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Clinical Trials on Homozygous αº-thalassemia in United Kingdom
Total 218 results
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DisperSol Technologies, LLCCompletedThalassemia MajorThailand, United States
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HealthCore-NERINational Heart, Lung, and Blood Institute (NHLBI)CompletedThalassemiaUnited States, Canada
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Emory UniversityPatient-Centered Outcomes Research InstituteCompletedSickle Cell Disease | Sickle Cell Anemia | Hemoglobin SC | Hemoglobin SS | Hemoglobin Beta ThalassemiaUnited States
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Novartis PharmaceuticalsActive, not recruitingFamilial Hypercholesterolemia - HomozygousGreece, Lebanon, Turkey, France, Canada, Malaysia, Netherlands, United States
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Dana-Farber Cancer InstituteTehran University of Medical SciencesCompletedThalassemia MajorUnited States, Iran, Islamic Republic of
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HealthCore-NERINational Heart, Lung, and Blood Institute (NHLBI)TerminatedHeart Diseases | Cardiovascular Diseases | Beta-ThalassemiaUnited States
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Novartis PharmaceuticalsCompletedBeta-ThalassemiaUnited States
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Novartis PharmaceuticalsCompletedAnemia | HemosiderosisUnited States, Germany, Belgium, United Kingdom, Italy, Canada, France
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National Heart, Lung, and Blood Institute (NHLBI)CompletedHematologic Diseases | Anemia, Sickle Cell | Beta-Thalassemia | Hematopoietic Stem Cell TransplantationUnited States, Canada
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UCSF Benioff Children's Hospital OaklandNovartis PharmaceuticalsCompletedTHALASSEMIA MAJORUnited States
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Sideris PharmaceuticalsTerminatedIron Overload | Beta-ThalassemiaUnited States, Canada, Lebanon, Thailand, Turkey
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Children's Hospital of PhiladelphiaAnn & Robert H Lurie Children's Hospital of Chicago; The Cooley's Anemia Foundation...CompletedThalassemia Major With Severe Transfusional Iron OverloadUnited States
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National Heart, Lung, and Blood Institute (NHLBI)Not yet recruitingSickle Cell Disease | Sickle Cell Disorders | Hb-SS Disease | Hemoglobin S | Disease Sickle Cell Anemia | Hemoglobin Beta Thalassemia DiseaseUnited States
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FerroKin BioSciences, Inc.CompletedBeta-thalassemia | Transfusional Iron OverloadUnited States, Australia, Thailand
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Wake Forest University Health SciencesCompletedHemianopia, Homonymous | Hemianopsia, HomonymousUnited States
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Georgetown UniversityOregon Health and Science University; Tesaro, Inc.TerminatedHomologous Recombination Deficiency | Solid Tumor, AdultUnited States
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Timothy OlsonActive, not recruitingSickle Cell Disease | Thalassemia MajorUnited States
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National Heart, Lung, and Blood Institute (NHLBI)RecruitingSickle Cell Anemia | Beta ThalassemiaUnited States
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Columbia UniversityActive, not recruitingSickle Cell Disease | Beta ThalassemiaUnited States
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National Institute of Allergy and Infectious Diseases...TerminatedAnemia, Sickle Cell | Hemoglobinopathies | Thalassemia | Hemoglobin SC Disease | Thalassemia MajorUnited States
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National Institute of Allergy and Infectious Diseases...RecruitingMalaria | Sickle Cell Disease | Alpha and Beta Thalassemia | Human PhysiologyUnited States
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ShireTerminatedBeta-Thalassemia | Transfusional Iron OverloadUnited States, Lebanon, Canada, Italy, Turkey
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Cerenis Therapeutics, SACompletedHomozygous Familial HypercholesterolemiaUnited States, Canada, Italy, Netherlands, United Kingdom
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Agios Pharmaceuticals, Inc.Active, not recruitingThalassemiaUnited States, Canada, United Kingdom
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Memorial Sloan Kettering Cancer CenterRecruitingSickle Cell Disease | Thalassemia | Thalassemia, BetaUnited States
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West Cancer CenterRecruitingHomologous Recombination Deficient Solid TumorsUnited States
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Novartis PharmaceuticalsCompletedNon-transfusion Dependent ThalassemiaGreece, Taiwan, Italy, United Kingdom, Lebanon, Turkey, Malaysia, Thailand, United States
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REGENXBIO Inc.National Heart, Lung, and Blood Institute (NHLBI)TerminatedHomozygous Familial Hypercholesterolemia (HoFH)United States, Canada, Italy, Netherlands
