- ICH GCP
- US Clinical Trials Registry
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Clinical Trials on Heterozygous Familial
Total 1171 results
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Gilead SciencesCompleted
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University of ChileUnknown
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Leiden University Medical CenterThe Dutch Brain Foundation (funding)Not yet recruitingCerebral Amyloid Angiopathy
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Kyowa Kirin, Inc.Kyowa Kirin Co., Ltd.CompletedX-linked HypophosphatemiaUnited States, Korea, Republic of, Japan, Ireland, United Kingdom, France, Italy
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Kyowa Kirin Pharmaceutical Development LtdCompletedX-linked HypophosphatemiaUnited Kingdom, France, Ireland, Italy
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NYU Langone HealthCompletedAnxiety Disorders | Familial Dysautonomia | Dysthymia | Paroxysmal Hypertension | Autosomal Recessive DiseaseUnited States
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Kyowa Hakko Kirin Pharma, Inc.Completed
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Universidade do PortoCentro Hospitalar Universitário São João, E.P.E. (CHUSJ); Centro de Investigação... and other collaboratorsRecruitingCarpal Tunnel Syndrome | Transthyretin AmyloidosisPortugal
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Assistance Publique - Hôpitaux de ParisRecruitingX-linked HypophosphatemiaFrance
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National Human Genome Research Institute (NHGRI)Merck Sharp & Dohme LLC; Duke University; University of Massachusetts, WorcesterRecruitingFever | Genetic Diseases | Familial Mediterranean Fever (FMF) | Autoinflammation | Periodic Fever | ROSAH | ALPK1United States
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Wuerzburg University HospitalKyowa Kirin, Inc.Completed
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Hospices Civils de LyonCompleted
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Kyowa Hakko Kirin Pharma, Inc.Kyowa Kirin Co., Ltd.CompletedX-linked HypophosphatemiaUnited States, Canada
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Peking Union Medical College HospitalUnknownX-linked HypophosphatemiaChina
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University of AarhusAarhus University Hospital; University of East Anglia; Kolding SygehusCompleted
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Zeria PharmaceuticalCompletedPrimary Hypophosphatemic RicketsJapan
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Bandim Health ProjectOdense University Hospital; Odense Patient Data Explorative Network; Municipality...CompletedCovid19 | Immunosenescence | Vaccine Preventable Disease | Morbidity | Non-specific Effects of Vaccines | Heterologous ImmunityDenmark
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NorthShore University HealthSystemNational Cancer Institute (NCI); Wake Forest University Health Sciences; Van... and other collaboratorsCompletedProstate Cancer | Prostate Cancer, Familial | Hereditary Prostate Cancer
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Washington University School of MedicineEli Lilly and Company; Hoffmann-La Roche; Avid Radiopharmaceuticals; National Institute... and other collaboratorsCompletedDementia | Alzheimers Disease | Alzheimers Disease, FamilialUnited States, Canada, France, Spain, Ireland, Australia, Puerto Rico, United Kingdom
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Vanderbilt University Medical CenterCompletedHealthy | Pulmonary Arterial HypertensionUnited States
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University Medicine GreifswaldOMT GmbH & Co. KGUnknownPulmonary Arterial Hypertension | PAHGermany
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Washington University School of MedicineEli Lilly and Company; Hoffmann-La Roche; Avid Radiopharmaceuticals; National Institute... and other collaboratorsRecruitingDementia | Alzheimers Disease | Alzheimers Disease, FamilialUnited States, Canada, Italy, Argentina, Australia, Colombia, France, Ireland, Mexico, Netherlands, Puerto Rico, Spain, United Kingdom, Brazil, Japan, Germany
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Washington University School of MedicineHoffmann-La Roche; National Institute on Aging (NIA); Alzheimer's AssociationTerminatedDementia | Alzheimers Disease | Alzheimers Disease, FamilialUnited States, France, Spain, Ireland, Canada, Australia, Puerto Rico, United Kingdom
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Mayo ClinicNational Cancer Institute (NCI)Active, not recruiting
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Keros Therapeutics, Inc.RecruitingPulmonary Arterial HypertensionUnited States, Australia
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University of Kansas Medical CenterAmerican Heart AssociationRecruitingPulmonary Arterial HypertensionUnited States
