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Clinical Trials on Hurler Syndrome (MPS I)
Total 799 results
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Rush University Medical CenterEmory UniversityEnrolling by invitationTuberous Sclerosis | Fragile X Syndrome | Rett Syndrome | Hamartoma Syndrome, Multiple | Angelman Syndrome | Creatine Deficiency, X-linked | Telomeric 22Q13 Monosomy Syndrome | Chromosome 15Q, Partial DeletionUnited States
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National Heart, Lung, and Blood Institute (NHLBI)CompletedHIV Infections | Acquired Immunodeficiency Syndrome | Retroviridae Infections | Blood Transfusion | HIV-1 | Blood Donors | HIV-2 | HTLV-I | HTLV-II
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National Institute of Mental Health (NIMH)CompletedDepression | Healthy | Premenstrual Syndrome | PMSUnited States
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St. Jude Children's Research HospitalCookies for Kids' CancerTerminatedAcute Myeloid Leukemia (AML) | Myelodysplastic Syndrome (MDS)United States
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BioMarin PharmaceuticalTerminatedMorquio A Syndrome | MPS IV A | Mucopolysaccharidosis IVAUnited Kingdom
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Charlotte Niemeyer, MDCompletedMyelodysplastic Syndrome (MDS) | Refractory Cytopenia of Childhood | Hematopoietic Stem Cell Transplantation (SCT) | Reduced Intensity Conditioning (RIC)Germany
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Hospices Civils de LyonCompletedFamilial Chylomicronemia Syndrome | Multifactorial Chylomicronemia SyndromeFrance
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Novartis PharmaceuticalsCompletedFamilial Chylomicronemia Syndrome (FCS)South Africa, Spain, France, Germany, United Kingdom, United States, Canada, Netherlands
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New French Society of AtherosclerosisAkcea TherapeuticsCompletedFamilial Chylomicronemia Syndrome | Multifactorial Chylomicronemia SyndromeFrance
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MP Biomedicals, LLCMP Biomedicals Asia Pacific Pte. Ltd.CompletedHTLV-I Infections | HTLV-II Infections | Human T-lymphotropic Virus 1 | Human T-lymphotropic Virus 2 | HTLV I Associated T Cell Leukemia Lymphoma | HTLV I Associated MyelopathiesUnited States
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BioMarin PharmaceuticalCompletedMorquio A Syndrome | MPS IVA | Mucopolysaccharidosis IVATaiwan, United States, Italy, United Kingdom
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Otsuka Pharmaceutical Development & Commercialization...TerminatedSchizophrenia | Schizoaffective Disorder | Metabolic Syndrome | Bipolar I DisorderCanada
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MP Biomedicals, LLCMP Biomedicals Asia Pacific Pte. Ltd.CompletedHTLV-I Infections | HTLV-II Infections | Human T-lymphotropic Virus 1 | Human T-lymphotropic Virus 2 | HTLV I Associated T Cell Leukemia Lymphoma | HTLV I Associated MyelopathiesUnited States
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MP Biomedicals, LLCVital Systems Inc.UnknownHTLV-I Infections | HTLV-II Infections | Human T-lymphotropic Virus 1 | Human T-lymphotropic Virus 2 | HTLV I Associated T Cell Leukemia Lymphoma | HTLV I Associated MyelopathiesUnited States
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Novartis PharmaceuticalsCompletedCryopyrin-associated Periodic Syndromes (CAPS) | Familial Cold Autoinflam Syn (FCAS) | Muckle-wells Syn (MWS) | Neonatal Onset Multisystem Inflam Disease (NOMID)Switzerland, United States, Germany, Norway, Austria
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Millennium Pain CenterCompleted
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Targazyme, Inc.UnknownLymphoma | Leukemia | Hodgkin's Lymphoma | Transplantation Infection | Myelodysplastic Syndrome (MDS) | Non-Hodgkin's Lymphoma (NHL) | Blood And Marrow TransplantationUnited States
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BioMarin PharmaceuticalTerminatedMorquio A Syndrome | MPS IVA | Mucopolysaccharidosis IVAUnited States, United Kingdom, Canada, Germany
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Memorial Sloan Kettering Cancer CenterRecruitingNon-Hodgkin's Lymphoma | Myelodysplastic Syndromes (MDS) | Acute Lymphoblastic Leukemia (ALL) | Myeloproliferative Disorder | Acute Myelogenous Leukemia (AML) | Chronic Myelogenous Leukemia (CML)United States
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medac GmbHSyneos Health; CelerionCompletedMyelodysplastic Syndromes (MDS) | Acute Lymphoblastic Leukaemias (ALL) | Acute Myeloid Leukaemias (AML) | Juvenile Myelomonocytic Leukaemias (JMML)Germany, United Kingdom, Italy, Austria, Czechia, Poland
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Your Super, INC.CitruslabsCompletedMenstrual Pain | PMS | Menstrual DiscomfortUnited States
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ViiV HealthcareGlaxoSmithKlineCompletedInfection, Human Immunodeficiency Virus I
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Vancouver Infectious Diseases CentreUnknownDrug Use | Human Immunodeficiency Virus I InfectionCanada