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Paul SzabolcsRecruitingSickle Cell Anemia | Diamond-blackfan Anemia | Beta-thalassemia MajorUnited States
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Alexandra BowersNational Eye Institute (NEI); Chadwick Optical Inc.CompletedHomonymous HemianopiaUnited States, United Kingdom
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National Heart, Lung, and Blood Institute (NHLBI)National Institutes of Health Clinical Center (CC); National Cancer Institute...RecruitingStem Cell Transplantation | Sickle Cell Disease | Thalassemia | Graft vs Host DiseaseUnited States
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Sangamo TherapeuticsEnrolling by invitationBlood and Lymphatic DiseasesUnited States
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Ann & Robert H Lurie Children's Hospital of ChicagoNational Heart, Lung, and Blood Institute (NHLBI)RecruitingSickle Cell Disease | Sickle B+ Thalassemia | Sickle Beta Zero Thalassemia | Sickle Cell Hemoglobin CUnited States
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Ann & Robert H Lurie Children's Hospital of ChicagoCompletedSickle Cell Disease | Sickle B+ Thalassemia | Sickle Beta Zero Thalassemia | Sickle Cell Hemoglobin CUnited States
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CelgeneRecruitingBeta-thalassemia | Myelodysplastic Syndromes (MDS) | Myeloproliferative Neoplasm(MPN)-Associated MyelofibrosisUnited States, Japan, Israel, United Kingdom, Turkey, Greece, France, Australia, Belgium, Bulgaria, Canada, Germany, Italy, Malaysia, Spain, Sweden, Taiwan, Thailand, Tunisia, China, Lebanon, Netherlands
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Fairview University Medical CenterCompletedNeutropenia | Sickle Cell Anemia | Red-Cell Aplasia, Pure | Thalassemia MajorUnited States
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Ann & Robert H Lurie Children's Hospital of ChicagoCompletedSickle Cell Disease | Sickle B+ Thalassemia | Sickle Beta Zero Thalassemia | Sickle Cell Hemoglobin CUnited States
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Ann & Robert H Lurie Children's Hospital of ChicagoNational Heart, Lung, and Blood Institute (NHLBI)Active, not recruitingSickle Cell Disease | Sickle B+ Thalassemia | Sickle Beta Zero Thalassemia | Sickle Cell Hemoglobin CUnited States
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National Heart, Lung, and Blood Institute (NHLBI)CompletedHomozygous Familial HypercholesterolemicUnited States
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Catherine BollardChildren's National Research InstituteActive, not recruitingThalassemia | Sickle Cell-thalassemia DiseaseUnited States
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HealthCore-NERINational Heart, Lung, and Blood Institute (NHLBI); Thalassemia Clinical Research...CompletedHematologic Diseases | Iron Overload | Hypertension, Pulmonary | Osteoporosis | Thalassemia | Beta-Thalassemia | Anemia, Cooley'sUnited States, Canada
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Boston Children's HospitalNovartisCompletedSickle Cell Disease | Thalassemia Major | Transfusion-dependent HemachromatosisUnited States
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Massachusetts Eye and Ear InfirmaryNational Eye Institute (NEI)RecruitingHemianopia, Homonymous | Tunnel Vision | Visual Field Defect, Peripheral | Visual Field Constriction Bilateral | Visual Field Defect Homonymous BilateralUnited States
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Massachusetts Eye and Ear InfirmaryNational Eye Institute (NEI)RecruitingTunnel Vision | Visual Field Defect, Peripheral | Visual Field Constriction Bilateral | Visual Field Defect Homonymous Bilateral | Hemianopsia | Homonymous HemianopiaUnited States
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Terumo BCTbioUnited States Department of Defense; U.S. Army Medical Research and Development... and other collaboratorsTerminatedTransfusion Dependent ThalassemiaUnited States, Israel, Italy, Turkey
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University of Texas Southwestern Medical CenterWithdrawn
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Vanderbilt University Medical CenterWashington University School of Medicine; University of Alabama at BirminghamRecruitingStroke | Sickle Cell Disease | Anemia, Sickle Cell | Sickle Cell Thalassemia | Sickle Cell-Beta0-ThalassemiaUnited States
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CelgeneAcceleron Pharma, Inc., a wholly-owned subsidiary of Merck & Co., Inc., Rahway...CompletedThalassemiaUnited States, Greece, Italy, Lebanon, Thailand, United Kingdom
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Washington University School of MedicineHealthCore-NERI; Pediatric Blood and Marrow Transplant ConsortiumCompletedSevere ThalassemiaUnited States
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Invenux, LLCState University of New York - Downstate Medical CenterActive, not recruitingSickle Cell Disease | Sickle-Beta Zero ThalassemiaUnited States