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Clinical Trials on Hurler Syndrome (MPS I)
Total 799 results
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Cornell UniversityLaidlaw Foundation; Epperson Fund; Beck Fellowship; Dan Cane FundCompletedPolycystic Ovary Syndrome | Ovarian Cysts | PCOS | Dysmenorrhea | Menstrual Pain | Premenstrual Dysphoric Disorder | Premenstrual Syndrome | Period Pain | Menstrual Problem | PMS | Menstrual Discomfort | Dysmenorrhea Primary | Cramps | Menstrual Cycle Abnormal | PCOS (Polycystic Ovary Syndrome) of Bilateral Ovaries | Period... and other conditionsUnited States
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National Heart, Lung, and Blood Institute (NHLBI)CompletedAcute Lymphoblastic Leukemia | Chronic Myelogenous Leukemia | Myelodysplastic Syndrome (MDS) | CLL (Chronic Lymphocytic Leukemia) | CML (Chronic Myelogenous LeukemiaUnited States
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Charite University, Berlin, GermanyRecruitingMultiple Sclerosis (MS) | Clinically Isolated Syndrome (CIS)Germany
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TakedaRecruitingHunter SyndromeCanada, France
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National Human Genome Research Institute (NHGRI)TerminatedPulmonary Fibrosis | Metabolic Disease | Oculocutaneous Albinism | Hermansky-Pudlak Syndrome (HPS) | Platelet Storage Pool DeficiencyUnited States
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GRIN Therapeutics, Inc.RecruitingTuberous Sclerosis Complex | Focal Cortical DysplasiaSpain, United Kingdom, Australia, Belgium, Canada, Italy, Poland
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NobelpharmaCompletedPlaque | Tuberous Sclerosis | Angiofibroma | Hypomelanotic MaculeJapan
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Dermatology Specialties Limited PartnershipCompletedTuberous Sclerosis | Facial AngiofibromaUnited States, Taiwan, Serbia, Spain, Australia, Czechia, Hungary, New Zealand, Slovakia
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National Cancer Institute (NCI)CompletedPlexiform Neurofibroma | Neurofibromatosis Type IUnited States
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NobelpharmaCompletedPlaque | Tuberous Sclerosis | Angiofibroma | Hypomelanotic MaculeJapan
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Le Bonheur Children's HospitalPfizer; University of Tennessee Health Science CenterCompleted
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Fundacio PuigvertMinistry of Health, SpainCompleted
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Children's Oncology GroupNational Cancer Institute (NCI)Active, not recruitingStage I Kidney Wilms Tumor | Stage II Kidney Wilms Tumor | Stage III Kidney Wilms Tumor | Stage IV Kidney Wilms Tumor | Adult Kidney Wilms Tumor | Beckwith-Wiedemann Syndrome | Childhood Kidney Wilms Tumor | Diffuse Hyperplastic Perilobar Nephroblastomatosis | Rhabdoid Tumor of the Kidney | Stage V Kidney...United States, Canada, Australia, New Zealand, Puerto Rico, Israel
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RTI InternationalEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsEnrolling by invitationPrimary Hyperoxaluria Type 3 | Diabetes Mellitus | Hemophilia A | Hemophilia B | Hereditary Fructose Intolerance | Cystic Fibrosis | Factor VII Deficiency | Phenylketonurias | Sickle Cell Disease | Dravet Syndrome | Duchenne Muscular Dystrophy | Prader-Willi Syndrome | Fragile X Syndrome | Chronic Granulomatous Disease and other conditionsUnited States
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Azienda Ospedaliero-Universitaria di ModenaRecruitingTurner Syndrome | Anomaly HeartItaly
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University of Colorado, DenverRecruitingTurner SyndromeUnited States
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Central Hospital, Nancy, FranceCompletedTurner SyndromeFrance
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Assistance Publique - Hôpitaux de ParisInstitut National de la Santé Et de la Recherche Médicale, FranceEnrolling by invitationPrimary Ovarian Insufficiency | Turner SyndromeFrance
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ShireCompletedHunter SyndromeSpain, United States, Canada, United Kingdom, France, Australia, Mexico
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Novo Nordisk A/SRecruitingTurner Syndrome | Noonan Syndrome | SGA | ISSKorea, Republic of, Malaysia, Netherlands, Spain, United States, Poland
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Gynecologic Oncology GroupNational Cancer Institute (NCI)Not yet recruitingLynch Syndrome | Recurrent Uterine Corpus Carcinoma | Stage I Uterine Corpus Cancer | Stage II Uterine Corpus Cancer | Stage III Uterine Corpus Cancer | Stage IV Uterine Corpus CancerUnited States
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Assistance Publique - Hôpitaux de ParisNot yet recruiting
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National Institute of Diabetes and Digestive and...RecruitingCystic Fibrosis | Turner Syndrome | Congenital Hepatic Fibrosis | Immunologic Deficiency Syndrome | Idiopathic Non-Cirrhotic Portal HypertensionUnited States
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Maastricht University Medical CenterEnrolling by invitationTuberous Sclerosis | Basal Cell Nevus Syndrome | Cutis Laxa | Epidermolysis Bullosa | Ichthyosis | Ectodermal Dysplasia | Albinism | Xeroderma Pigmentosum | Birt-Hogg-Dube Syndrome | Palmoplantar KeratosesNetherlands
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National Institute of Neurological Disorders and...CompletedMultiple Sclerosis | Vasculitis | Tropical Spastic Paraparesis | HTLV-I Infection | Herpesviridae InfectionUnited States