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Université Catholique de LouvainCliniques universitaires Saint-Luc- Université Catholique de LouvainCompletedHuman Immunodeficiency Virus I InfectionBelgium
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ViiV HealthcareGlaxoSmithKline; ShionogiCompletedInfection, Human Immunodeficiency Virus IGermany, Spain, France, Australia, United States, Canada, United Kingdom, Italy, Russian Federation
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ViiV HealthcareGlaxoSmithKlineCompletedInfection, Human Immunodeficiency Virus IUnited States, Puerto Rico
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ViiV HealthcareGlaxoSmithKlineWithdrawnInfection, Human Immunodeficiency Virus IUnited States
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Nova Southeastern UniversityNational Institute of Mental Health (NIMH)CompletedHuman Immunodeficiency Virus I InfectionUnited States
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Hospices Civils de LyonTerminatedSelection of Farnesoid X Receptor (FXR) Ligands on the Reactivation of Latent HIV Proviruses (FXR#2)Human Immunodeficiency Virus I InfectionFrance
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Fred Hutchinson Cancer CenterUniversity of WashingtonCompleted
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GlaxoSmithKlineCompletedInfection, Human Immunodeficiency Virus I
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Vir Biotechnology, Inc.Bill and Melinda Gates FoundationCompletedHIV I InfectionUnited States
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ViiV HealthcareGlaxoSmithKlineTerminatedInfection, Human Immunodeficiency Virus IUnited States, Canada, Puerto Rico
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ViiV HealthcareGlaxoSmithKlineCompleted
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ViiV HealthcareGlaxoSmithKline; ShionogiCompletedInfection, Human Immunodeficiency Virus IUnited States, Spain, Germany, Australia, Canada, Belgium, Denmark, Netherlands, United Kingdom, France, Italy, Romania
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ViiV HealthcareGlaxoSmithKlineCompletedInfection, Human Immunodeficiency Virus IUnited States, Spain, Canada, Russian Federation, Romania, Belgium, South Africa
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Groupe Francophone des MyelodysplasiesAstex Pharmaceuticals, Inc.Completed
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National Cancer Institute (NCI)Completed
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National Cancer Institute (NCI)TerminatedRecurrent Cutaneous T-cell Non-Hodgkin Lymphoma | Recurrent Mycosis Fungoides/Sezary Syndrome | Stage III Cutaneous T-cell Non-Hodgkin Lymphoma | Stage III Mycosis Fungoides/Sezary Syndrome | Stage IV Cutaneous T-cell Non-Hodgkin Lymphoma | Stage IV Mycosis Fungoides/Sezary Syndrome | Stage I... and other conditionsUnited States
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Joanne Kurtzberg, MDAldagenCompletedAnemia, Aplastic | MDS | Inborn Errors of Metabolism | Congenital Marrow Failure | Congenital Immunodeficiency SyndromeUnited States
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St. Jude Children's Research HospitalKaryopharm Therapeutics IncCompletedAcute Myeloid Leukemia (AML) | Acute Lymphoblastic Leukemia (ALL) | Myelodysplastic Syndrome (MDS) | Mixed Phenotype Acute Leukemia (MPAL)United States
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BioMarin PharmaceuticalTerminatedMorquio A Syndrome | MPS IVA | Mucopolysaccharidosis IVAUnited Kingdom, United States, Germany
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Masonic Cancer Center, University of MinnesotaCompletedLymphoma | Chronic Lymphocytic Leukemia (CLL) | Myelodysplastic Syndromes (MDS) | Myeloma | Acute Lymphoblastic Leukemia (ALL) | Acute Myelogenous Leukemia (AML) | Chronic Myelogenous Leukemia (CML)United States
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GeNeuro Innovation SASCompletedMultiple Sclerosis (MS) | Clinically Isolated Syndrome (CIS) | Secondary Progressive MS | Primary Progressive MS | Relapsing-Remitting MSFrance, Spain, Switzerland
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Ferring PharmaceuticalsTerminated
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Merck KGaA, Darmstadt, GermanyCompletedGrowth Hormon Deficiency | Turner Syndrome in Pre-pubertal Children
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AllerganActive, not recruitingInterstitial Cystitis/Bladder Pain Syndrome (IC/BPS)United States, Canada
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BioMarin PharmaceuticalCompletedMorquio A Syndrome | MPS IVA | Mucopolysaccharidosis IV AUnited States, Canada, France, Taiwan, Argentina, Colombia, Spain, Turkey, Japan, Saudi Arabia, Netherlands, Denmark, Korea, Republic of, Brazil, United Kingdom, Germany, Norway, Portugal, Italy, Qatar
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Visirna Therapeutics HK LimitedNot yet recruitingFamilial Chylomicronemia Syndrome
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Ionis Pharmaceuticals, Inc.Active, not recruitingFamilial Chylomicronemia SyndromeSpain, United Kingdom, France, Canada, United States, Italy, Netherlands, Norway, Portugal, Slovakia, Sweden