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Clinical Trials on Hyper-IgM+Immunodeficiency+Syndrome%2C+Type+1
Total 582 results
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Children's Hospital Medical Center, CincinnatiRecruitingNeurofibromatosis 1 | Noonan Syndrome | Legius Syndrome | Cardiofaciocutaneous Syndrome | Costello Syndrome | SYNGAP1-Related Intellectual Disability | DLG4 | RAS Mutation | Noonan Syndrome With Multiple Lentigines | Noonan Neurofibromatosis Syndrome | Smith-Kingsmore Syndrome | MTOR Gene Mutation | GATOR-1 Gene... and other conditionsUnited States
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AstraZenecaApproved for marketingNF type1 With Inoperable Plexiform NeurofibromasUnited States
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Sanford HealthUniversity of Exeter; The Leona M. and Harry B. Helmsley Charitable Trust; Pacific...RecruitingType 1 Diabetes | Celiac DiseaseUnited States
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Ultragenyx Pharmaceutical IncTerminatedGlucose Transporter Type 1 Deficiency SyndromeUnited States, Spain, Denmark, United Kingdom, Australia
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Emory UniversityGeorgia Center for Oncology Research & EducationNot yet recruitingHuman Immunodeficiency Virus | Human Papilloma Virus | Anal Intraepithelial Neoplasia | High-Grade Squamous Intraepithelial LesionsUnited States
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Vitaflo International, LtdCompletedIntractable Epilepsy | Glucose Transporter Type 1 Deficiency Syndrome | Ketogenic DietingUnited Kingdom
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Vitaflo International, LtdCompletedGlucose Transporter Type 1 Deficiency Syndrome | Ketogenic Dieting | Epilepsy IntractableUnited Kingdom
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Ann & Robert H Lurie Children's Hospital of ChicagoNational Institute of Neurological Disorders and Stroke (NINDS); Children's...RecruitingNeurofibromatosis 1 | Neurofibromatosis Type 1 | NF1United States
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Guy's and St Thomas' NHS Foundation TrustRecruitingNeurofibromatosis Type 1United Kingdom
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University Hospital, Strasbourg, FranceRecruitingNeurofibromatosis Type 1France
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National Cancer Institute (NCI)CompletedNeurofibroma | Neurofibromatosis Type 1United States
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Joergen SerupSahlgrenska University Hospital, SwedenActive, not recruitingCutaneous NeurofibromaDenmark, Sweden
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Centre Leon BerardRecruitingNeurofibroma | Neurofibroma, PlexiformFrance
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AstraZenecaMerck Sharp & Dohme LLCActive, not recruitingNeurofibromatosis Type 1United States, Spain, Germany, Netherlands, Russian Federation, Italy, Japan
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Shriners Hospitals for ChildrenCompletedNeurofibromatosis Type 1United States
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Washington University School of MedicineCompleted
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Ann & Robert H Lurie Children's Hospital of ChicagoCompleted
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KU LeuvenUnknownNeurofibromatosis Type 1Belgium
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Murdoch Childrens Research InstituteRoyal Children's HospitalCompletedPrimary Immunodeficiency | Invasive Pneumococcal Disease, Protection Against | Invasive Pneumococcal Disease, Recurrent Isolated, 1 | Invasive Pneumococcal Disease, Recurrent Isolated, 2Australia, New Zealand
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AstraZenecaRecruitingNeurofibromatosis Type 1Portugal, Spain, United Kingdom, Israel, France, Italy, Switzerland, Germany, Austria
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Assistance Publique - Hôpitaux de ParisCompletedNeurofibromatosis Type 1France
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Children's National Research InstituteEmory University; University of Texas Southwestern Medical Center; Arizona State...Completed
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Shriners Hospitals for ChildrenUniversity of Utah; Thrasher Research FundCompletedNeurofibromatosis Type 1United States
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University Hospital, ToulouseUnknownNeurofibromatosis Type 1France
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University of Alabama at BirminghamNational Cancer Institute (NCI); Children's Hospital of Philadelphia; Washington... and other collaboratorsCompletedNeurofibromatosis Type 1United States, Australia
