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Clinical Trials on Hyper-IgM+Immunodeficiency+Syndrome%2C+Type+1
Total 582 results
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Washington University School of MedicineCompletedNeurofibromatosis Type 1 | Pediatric Brain TumorUnited States
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University Hospital, ToulouseCompleted
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National Cancer Institute (NCI)Active, not recruitingNeurofibromatosis 1 (NF1) | Plexiform Neurofibromas (PN)United States
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NYU Langone HealthCompletedNeurofibromatosis 1 and 2 (NF1 and NF2)United States
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Centre Hospitalier Universitaire de LiegeSanofi; Takeda; University of Liege; Orchard Therapeutics; Centre Hospitalier Régional... and other collaboratorsRecruitingCongenital Adrenal Hyperplasia | Hemophilia A | Hemophilia B | Mucopolysaccharidosis I | Mucopolysaccharidosis II | Cystic Fibrosis | Alpha 1-Antitrypsin Deficiency | Sickle Cell Disease | Fanconi Anemia | Chronic Granulomatous Disease | Wilson Disease | Severe Congenital Neutropenia | Ornithine Transcarbamylase... and other conditionsBelgium
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Bellicum PharmaceuticalsTerminatedLymphoma, Non-Hodgkin | Myelodysplastic Syndromes | Acute Lymphoblastic Leukemia | Primary Immunodeficiency | Anemia, Sickle Cell | Hemoglobinopathies | Fanconi Anemia | Anemia, Aplastic | Thalassemia | Cytopenia | Diamond Blackfan Anemia | Leukemia, Acute Myeloid (AML), ChildItaly
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National Cancer Institute (NCI)RecruitingMesothelioma | Familial Cancer | BRCA1-Associated Protein-1 (BAP1) Mutations | Tumor Predisposition Syndrome (TPDS)United States
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Scripps Translational Science InstituteCue HealthRecruitingImmunoCARE: Rapid, Accurate COVID Testing to Reduce Hospitalization of Immunocompromised IndividualsHIV Infections | Lymphoma | Leukemia | Cancer | Multiple Myeloma | Immunosuppression | Immunodeficiency | Transplant | Graft Versus Host Disease | Age-Related ImmunodeficiencyUnited States
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Therapeutic Advances in Childhood Leukemia ConsortiumNot yet recruitingNeurofibromatosis 1 | JMML | Leukemia, Juvenile Myelomonocytic | JCML | CBL Syndrome
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Kirby InstituteGilead Sciences; Melanoma Institute Australia; St Vincent's Hospital, Sydney; Royal... and other collaboratorsActive, not recruitingCOVID-19 | Cancer | Primary Immune Deficiency Disorder | HIV-1-infection | Immunosuppression DisordersAustralia
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National Cancer Institute (NCI)CompletedNeurofibromatosis Type 1 | Recurrent Childhood Pilocytic Astrocytoma | Recurrent Childhood Visual Pathway GliomaUnited States, Canada, Australia, New Zealand
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Baylor College of MedicineThe Methodist Hospital Research Institute; Center for Cell and Gene Therapy...RecruitingHaploidentical Hematopoietic Cell Transplantation Using TCR Alpha/Beta and CD19 Depletion (HAPLOTAB)Myelodysplastic Syndromes | Primary Immunodeficiency Diseases | Hemoglobinopathies | Chronic Myeloid Leukemia | Cytopenia | Severe Aplastic Anemia | Bone Marrow Failure Syndrome | Acute Myeloid Leukemia in Remission | Hemophagocytic Lymphohistiocytoses | Acute Lymphoblastic Leukemia in Remission | Severe...United States
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National Cancer Institute (NCI)Children's Oncology GroupActive, not recruitingJuvenile Myelomonocytic Leukemia | Neurofibromatosis Type 1United States
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Children's Oncology GroupNational Cancer Institute (NCI)CompletedBrain and Central Nervous System Tumors | Neurofibromatosis Type 1Canada, United States
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CENTOGENE GmbH RostockCompletedHereditary Angioedema | Hereditary Angioedema Type I | Hereditary Angioedema Type II | C1 Esterase Inhibitor Deficiency | HAE | Angio Edema | C4 Deficiency | Hereditary Angioedema Type IIITurkey, Armenia, Georgia, India, Peru, Poland, Romania
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Bellicum PharmaceuticalsTerminatedLymphoma, Non-Hodgkin | Acute Lymphoblastic Leukemia | Primary Immunodeficiency | Anemia, Sickle Cell | Hemoglobinopathies | Fanconi Anemia | Anemia, Aplastic | Myelodysplastic Syndrome | Thalassemia | Cytopenia | Diamond Blackfan Anemia | Osteopetrosis | Leukemia, Acute Myeloid (AML), ChildUnited Kingdom, Italy
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Chia Tai Tianqing Pharmaceutical Group Co., Ltd.Not yet recruitingType I NeurofibromatosisChina
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St. Jude Children's Research HospitalRecruitingPancreatic Cancer | Hodgkin Lymphoma | Lynch Syndrome | Tuberous Sclerosis | Fanconi Anemia | AML | Non Hodgkin Lymphoma | Familial Adenomatous Polyposis | Acute Leukemia | Nevoid Basal Cell Carcinoma Syndrome | Neurofibromatosis Type 1 | Neuroblastoma | Retinoblastoma | MDS | Rhabdomyosarcoma | Von Hippel-Lindau Disease | Adrenocortical Carcinoma and other conditionsUnited States
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University Health Network, TorontoCIHR Canadian HIV Trials NetworkCompletedHIV Infections | HIV Infection | Herpes Simplex Type IICanada, United Kingdom, Argentina, Brazil
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University of ArkansasWithdrawnPancreatic Neoplasms | Colorectal Neoplasms, Hereditary Nonpolyposis | BRCA1 Gene Mutation | BRCA2 Gene Mutation | Hereditary Pancreatitis | Ataxia Telangiectasia | Peutz-Jegher's Syndrome | Familial Atypical Mole-Malignant Melanoma SyndromeUnited States