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Nanjing First Hospital, Nanjing Medical UniversityTianjin Medical University General HospitalRecruitingPulmonary Arterial HypertensionChina
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University of Texas Southwestern Medical CenterRecruitingPulmonary Arterial HypertensionUnited States
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Laval UniversityCanadian Institutes of Health Research (CIHR); Resverlogix CorpNot yet recruiting
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ActelionRecruitingPulmonary Arterial HypertensionBelgium, United States, Italy, Canada, Taiwan, Greece, China, Korea, Republic of, Germany, Israel, Austria, Russian Federation, Australia, Thailand, United Kingdom, Brazil, Malaysia, Spain, Ukraine, Bulgaria, Colombia, Mexico, Turkey, Vietna... and more
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Novartis PharmaceuticalsCompletedPulmonary Arterial HypertensionSpain, Germany, Poland, United Kingdom, Netherlands, Argentina, United States
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Novartis PharmaceuticalsCompletedPulmonary Arterial HypertensionUnited States, Spain, Germany, Poland, United Kingdom, Netherlands, Argentina
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University of PittsburghBoston University; National Heart, Lung, and Blood Institute (NHLBI); Northeastern...CompletedPathologic Processes | Heart Diseases | Atrial Fibrillation | Arrhythmia, Cardiac | Familial Atrial FibrillationUnited States
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Janssen-Cilag S.p.A.CompletedPulmonary Arterial HypertensionItaly
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Merck Sharp & Dohme LLCActive, not recruitingPulmonary Arterial HypertensionJapan
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United TherapeuticsCompletedPulmonary Arterial Hypertension
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United TherapeuticsCompletedPulmonary Arterial HypertensionUnited States
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ActelionCompletedPulmonary Arterial HypertensionUnited States, Poland, Ukraine, United Kingdom, China, Germany, Taiwan, France, Spain, Switzerland, Argentina, Belarus, Belgium, Colombia, Israel, India, Malaysia, Romania, Serbia, Canada, Australia, Netherlands, Denmark, Greece, Korea,... and more
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Acceleron Pharma Inc. (a wholly owned subsidiary...CompletedPulmonary Arterial HypertensionSpain, United States, Israel, Australia, Germany, United Kingdom, France, Brazil
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Eiger BioPharmaceuticalsTerminatedPulmonary Arterial HypertensionUnited States, Canada
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Vigonvita Life SciencesShanghai Institute of Materia Medica, Chinese Academy of SciencesCompletedPulmonary Arterial HypertensionChina
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United TherapeuticsCompletedAn Open-Label, Long-Term Study of Oral Treprostinil in Subjects With Pulmonary Arterial HypertensionPulmonary Arterial HypertensionKorea, Republic of, United States, Australia, Austria, Taiwan, China, Israel, Canada, India, Germany, Singapore, United Kingdom, Brazil, Italy, Netherlands, Argentina, Sweden, Chile, Denmark, France, Greece, Mexico, Poland
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Steeve ProvencherResverlogix CorpCompletedPulmonary Arterial HypertensionCanada
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United TherapeuticsCompletedPulmonary Arterial HypertensionUnited States, Canada, India, United Kingdom, Spain, Israel, Australia, Belgium, France, Austria, China, Germany, Ireland, Italy, Mexico, Netherlands, Poland, Portugal, Puerto Rico, Sweden
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Pfizer's Upjohn has merged with Mylan to form Viatris...TerminatedPulmonary Arterial HypertensionItaly, United Kingdom, United States, Belgium, Brazil, China, Bulgaria, Greece, India, Latvia, Malaysia, Netherlands, Philippines, Poland, Romania, Russian Federation, Thailand
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RenJi HospitalUnknownPulmonary Arterial HypertensionChina
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University of Texas Southwestern Medical CenterNational Center for Research Resources (NCRR)CompletedPulmonary Arterial HypertensionUnited States
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Altavant Sciences GmbHPPD; Altavant Sciences, Inc.TerminatedPulmonary Arterial HypertensionUnited States, Canada
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United TherapeuticsCompletedPulmonary Arterial HypertensionKorea, Republic of, United States, Australia, Austria, Taiwan, China, Israel, Canada, India, Germany, Singapore, United Kingdom, Brazil, Italy, Netherlands, Argentina, Sweden, Chile, Denmark, France, Greece, Mexico, Poland
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ActelionTerminated