwitzerlandCompletedHeterozygous HaemoglobinopathySwitzerland
-
University of PennsylvaniaCompletedHypercholesterolemia, Familial
-
Kastle Therapeutics, LLCIonis Pharmaceuticals, Inc.CompletedHypercholesterolemia, FamilialUnited States, Netherlands
-
AstraZenecaCompletedFamilial HypercholesterolaemiaUnited States, Netherlands, Norway, Canada, Belgium
-
Umeå UniversityCompleted
-
University of PennsylvaniaUniversity of Amsterdam; University of Cape Town; University of Witwatersrand...RecruitingHomozygous Familial HypercholesterolemiaUnited States, Netherlands, South Africa
-
LIB Therapeutics LLCCompletedHomozygous Familial HypercholesterolemiaUnited States, Israel, Norway, South Africa, Turkey, India
-
AstraZenecaCompletedHomozygous Familial Hypercholesterolemia (HoFH)Malaysia, Canada, Israel, Netherlands, Taiwan, Belgium, Denmark
-
Organon and CoCompletedPrimary Hypercholesterolemia | Homozygous Familial Hypercholesterolemia
-
HDL TherapeuticsMedStar Heart and Vascular InstituteUnknownHomozygous Familial Hypercholesterolemia | HoFHUnited States
-
Federal Research and Clinical Center of Physical-Chemical...Endocrinology Research Centre, MoscowCompletedObesity; FamilialRussian Federation
-
Centre Hospitalier Universitaire DijonCompletedLumbar Stenosis, FamilialFrance
-
Herzog HospitalJoint Distribution Committee (JDC)Unknown
-
Assistance Publique - Hôpitaux de ParisMinistry of Health, FranceCompletedHeterozygous Carriers of Gitelman SyndromeFrance
-
Amryt PharmaRecruitingHomozygous Familial HypercholesterolemiaItaly, United States, Argentina, Canada, France, Greece, Netherlands, United Kingdom
-
AmgenCompletedSevere Familial HypercholesterolemiaItaly, Czechia, United States, Israel, New Zealand, South Africa, France, Spain, Australia, Belgium, Canada, Netherlands, Hong Kong, Brazil, United Kingdom, Greece, Japan, Lebanon
-
Bristol-Myers SquibbTerminatedPrimary Familial Dilated CardiomyopathyUnited States, Germany, Spain, United Kingdom
-
Innovent Biologics (Suzhou) Co. Ltd.CompletedHomozygous Familial HypercholesterolemiaChina
-
Regeneron PharmaceuticalsCompletedHomozygous Familial HypercholesterolemiaUnited States, Australia, Austria, Netherlands, Taiwan, Ukraine
-
Novartis PharmaceuticalsCompletedA Study of Inclisiran in Participants With Homozygous Familial Hypercholesterolemia (HoFH) (ORION-5)Homozygous Familial HypercholesterolemiaHong Kong, Israel, Russian Federation, Serbia, South Africa, Taiwan, Turkey, Ukraine
-
Akcea TherapeuticsIonis Pharmaceuticals, Inc.WithdrawnHomozygous Familial HypercholesterolemiaCanada
-
AmgenCompletedHomozygous Familial HypercholesterolemiaNew Zealand, South Africa, France, United States, Spain, Belgium, Czechia, Italy, Netherlands, Hong Kong, Canada, Lebanon
-
Aegerion Pharmaceuticals, Inc.CompletedFamilial Hypercholesterolemia - HomozygousJapan
-
Aegerion Pharmaceuticals, Inc.FDA Office of Orphan Products DevelopmentCompletedHomozygous Familial HypercholesterolemiaUnited States, Canada, Italy, South Africa
-
National Eye Institute (NEI)CompletedEye Diseases | Exudatiaon | Avascular Retina | Retina Fold | Familial Exudative Vitreoretinopathy | FEVRCanada, United Kingdom
-
Laval UniversityCompletedHomozygous Familial HypercholesterolemiaCanada
-
Cerenis Therapeutics, SACompletedHomozygous Familial HypercholesterolemiaUnited States, Canada, Italy, Netherlands, United Kingdom
-
Aegerion Pharmaceuticals, Inc.University of Pennsylvania; Doris Duke Charitable FoundationCompletedHomozygous Familial HypercholesterolemiaUnited States
-
The University of Western AustraliaNational Health and Medical Research Council, AustraliaUnknownFamilial Hypercholesterolaemia | HypertriglyceridaemiaAustralia
-
VIVE - The Danish Center for Social Science ResearchKFUMs Sociale Arbejde; FDF; KFUM spejderneCompleted
-
GCS IHFB Cognacq-JayFondation de FranceCompletedBereaved FamiliesFrance
-
M.D. Anderson Cancer CenterRUNX1 FoundationRecruitingRUNX1 Familial Platelet DisorderUnited States
-
Catabasis PharmaceuticalsCompletedHypertriglyceridemia | Hyperlipoproteinemia Type I | Lipoprotein Lipase Deficiency, Familial | Chylomicronemia, FamilialCanada
-
National Institute of Diabetes and Digestive and...RecruitingLipodystrophyUnited States
-
Chinese Medical AssociationRecruitingAortic Dissection | Family Research | Aortic Dissection, Familial, With or Without Aortic AneurysmChina
-
Danish Headache CenterEUROHEADCompletedHealthy Volunteers | Familial Hemiplegic Migraine Type 1 and 2Denmark
-
PfizerCompletedTransthyretin Familial Amyloid Poluneuropathy
-
The Rogosin InstituteRecruitingHomozygous Familial HypercholesterolemiaUnited States
-
AstraZenecaCompletedHomozygous Familial Hypercholesterolemia (HoFH)Malaysia, Canada, Taiwan, Belgium, Denmark, Israel