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Atara BiotherapeuticsNo longer availableLymphoproliferative Disorders | Stem Cell Transplant Complications | Epstein-Barr Virus (EBV) Infections | EBV+ Associated Lymphoma | EBV+ Associated Post-transplant Lymphoproliferative Disease (EBV+ PTLD) | Epstein-Barr Viremia | Lymphoma, AIDS-related | Epstein-Barr Virus-associated Lymphoproliferative... and other conditions
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M.D. Anderson Cancer CenterNational Cancer Institute (NCI)RecruitingAcquired Immunodeficiency Syndrome | BK Virus Infection | Merkel Cell Carcinoma | Human Immunodeficiency Virus | Malignant Neoplasm | JC Virus Infection | Merkel Cell Polyomavirus Infection | Viral EncephalitisUnited States
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The Hospital for Sick ChildrenCompletedDiabetes Mellitus, Type 1 | Celiac Disease | CeliacCanada
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The Hospital for Sick ChildrenCompletedDiabetes Mellitus, Type 1 | Celiac DiseaseCanada
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University of BirminghamHeart of England NHS TrustCompletedType 1 Diabetes | Obstructive Sleep ApnoeaUnited Kingdom
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National Cancer Institute (NCI)CompletedNeurofibroma, Plexiform | Neurofibromatosis Type IUnited States, Germany
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St. Justine's HospitalTerminatedPlexiform NeurofibromasCanada
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Mayo ClinicNational Cancer Institute (NCI)RecruitingNeurofibromatosis Type 1 | Metastatic Malignant Peripheral Nerve Sheath Tumor | Recurrent Malignant Peripheral Nerve Sheath TumorUnited States
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Great Ormond Street Hospital for Children NHS Foundation...AstraZenecaCompletedNeurofibromatosis Type 1 | Optic Nerve Glioma | Plexiform NeurofibromaUnited Kingdom
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National Cancer Institute (NCI)CompletedNeurofibromatosis Type 1 | Cutaneous Neurofibroma | Optic Nerve GliomaUnited States
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National Institute of Allergy and Infectious Diseases...RecruitingChronic Granulomatous Disease (CGD) | X-Linked Severe Combined Immune Deficiency (XSCID) | Leukocyte Adhesion Deficiency 1 (LAD) | Graft Versus Host Disease (cGvHD)United States
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H. Lee Moffitt Cancer Center and Research InstituteRecruitingLynch Syndrome | Pancreatic Ductal Adenocarcinoma | Chronic Pancreatitis | Pancreatic Cyst | Ataxia Telangiectasia | FAP | Peutz-Jeghers Syndrome | PALB2 Gene Mutation | BRCA Mutation | Fatty Pancreas | Genetic Pancreatic Cancer | Genetic Pancreatitis | Familial Atypical Multiple Mole-MelanomaUnited States
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HAE Global Registry FoundationRecruitingHereditary Angioedema Type I and IIItaly
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KalVista Pharmaceuticals, Ltd.CompletedHereditary AngioedemaUnited States, Austria, Czechia, Germany, Hungary, Italy, Netherlands, North Macedonia, Poland, United Kingdom
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Prothya BiosolutionsCompletedHereditary Angioedema Type I | Angioneurotic EdemaNetherlands
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Centre Hospitalier Universitaire DijonRecruitingMultiple Endocrine NeoplasiaFrance
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Central Hospital, Nancy, FranceEnrolling by invitationAutoimmune Diseases | Type 1 Diabetes | Graves Disease | Celiac Disease | Vitiligo | Hashimoto Disease | Addison DiseaseFrance
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M.D. Anderson Cancer CenterNational Cancer Institute (NCI)Active, not recruitingHematopoietic and Lymphoid Cell Neoplasm | Myelofibrosis | Acute Myeloid Leukemia Arising From Previous Myelodysplastic Syndrome | Secondary Acute Myeloid Leukemia | Recurrent Acute Myeloid Leukemia | Recurrent Chronic Myelomonocytic Leukemia | Refractory Chronic Myelomonocytic Leukemia | High Risk... and other conditionsUnited States
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Lund UniversityUnknownDiabetes Mellitus, Type 1 | Celiac Disease in Children | RemissionSweden
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University Hospital, Basel, SwitzerlandRecruiting
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Massachusetts General HospitalJohns Hopkins UniversityRecruitingNeurofibromatosis 1United States
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University of ArkansasRecruitingNeurofibromatosis 1United States
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Children's Hospital Medical Center, CincinnatiActive, not recruitingNeurofibromatosis 1United States
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The University of Texas Health Science Center,...Texas Neurofibromatosis FoundationCompletedNeurofibromatosis 1United States
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Juha PeltonenUnknownNeurofibromatosis 1
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Mayo ClinicCompletedNeurofibromatosis
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Stanford UniversityJohns Hopkins University; University of California, San FranciscoRecruitingNeurofibromatosis 1United States
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National Cancer Institute (NCI)RecruitingNeurofibromatosis 1United States
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Children's Hospital Medical Center, CincinnatiUnited States Department of DefenseRecruitingNeurofibromatosis 1United States
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NobelpharmaTerminated