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Clinical Trials on Hyper-IgM+Immunodeficiency+Syndrome%2C+Type+1
Total 582 results
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AstraZenecaMerck Sharp & Dohme LLCActive, not recruitingNeurofibromatosis Type 1United States, Spain, Poland, Russian Federation
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Shriners Hospitals for ChildrenUniversity of UtahCompletedNeurofibromatosis Type 1 | Tibial DysplasiaUnited States
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University of Alabama at BirminghamNational Cancer Institute (NCI); Children's Hospital of Philadelphia; Washington... and other collaboratorsCompletedNeurofibromatosis Type 1United States
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Pharvaris Netherlands B.V.RecruitingHereditary Angioedema | Hereditary Angioedema Type I | Hereditary Angioedema Type II | Hereditary Angioedema Types I and II | Hereditary Angioedema Attack | Hereditary Angioedema With C1 Esterase Inhibitor Deficiency | Hereditary Angioedema - Type 1 | Hereditary Angioedema - Type 2 | C1 Esterase Inhibitor... and other conditionsUnited States, Puerto Rico
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TakedaRecruitingMultiple Myeloma | Secondary Immunodeficiency (SID)Greece, Spain, Italy, Romania, Argentina, Czechia, France, Germany, Poland, Sweden, Turkey
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Kristina HardyChildren's Hospital Los Angeles; Sydney Children's Hospitals Network; Royal Children... and other collaboratorsCompletedNeurofibromatosis Type 1United States
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Erasmus Medical CenterUniversitaire Ziekenhuizen KU Leuven; ZonMw: The Netherlands Organisation for... and other collaboratorsTerminatedNeurofibromatosis Type 1Spain, Belgium, Netherlands
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Massachusetts General HospitalCompletedNeurofibromatosis Type 1 | Cutaneous NeurofibromasUnited States
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John Jay High SchoolUnknownNeurofibromatosis Type 1United States
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Pharvaris Netherlands B.V.RecruitingHereditary Angioedema | Hereditary Angioedema Type I | Hereditary Angioedema Type II | Hereditary Angioedema Types I and II | Hereditary Angioedema Attack | Hereditary Angioedema With C1 Esterase Inhibitor Deficiency | Hereditary Angioedema - Type 1 | Hereditary Angioedema - Type 2 | C1 Esterase Inhibitor... and other conditionsUnited States, Bulgaria, Czechia, Hungary, Spain, France, Germany, Poland, Canada, Israel
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Akcea TherapeuticsIonis Pharmaceuticals, Inc.CompletedFamilial Chylomicronemia Syndrome | Lipoprotein Lipase Deficiency | Hyperlipoproteinemia Type 1United States, Canada, Germany, Israel, Italy, South Africa, Spain, United Kingdom, Brazil, France, Netherlands
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Akcea TherapeuticsIonis Pharmaceuticals, Inc.CompletedFamilial Chylomicronemia Syndrome | Lipoprotein Lipase Deficiency | Hyperlipoproteinemia Type 1Canada
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University of HelsinkiActive, not recruitingType1diabetes | Celiac DiseaseFinland
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Pediatric Brain Tumor ConsortiumNational Cancer Institute (NCI); American Lebanese Syrian Associated Charities...RecruitingLow Grade Glioma (LGG) of Brain With BRAF Aberration | High Grade Glioma (HGG) of the Brain With BRAF Aberration | Low Grade Glioma of Brain With Neurofibromatosis Type 1United States
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AstraZenecaMerck Sharp & Dohme LLCActive, not recruitingNeurofibromatosis 1 | Neurofibroma PlexiformChina
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University of Alabama at BirminghamPacific Pediatric Neuro-Oncology Consortium; Array BioPharmaActive, not recruitingNeurofibromatosis Type 1 | Plexiform NeurofibromaUnited States
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Assistance Publique - Hôpitaux de ParisNovartisCompletedNeurofibromatoses | Neurofibromatosis Type 1 | Plexiform NeurofibromaFrance
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Washington University School of MedicineSt. Louis Children's HospitalTerminated
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Children's Hospital of PhiladelphiaCompletedNeurofibromatosis Type 1 | Precancerous ConditionUnited States
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National Cancer Institute (NCI)TerminatedNeurofibromatosis Type 1 | Plexiform Neurofibroma | Spinal Cord NeurofibromaUnited States
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Children's Hospital of PhiladelphiaTerminatedNeurofibromatosis Type 1 | Precancerous ConditionUnited States
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Assistance Publique - Hôpitaux de ParisRecruitingHTLV-1 Infection | Lymphoproliferation Induced by HTLV-1 | HTLV-1 Adult T-cell Lymphoma / LeukemiaFrance
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National Cancer Institute (NCI)Active, not recruitingNeurofibromatosis 1 | Neurofibroma, Plexiform | Neurofibromatosis Type 1 | NF1United States
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National Cancer Institute (NCI)CompletedNeurofibromatosis Type 1 | Plexiform NeurofibromasUnited States