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Tel-Aviv Sourasky Medical CenterUnknownNeurofibromatosis Type 1
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National Cancer Institute (NCI)CompletedPlexiform Neurofibroma | Neurofibromatosis Type IUnited States
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Instituto Nacional de Cardiologia Ignacio ChavezEchoNous Inc.RecruitingCardiorenal Syndrome Type 1Mexico
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Chulalongkorn UniversityNot yet recruitingEmpagliflozin in Cardiorenal Syndrome Type 1Thailand
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Drexel UniversityUniversity of North Carolina, Chapel Hill; University of KwaZuluCompletedChlamydia | Gonorrhea | Human Immunodeficiency Virus | Trichomonas Vaginitis | Herpes Simplex Type IISouth Africa
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National Cancer Institute (NCI)RecruitingKaposi's Sarcoma | Human Immunodeficiency Virus | Castleman's Disease | Viral-Associated CancerUnited States
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Vivent HealthH. Lee Moffitt Cancer Center and Research InstituteRecruitingHuman Immunodeficiency Virus | Human Papilloma VirusUnited States
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Medical College of WisconsinNational Cancer Institute (NCI); National Heart, Lung, and Blood Institute... and other collaboratorsCompletedChronic Granulomatous Disease | Hemophagocytic Lymphohistiocytosis | Leukocyte Adhesion Deficiency | Chronic Active Epstein-Barr Virus Infection | HIGM-1 | IPEXUnited States, Canada
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Rigshospitalet, DenmarkOdense University Hospital; University of Copenhagen; Imperial College London; University... and other collaboratorsActive, not recruitingMyelodysplastic Syndromes | Cytopenia | Chronic Myelomonocytic Leukemia-1Denmark, United States
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M.D. Anderson Cancer CenterRecruitingMyelodysplastic Syndrome | Recurrent Chronic Myelomonocytic Leukemia | Recurrent Myelodysplastic Syndrome | Chronic Myelomonocytic Leukemia-1 | Chronic Myelomonocytic Leukemia-2 | Chronic Myelomonocytic Leukemia-0United States
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National University Health System, SingaporeCompletedThymic Carcinoid | Multiple Endocrine Neoplasia Type 1 (MEN-1)Singapore
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Institut National de la Santé Et de la Recherche...Not yet recruitingAutoimmune Diseases | Systemic Lupus Erythematosus | Primary Immunodeficiency | Autoimmune Hepatitis | Juvenile Idiopathic Arthritis | IBD | Autoimmune Rheumatologic Disease | Autoimmune Diabetes | APECED | IPEX | Hemophagocytic Lymphohistiocytoses | Autoimmune Lymphoproliferative Syndrome | Autoimmune Thrombocytopenia and other conditions
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AlexionRecruiting
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Massachusetts General HospitalJohns Hopkins UniversityActive, not recruitingCutaneous NeurofibromaUnited States
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AstraZenecaWithdrawnNeurofibromatosis Type 1 | Plexiform Neurofibromas | Post-operativeChina
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Case Comprehensive Cancer CenterTerminatedGlioma | Brain Tumor | Neurofibromatosis Type 1United States
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University of UtahNational Institute of Neurological Disorders and Stroke (NINDS)CompletedNeurofibromatosis Type 1United States
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Massachusetts General HospitalCompletedNeurofibromatosis Type 1 | Cutaneous NeurofibromasUnited States
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University Hospital, ToulouseCompleted
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Hospices Civils de LyonCompletedNeurofibromatosis Type 1France
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KU LeuvenUnknownNeurofibromatosis Type 1Belgium
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Johns Hopkins UniversityNeurofibromatosis Therapeutic Acceleration ProgramRecruitingNeurofibromatosis 1 | Neurofibromatosis Type 1 | Cutaneous Neurofibroma | Neurofibromatosis (Nonmalignant)United States
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Nicole BacaRecruiting
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Spectrum Health HospitalsVan Andel Research InstituteRecruitingNeurofibromatosis Type 1 | Plexiform Neurofibromas | Cutaneous NeurofibromasUnited States