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University Hospital, Strasbourg, FranceRecruiting
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The University of Texas Health Science Center,...American Heart AssociationRecruiting
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Ascendis Pharma Endocrinology Division A/SActive, not recruitingTurner SyndromeUnited States
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Sohag UniversityCompletedTurner SyndromeEgypt
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Nemours Children's ClinicGenentech, Inc.CompletedHypogonadism | Turner Syndrome | Premature Ovarian FailureUnited States, Chile
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Maastricht University Medical CenterRecruitingQuality of Life | Tuberous Sclerosis | Basal Cell Nevus Syndrome | Cutis Laxa | Epidermolysis Bullosa | Ichthyosis | Ectodermal Dysplasia | Albinism | Birt-Hogg-Dube Syndrome | Palmoplantar KeratosesNetherlands
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dr. Laura C. G. de Graaff-HerderNot yet recruitingCongenital Adrenal Hyperplasia | Hypogonadotropic Hypogonadism | Growth Hormone Deficiency | Turner Syndrome | Addison's Disease | Klinefelter Syndrome | Combined Pituitary Hormone Deficiency | Androgen Insensitivity Syndrome | Thyroid DysgenesisSpain, United Kingdom, Belgium, Netherlands
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Benovus Bio, Inc.UnknownMyelodysplastic Syndrome (MDS) | Acute Myelogenous Leukemia (AML) | Multiple Myeloma (MM) | Smoldering Multiple Myeloma (sMM)United States
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ShireCompletedHunter SyndromeUnited States, United Kingdom, Canada
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Ferring PharmaceuticalsCompletedTurner's Syndrome | Human Growth Hormone DeficiencyFrance
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Radboud University Medical CenterActive, not recruitingTurner Syndrome | Premature Ovarian Failure | Fertility Preservation | Live Birth | Ovarian Tissue CryopreservationNetherlands
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Nemours Children's ClinicEli Lilly and CompanyCompletedHypogonadism | Turner Syndrome | Premature Ovarian FailureUnited States
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University Hospital, BrestRecruiting
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Universitair Ziekenhuis BrusselUnknownSleep DisorderBelgium
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National Cancer Institute (NCI)CompletedParents of Children With Cancer | Parents of Children With NF1 | Parents of Children With Neurofibromatosis Type IUnited States, Canada
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University Hospital, BordeauxCompletedTuberous Sclerosis | Renal AngiomyolipomasFrance
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Taipei Medical University WanFang HospitalCompletedAortic Dissection | Pulmonary Thromboembolism | May-Thurner Syndrome | Thrombosis in Left Atrium and Right Axillary Artery | Double IVCTaiwan
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Dana-Farber Cancer InstituteNational Cancer Institute (NCI); Wyeth is now a wholly owned subsidiary of... and other collaboratorsCompletedTuberous Sclerosis | Nonmalignant Neoplasm | Lymphangioleimyomatosis | Kidney AngiomyolipomaUnited States
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Wake Forest University Health SciencesNational Cancer Institute (NCI)CompletedUnspecified Childhood Solid Tumor, Protocol Specific | Primary Myelofibrosis | Polycythemia Vera | Essential Thrombocythemia | Stage I Multiple Myeloma | Stage II Multiple Myeloma | Stage III Multiple Myeloma | Chronic Myelomonocytic Leukemia | Juvenile Myelomonocytic Leukemia | Burkitt Lymphoma | Secondary... and other conditionsUnited States
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City of Hope Medical CenterNational Cancer Institute (NCI)CompletedPrimary Myelofibrosis | Polycythemia Vera | Essential Thrombocythemia | Stage I Multiple Myeloma | Stage II Multiple Myeloma | Stage III Multiple Myeloma | Chronic Myelomonocytic Leukemia | Recurrent Adult Acute Myeloid Leukemia | Extranodal Marginal Zone B-cell Lymphoma of Mucosa-associated Lymphoid... and other conditionsUnited States
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Centre Hospitalier Universitaire de LiegeSanofi; Takeda; University of Liege; Orchard Therapeutics; Centre Hospitalier Régional... and other collaboratorsRecruitingCongenital Adrenal Hyperplasia | Hemophilia A | Hemophilia B | Mucopolysaccharidosis I | Mucopolysaccharidosis II | Cystic Fibrosis | Alpha 1-Antitrypsin Deficiency | Sickle Cell Disease | Fanconi Anemia | Chronic Granulomatous Disease | Wilson Disease | Severe Congenital Neutropenia | Ornithine Transcarbamylase... and other conditionsBelgium
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Ohio State University Comprehensive Cancer CenterCompletedCrohn Disease | Familial Adenomatous Polyposis | Stage IIIA Colon Cancer | Stage IIIB Colon Cancer | Stage IIIC Colon Cancer | Recurrent Colon Cancer | Stage I Colon Cancer | Stage IIA Colon Cancer | Stage IIB Colon Cancer | Stage IIC Colon Cancer | Adenomatous Polyp | Hereditary Intestinal Polyposis SyndromeUnited States
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University of AarhusAarhus University HospitalRecruitingCardiovascular Diseases | Turner Syndrome | Metabolic Disease | Klinefelter Syndrome | Immunologic Disease | Sex Chromosome AbnormalityDenmark
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University of AarhusCompletedMarfan Syndrome | Bicuspid Aortic Valve | Turner SyndromeDenmark
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Novartis PharmaceuticalsRecruiting