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Nantes University HospitalUniversité d'Angers (Angers, France); Association Neurofibromatoses et RecklinghaüsenCompletedNeurofibromatosis Type 1France
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National Cancer Institute (NCI)CompletedNeurofibromatosis Type 1 | Precancerous ConditionUnited States
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UK Kidney AssociationRecruitingVasculitis | AL Amyloidosis | Tuberous Sclerosis | Fabry Disease | Cystinuria | Focal Segmental Glomerulosclerosis | IgA Nephropathy | Bartter Syndrome | Pure Red Cell Aplasia | Membranous Nephropathy | Atypical Hemolytic Uremic Syndrome | Autosomal Dominant Polycystic Kidney Disease | Cystinosis | Nephronophthisis | BK Nephropathy and other conditionsUnited Kingdom
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National Cancer Institute (NCI)Active, not recruitingLow Grade Glioma | Recurrent Visual Pathway Glioma | Refractory Visual Pathway Glioma | Recurrent Childhood Pilocytic Astrocytoma | Recurrent Neurofibromatosis Type 1 | Refractory Neurofibromatosis Type 1United States
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PETHEMA FoundationCompleted
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Genzyme, a Sanofi CompanyCompletedHIV Infections | Lymphoma, Non-HodgkinUnited States
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Manchester University NHS Foundation TrustManchester Metropolitan UniversityCompletedMuscle Weakness | Neurofibromatosis Type 1United Kingdom
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National Human Genome Research Institute (NHGRI)CompletedNeurofibromatosis Type 1 | NF1 | Von Recklinghausen DiseaseUnited States
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Sanford HealthNational Ataxia Foundation; Beyond Batten Disease Foundation; Pitt Hopkins Research... and other collaboratorsRecruitingMitochondrial Diseases | Retinitis Pigmentosa | Myasthenia Gravis | Eosinophilic Gastroenteritis | Multiple System Atrophy | Leiomyosarcoma | Leukodystrophy | Anal Fistula | Spinocerebellar Ataxia Type 3 | Friedreich Ataxia | Kennedy Disease | Lyme Disease | Hemophagocytic Lymphohistiocytosis | Spinocerebellar Ataxia... and other conditionsUnited States, Australia
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Donald BaselRecruiting
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Guy's and St Thomas' NHS Foundation TrustCompletedNeurofibromatosis 1, NF1United Kingdom
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Roger PackerWithdrawnNeurofibromatosis Type 1 | Tumors of the Central Nervous SystemUnited States
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Children's Hospital of Fudan UniversityRecruitingImmunologic Deficiency Syndromes | Diabetes Mellitus, Type 1China
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Roger PackerChildren's National Research InstituteCompletedTarceva/Rapamycin for Children With Low-grade Gliomas With or Without Neurofibromatosis Type 1 (NF1)Low-grade GliomasUnited States
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National Cancer Institute (NCI)Enrolling by invitationHIV | Neurofibromatosis Type 1 | Brain TumorsUnited States
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Universitaire Ziekenhuizen KU LeuvenUnknownNeurofibromatosis Type 1Belgium
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Samsung Medical CenterNot yet recruitingCharcot-Marie-Tooth Disease, Type 1
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Atara BiotherapeuticsRecruitingLymphoproliferative Disorders | Leiomyosarcoma | Stem Cell Transplant Complications | Solid Organ Transplant Complications | Epstein-Barr Virus (EBV)-Associated Diseases | EBV+ Post-transplant Lymphoproliferative Disease (EBV+ PTLD) | Allogeneic Hematopoietic Cell Transplant | EBV+ Sarcomas | EBV+ Lymphoproliferative... and other conditionsUnited States, Austria, Belgium, France, Italy, Spain, United Kingdom
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Centre Hospitalier Universitaire, AmiensCompletedDiabetes Mellitus, Type 1France
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Jersey Shore University Medical CenterRutgers University; Rutgers Cancer Institute of New JerseyCompletedPancreatic Cancer | Parathyroid Disease | Thymic Cancer | MEN1 SyndromeUnited States
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Glaxo WellcomeCompletedHIV Infections | Lymphoma, Non-HodgkinUnited States
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Lund UniversityRecruitingType 1 Diabetes | Thyroid | Celiac Disease in ChildrenSweden
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Sarcoma Alliance for Research through CollaborationNational Cancer Institute (NCI)CompletedSarcoma | Neurofibromatosis Type 1United States
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National Cancer Institute (NCI)RecruitingNeurofibromatosis Type 1 | Low Grade Glioma | Visual Pathway GliomaUnited States, Canada, Puerto Rico
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Vanderbilt UniversityEunice Kennedy Shriver National Institute of Child Health and Human Development...RecruitingNeurofibromatosis Type 1 | Reading Disability | NF1 | Learning DisabilityUnited States
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Vanderbilt UniversityNational Institute of Neurological Disorders and Stroke (NINDS)CompletedNeurofibromatosis Type 1 | Reading DisabilitiesUnited States